JP2021533197A5 - - Google Patents

Info

Publication number
JP2021533197A5
JP2021533197A5 JP2021529257A JP2021529257A JP2021533197A5 JP 2021533197 A5 JP2021533197 A5 JP 2021533197A5 JP 2021529257 A JP2021529257 A JP 2021529257A JP 2021529257 A JP2021529257 A JP 2021529257A JP 2021533197 A5 JP2021533197 A5 JP 2021533197A5
Authority
JP
Japan
Prior art keywords
oligonucleotide
complex
transferrin receptor
complex according
receptor antibody
Prior art date
Application number
JP2021529257A
Other languages
English (en)
Japanese (ja)
Other versions
JP2021533197A (ja
JPWO2020028841A5 (https=
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2019/044960 external-priority patent/WO2020028841A1/en
Publication of JP2021533197A publication Critical patent/JP2021533197A/ja
Publication of JP2021533197A5 publication Critical patent/JP2021533197A5/ja
Publication of JPWO2020028841A5 publication Critical patent/JPWO2020028841A5/ja
Priority to JP2025006544A priority Critical patent/JP2025071093A/ja
Pending legal-status Critical Current

Links

JP2021529257A 2018-08-02 2019-08-02 ポンペ病を処置するための筋標的化複合体およびそれらの使用 Pending JP2021533197A (ja)

Priority Applications (1)

Application Number Priority Date Filing Date Title
JP2025006544A JP2025071093A (ja) 2018-08-02 2025-01-17 ポンペ病を処置するための筋標的化複合体およびそれらの使用

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201862713959P 2018-08-02 2018-08-02
US62/713,959 2018-08-02
PCT/US2019/044960 WO2020028841A1 (en) 2018-08-02 2019-08-02 Muscle targeting complexes and uses thereof for treating pompe disease

Related Child Applications (1)

Application Number Title Priority Date Filing Date
JP2025006544A Division JP2025071093A (ja) 2018-08-02 2025-01-17 ポンペ病を処置するための筋標的化複合体およびそれらの使用

Publications (3)

Publication Number Publication Date
JP2021533197A JP2021533197A (ja) 2021-12-02
JP2021533197A5 true JP2021533197A5 (https=) 2022-08-10
JPWO2020028841A5 JPWO2020028841A5 (https=) 2022-08-10

Family

ID=69230844

Family Applications (2)

Application Number Title Priority Date Filing Date
JP2021529257A Pending JP2021533197A (ja) 2018-08-02 2019-08-02 ポンペ病を処置するための筋標的化複合体およびそれらの使用
JP2025006544A Pending JP2025071093A (ja) 2018-08-02 2025-01-17 ポンペ病を処置するための筋標的化複合体およびそれらの使用

Family Applications After (1)

Application Number Title Priority Date Filing Date
JP2025006544A Pending JP2025071093A (ja) 2018-08-02 2025-01-17 ポンペ病を処置するための筋標的化複合体およびそれらの使用

Country Status (9)

Country Link
US (1) US20210317226A1 (https=)
EP (1) EP3830127A4 (https=)
JP (2) JP2021533197A (https=)
KR (1) KR20210054513A (https=)
CN (2) CN118662653A (https=)
CA (1) CA3108285A1 (https=)
EA (1) EA202190417A1 (https=)
IL (1) IL280483A (https=)
WO (1) WO2020028841A1 (https=)

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FI3635009T3 (fi) 2017-06-07 2026-04-07 Regeneron Pharma Koostumuksia ja menetelmiä entsyymien internalisoimiseksi
JP7779653B2 (ja) 2018-02-07 2025-12-03 リジェネロン・ファーマシューティカルズ・インコーポレイテッド 治療用タンパク質送達のための方法および組成物
EP3793591A1 (en) 2018-05-17 2021-03-24 Regeneron Pharmaceuticals, Inc. Anti-cd63 antibodies, conjugates, and uses thereof
US12370264B1 (en) 2018-08-02 2025-07-29 Dyne Therapeutics, Inc. Complexes comprising an anti-transferrin receptor antibody linked to an oligonucleotide and method of delivering oligonucleotide to a subject
US11911484B2 (en) 2018-08-02 2024-02-27 Dyne Therapeutics, Inc. Muscle targeting complexes and uses thereof for treating myotonic dystrophy
US12018087B2 (en) 2018-08-02 2024-06-25 Dyne Therapeutics, Inc. Muscle-targeting complexes comprising an anti-transferrin receptor antibody linked to an oligonucleotide and methods of delivering oligonucleotide to a subject
US12097263B2 (en) 2018-08-02 2024-09-24 Dyne Therapeutics, Inc. Muscle targeting complexes and uses thereof for treating myotonic dystrophy
EP3829595A4 (en) 2018-08-02 2022-08-24 Dyne Therapeutics, Inc. MUSCLE-DIRECTED COMPLEXES AND USES THEREOF IN THE TREATMENT OF DYSTROPHINOPATHIES
US20220193250A1 (en) 2018-08-02 2022-06-23 Dyne Therapeutics, Inc. Muscle targeting complexes and uses thereof for treating facioscapulohumeral muscular dystrophy
US11168141B2 (en) 2018-08-02 2021-11-09 Dyne Therapeutics, Inc. Muscle targeting complexes and uses thereof for treating dystrophinopathies
US20230330246A1 (en) * 2020-05-05 2023-10-19 Avidity Biosciences, Inc. Compositions and methods of treating pompe disease
US11638761B2 (en) 2021-07-09 2023-05-02 Dyne Therapeutics, Inc. Muscle targeting complexes and uses thereof for treating Facioscapulohumeral muscular dystrophy
IL309936A (en) 2021-07-09 2024-03-01 Dyne Therapeutics Inc Muscle targeting complexes and formulations for the treatment of dystrophinopathy
US11771776B2 (en) 2021-07-09 2023-10-03 Dyne Therapeutics, Inc. Muscle targeting complexes and uses thereof for treating dystrophinopathies
US11672872B2 (en) 2021-07-09 2023-06-13 Dyne Therapeutics, Inc. Anti-transferrin receptor antibody and uses thereof
US11969475B2 (en) 2021-07-09 2024-04-30 Dyne Therapeutics, Inc. Muscle targeting complexes and uses thereof for treating facioscapulohumeral muscular dystrophy
US11633498B2 (en) 2021-07-09 2023-04-25 Dyne Therapeutics, Inc. Muscle targeting complexes and uses thereof for treating myotonic dystrophy
EP4396231A1 (en) 2021-09-01 2024-07-10 Biogen MA Inc. Anti-transferrin receptor antibodies and uses thereof
US20250339553A1 (en) 2022-04-15 2025-11-06 Dyne Therapeutics, Inc. Muscle targeting complexes and formulations for treating myotonic dystrophy
CA3263494A1 (en) * 2022-07-29 2024-02-01 Regeneron Pharmaceuticals, Inc. ANTI-TFR FUSIONS: PAYLOAD AND THEIR METHODS OF USE
WO2025160275A1 (en) 2024-01-24 2025-07-31 Arrowhead Pharmaceuticals, Inc. Anti-transferrin receptor antibodies, conjugates thereof, and uses thereof

Family Cites Families (5)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
WO2004094647A2 (en) * 2003-04-18 2004-11-04 Cytovia, Inc. Methods of treating diseases responsive to induction of apoptosis and screening assays
US20170182189A1 (en) * 2014-05-23 2017-06-29 Genzyme Corporation Inhibiting or downregulating glycogen synthase by creating premature stop codons using antisense oligonucleotides
AU2016365834B2 (en) * 2015-12-08 2023-09-28 Regeneron Pharmaceuticals, Inc. Compositions and methods for internalizing enzymes
CA3021267A1 (en) * 2016-04-18 2017-10-26 Sarepta Therapeutics, Inc. Antisense oligomers and methods of using the same for treating diseases associated with the acid alpha-glucosidase gene
CN109310765A (zh) * 2016-06-20 2019-02-05 领先基因生物技术股份有限公司 抗体-药物偶联物

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