JP2020537637A5 - - Google Patents

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JP2020537637A5
JP2020537637A5 JP2020516820A JP2020516820A JP2020537637A5 JP 2020537637 A5 JP2020537637 A5 JP 2020537637A5 JP 2020516820 A JP2020516820 A JP 2020516820A JP 2020516820 A JP2020516820 A JP 2020516820A JP 2020537637 A5 JP2020537637 A5 JP 2020537637A5
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suspension
immunosuppressant
raav
use according
hids
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JP2020516820A
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JP7449223B2 (ja
JP2020537637A (ja
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JP2020516820A 2017-09-22 2018-09-21 ムコ多糖症ii型を治療するための遺伝子療法 Active JP7449223B2 (ja)

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JP2024031557A JP2024063154A (ja) 2017-09-22 2024-03-01 ムコ多糖症ii型を治療するための遺伝子療法

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US201762561769P 2017-09-22 2017-09-22
US201762562179P 2017-09-22 2017-09-22
US62/562,179 2017-09-22
US62/561,769 2017-09-22
US201762573841P 2017-10-18 2017-10-18
US62/573,841 2017-10-18
PCT/US2018/052129 WO2019060662A1 (en) 2017-09-22 2018-09-21 GENE THERAPY FOR THE TREATMENT OF MUCOPOLYSACCHARIDOSE TYPE II

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JP2020537637A JP2020537637A (ja) 2020-12-24
JP2020537637A5 true JP2020537637A5 (enExample) 2021-10-21
JP7449223B2 JP7449223B2 (ja) 2024-03-13

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JP2024031557A Pending JP2024063154A (ja) 2017-09-22 2024-03-01 ムコ多糖症ii型を治療するための遺伝子療法

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US (3) US11819539B2 (enExample)
EP (1) EP3684938A1 (enExample)
JP (2) JP7449223B2 (enExample)
KR (2) KR102883778B1 (enExample)
AU (1) AU2018335752B2 (enExample)
BR (1) BR112020005249A2 (enExample)
CA (1) CA3076036A1 (enExample)
IL (1) IL273427B2 (enExample)
SG (1) SG11202002457RA (enExample)
TW (1) TWI835747B (enExample)
WO (1) WO2019060662A1 (enExample)

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JP2020526514A (ja) 2017-07-06 2020-08-31 ザ・トラステイーズ・オブ・ザ・ユニバーシテイ・オブ・ペンシルベニア ムコ多糖症i型を治療するための遺伝子治療
TWI835747B (zh) * 2017-09-22 2024-03-21 賓州大學委員會 用於治療黏多醣病 ii 型之基因治療
IL280198B1 (en) 2018-07-18 2025-09-01 Regenxbio Inc Treatment of mucopolysaccharidosis I with fully glycosylated human iduronidase-alpha-L (idus)
WO2021070082A1 (en) 2019-10-07 2021-04-15 Wӓrtsilӓ Services Switzerland Ltd. Step lift control of hydraulically actuated poppet valves
JP2023511382A (ja) 2020-01-22 2023-03-17 レジェンクスバイオ インコーポレーテッド 完全ヒトグリコシル化ヒトα-L-イズロニダーゼ(IDUA)を用いたムコ多糖症I型の治療

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