CN118662653A - 肌肉靶向复合物及其用于治疗蓬佩病的用途 - Google Patents

肌肉靶向复合物及其用于治疗蓬佩病的用途 Download PDF

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Publication number
CN118662653A
CN118662653A CN202410663435.8A CN202410663435A CN118662653A CN 118662653 A CN118662653 A CN 118662653A CN 202410663435 A CN202410663435 A CN 202410663435A CN 118662653 A CN118662653 A CN 118662653A
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complex
antibody
oligonucleotide
transferrin receptor
muscle
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CN202410663435.8A
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Chinese (zh)
Inventor
罗梅什·R·苏布拉马尼亚
穆罕默德·T·卡塔纳尼
蒂莫西·威登
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Dyne Therapeutics Inc
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Dyne Therapeutics Inc
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    • C07K16/18—Immunoglobulins [IG], e.g. monoclonal or polyclonal antibodies against material from animals or humans
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CN202410663435.8A 2018-08-02 2019-08-02 肌肉靶向复合物及其用于治疗蓬佩病的用途 Pending CN118662653A (zh)

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US201862713959P 2018-08-02 2018-08-02
US62/713,959 2018-08-02
PCT/US2019/044960 WO2020028841A1 (en) 2018-08-02 2019-08-02 Muscle targeting complexes and uses thereof for treating pompe disease
CN201980064590.5A CN112912399A (zh) 2018-08-02 2019-08-02 肌肉靶向复合物及其用于治疗蓬佩病的用途

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CN201980064590.5A Pending CN112912399A (zh) 2018-08-02 2019-08-02 肌肉靶向复合物及其用于治疗蓬佩病的用途

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US (1) US20210317226A1 (https=)
EP (1) EP3830127A4 (https=)
JP (2) JP2021533197A (https=)
KR (1) KR20210054513A (https=)
CN (2) CN118662653A (https=)
CA (1) CA3108285A1 (https=)
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