JP2018531609A5 - - Google Patents

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Publication number
JP2018531609A5
JP2018531609A5 JP2018521395A JP2018521395A JP2018531609A5 JP 2018531609 A5 JP2018531609 A5 JP 2018531609A5 JP 2018521395 A JP2018521395 A JP 2018521395A JP 2018521395 A JP2018521395 A JP 2018521395A JP 2018531609 A5 JP2018531609 A5 JP 2018531609A5
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Japan
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nucleic acid
seq
vector
sequence
fxn
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JP2018521395A
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Japanese (ja)
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JP6767483B2 (ja
JP2018531609A (ja
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Priority claimed from PCT/IB2016/056572 external-priority patent/WO2017077451A1/en
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Publication of JP2018531609A5 publication Critical patent/JP2018531609A5/ja
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JP2018521395A 2015-11-05 2016-11-01 遺伝子療法のための、改変されたフリードライヒ運動失調症遺伝子およびベクター Expired - Fee Related JP6767483B2 (ja)

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US201562251288P 2015-11-05 2015-11-05
US62/251,288 2015-11-05
US201662411980P 2016-10-24 2016-10-24
US62/411,980 2016-10-24
PCT/IB2016/056572 WO2017077451A1 (en) 2015-11-05 2016-11-01 Modified friedreich ataxia genes and vectors for gene therapy

Related Child Applications (1)

Application Number Title Priority Date Filing Date
JP2020156320A Division JP2021019591A (ja) 2015-11-05 2020-09-17 遺伝子療法のための、改変されたフリードライヒ運動失調症遺伝子およびベクター

Publications (3)

Publication Number Publication Date
JP2018531609A JP2018531609A (ja) 2018-11-01
JP2018531609A5 true JP2018531609A5 (https=) 2019-12-12
JP6767483B2 JP6767483B2 (ja) 2020-10-14

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ID=57288476

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JP2018521395A Expired - Fee Related JP6767483B2 (ja) 2015-11-05 2016-11-01 遺伝子療法のための、改変されたフリードライヒ運動失調症遺伝子およびベクター
JP2020156320A Pending JP2021019591A (ja) 2015-11-05 2020-09-17 遺伝子療法のための、改変されたフリードライヒ運動失調症遺伝子およびベクター

Family Applications After (1)

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JP2020156320A Pending JP2021019591A (ja) 2015-11-05 2020-09-17 遺伝子療法のための、改変されたフリードライヒ運動失調症遺伝子およびベクター

Country Status (18)

Country Link
US (2) US10548947B2 (https=)
EP (1) EP3370778A1 (https=)
JP (2) JP6767483B2 (https=)
KR (2) KR102200642B1 (https=)
CN (1) CN108348621A (https=)
AU (2) AU2016347887B2 (https=)
BR (1) BR112018007453A2 (https=)
CA (1) CA2947584A1 (https=)
CO (1) CO2018004564A2 (https=)
HK (1) HK1250924A1 (https=)
IL (1) IL259141A (https=)
MX (1) MX2018005084A (https=)
PE (1) PE20181156A1 (https=)
PH (1) PH12018500964A1 (https=)
RU (2) RU2021102893A (https=)
SG (2) SG11201802408RA (https=)
TW (2) TWI654301B (https=)
WO (1) WO2017077451A1 (https=)

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