JP2021090458A5 - - Google Patents

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JP2021090458A5
JP2021090458A5 JP2021037024A JP2021037024A JP2021090458A5 JP 2021090458 A5 JP2021090458 A5 JP 2021090458A5 JP 2021037024 A JP2021037024 A JP 2021037024A JP 2021037024 A JP2021037024 A JP 2021037024A JP 2021090458 A5 JP2021090458 A5 JP 2021090458A5
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pharmaceutical composition
seq
intron
moiety
exon
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JP2021037024A
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JP2021037024A 2015-03-18 2021-03-09 ミオスタチンにおけるアンチセンスに誘導されるエクソンの排除 Pending JP2021090458A (ja)

Applications Claiming Priority (4)

Application Number Priority Date Filing Date Title
US201562135048P 2015-03-18 2015-03-18
US62/135,048 2015-03-18
US201562162571P 2015-05-15 2015-05-15
US62/162,571 2015-05-15

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JP2021090458A JP2021090458A (ja) 2021-06-17
JP2021090458A5 true JP2021090458A5 (OSRAM) 2021-11-11

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JP2017548452A Active JP6942054B2 (ja) 2015-03-18 2016-03-18 ミオスタチンにおけるアンチセンスに誘導されるエクソンの排除
JP2021037024A Pending JP2021090458A (ja) 2015-03-18 2021-03-09 ミオスタチンにおけるアンチセンスに誘導されるエクソンの排除

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US (2) US11015200B2 (OSRAM)
EP (1) EP3271372A4 (OSRAM)
JP (2) JP6942054B2 (OSRAM)
BR (1) BR112017019971A2 (OSRAM)
MA (1) MA41795A (OSRAM)
WO (1) WO2016149659A2 (OSRAM)

Families Citing this family (9)

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JP6875684B2 (ja) * 2015-09-16 2021-05-26 日本新薬株式会社 筋萎縮症治療用アンチセンス核酸
US20190337987A1 (en) * 2016-12-30 2019-11-07 Olipass Corporation Exon skipping by peptide nucleic acid derivatives
US11572560B2 (en) 2018-10-03 2023-02-07 Massachusetts Institute Of Technology Splicing-dependent transcriptional gene silencing or activation
WO2021044004A1 (en) * 2019-09-05 2021-03-11 Sanofi Oligonucleotides containing nucleotide analogs
KR20230130639A (ko) * 2020-12-03 2023-09-12 (주)라트바이오 마이오스타틴 유전자가 변형된 형질전환 동물
CN116981772A (zh) * 2021-02-26 2023-10-31 神户天然物化学株式会社 表达肌抑素的剪接变体的核酸药物

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