JP2020503009A5 - - Google Patents

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JP2020503009A5
JP2020503009A5 JP2019531378A JP2019531378A JP2020503009A5 JP 2020503009 A5 JP2020503009 A5 JP 2020503009A5 JP 2019531378 A JP2019531378 A JP 2019531378A JP 2019531378 A JP2019531378 A JP 2019531378A JP 2020503009 A5 JP2020503009 A5 JP 2020503009A5
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antisense oligomer
oligomer conjugate
pharmaceutically acceptable
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JP2019531378A
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JP2020503009A (ja
JP7118063B2 (ja
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Priority claimed from PCT/US2017/066222 external-priority patent/WO2018118599A1/en
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JP2019531378A 2016-12-19 2017-12-13 筋ジストロフィーに対するエクソンスキッピングオリゴマーコンジュゲート Active JP7118063B2 (ja)

Applications Claiming Priority (9)

Application Number Priority Date Filing Date Title
US201662436182P 2016-12-19 2016-12-19
US62/436,182 2016-12-19
US201762443476P 2017-01-06 2017-01-06
US62/443,476 2017-01-06
US201762479173P 2017-03-30 2017-03-30
US62/479,173 2017-03-30
US201762562080P 2017-09-22 2017-09-22
US62/562,080 2017-09-22
PCT/US2017/066222 WO2018118599A1 (en) 2016-12-19 2017-12-13 Exon skipping oligomer conjugates for muscular dystrophy

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JP2020202518A Division JP2021045160A (ja) 2016-12-19 2020-12-07 筋ジストロフィーに対するエクソンスキッピングオリゴマーコンジュゲート

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JP2020503009A JP2020503009A (ja) 2020-01-30
JP2020503009A5 true JP2020503009A5 (US07794700-20100914-C00152.png) 2021-01-21
JP7118063B2 JP7118063B2 (ja) 2022-08-15

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JP2019531378A Active JP7118063B2 (ja) 2016-12-19 2017-12-13 筋ジストロフィーに対するエクソンスキッピングオリゴマーコンジュゲート
JP2020202518A Withdrawn JP2021045160A (ja) 2016-12-19 2020-12-07 筋ジストロフィーに対するエクソンスキッピングオリゴマーコンジュゲート
JP2023136250A Pending JP2023156512A (ja) 2016-12-19 2023-08-24 筋ジストロフィーに対するエクソンスキッピングオリゴマーコンジュゲート

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JP2023136250A Pending JP2023156512A (ja) 2016-12-19 2023-08-24 筋ジストロフィーに対するエクソンスキッピングオリゴマーコンジュゲート

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US (4) US10888578B2 (US07794700-20100914-C00152.png)
EP (1) EP3554553B1 (US07794700-20100914-C00152.png)
JP (3) JP7118063B2 (US07794700-20100914-C00152.png)
KR (2) KR102552428B1 (US07794700-20100914-C00152.png)
CN (1) CN110290812B (US07794700-20100914-C00152.png)
AU (1) AU2017382723A1 (US07794700-20100914-C00152.png)
BR (1) BR112019012647A2 (US07794700-20100914-C00152.png)
CA (1) CA3046793A1 (US07794700-20100914-C00152.png)
CO (1) CO2019007397A2 (US07794700-20100914-C00152.png)
DK (1) DK3554553T3 (US07794700-20100914-C00152.png)
ES (1) ES2927079T3 (US07794700-20100914-C00152.png)
HR (1) HRP20220943T1 (US07794700-20100914-C00152.png)
HU (1) HUE059843T2 (US07794700-20100914-C00152.png)
IL (2) IL267244B (US07794700-20100914-C00152.png)
LT (1) LT3554553T (US07794700-20100914-C00152.png)
MD (1) MD3554553T2 (US07794700-20100914-C00152.png)
MX (1) MX2019006882A (US07794700-20100914-C00152.png)
MY (1) MY195801A (US07794700-20100914-C00152.png)
NZ (1) NZ755416A (US07794700-20100914-C00152.png)
PL (1) PL3554553T3 (US07794700-20100914-C00152.png)
PT (1) PT3554553T (US07794700-20100914-C00152.png)
RS (1) RS63610B1 (US07794700-20100914-C00152.png)
SA (1) SA519402154B1 (US07794700-20100914-C00152.png)
SG (1) SG10202012839TA (US07794700-20100914-C00152.png)
TW (1) TWI760402B (US07794700-20100914-C00152.png)
WO (1) WO2018118599A1 (US07794700-20100914-C00152.png)
ZA (1) ZA201904092B (US07794700-20100914-C00152.png)

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MX2019006882A (es) * 2016-12-19 2019-08-16 Sarepta Therapeutics Inc Conjugados de oligomeros de omision de exon para distrofia muscular.
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