KR102200642B1 - 유전자 치료를 위한 변형된 프리드라이히 운동실조증 유전자 및 벡터 - Google Patents

유전자 치료를 위한 변형된 프리드라이히 운동실조증 유전자 및 벡터 Download PDF

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KR102200642B1
KR102200642B1 KR1020187015819A KR20187015819A KR102200642B1 KR 102200642 B1 KR102200642 B1 KR 102200642B1 KR 1020187015819 A KR1020187015819 A KR 1020187015819A KR 20187015819 A KR20187015819 A KR 20187015819A KR 102200642 B1 KR102200642 B1 KR 102200642B1
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nucleic acid
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sequence
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리차드 제이 새멀스키
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뱀부 테라퓨틱스 인코포레이티드
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KR1020187015819A 2015-11-05 2016-11-01 유전자 치료를 위한 변형된 프리드라이히 운동실조증 유전자 및 벡터 Expired - Fee Related KR102200642B1 (ko)

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US201562251288P 2015-11-05 2015-11-05
US62/251,288 2015-11-05
US201662411980P 2016-10-24 2016-10-24
US62/411,980 2016-10-24
PCT/IB2016/056572 WO2017077451A1 (en) 2015-11-05 2016-11-01 Modified friedreich ataxia genes and vectors for gene therapy

Related Child Applications (1)

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KR1020217000034A Division KR20210005994A (ko) 2015-11-05 2016-11-01 유전자 치료를 위한 변형된 프리드라이히 운동실조증 유전자 및 벡터

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KR20180077275A KR20180077275A (ko) 2018-07-06
KR102200642B1 true KR102200642B1 (ko) 2021-01-12

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KR1020187015819A Expired - Fee Related KR102200642B1 (ko) 2015-11-05 2016-11-01 유전자 치료를 위한 변형된 프리드라이히 운동실조증 유전자 및 벡터
KR1020217000034A Withdrawn KR20210005994A (ko) 2015-11-05 2016-11-01 유전자 치료를 위한 변형된 프리드라이히 운동실조증 유전자 및 벡터

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US (2) US10548947B2 (https=)
EP (1) EP3370778A1 (https=)
JP (2) JP6767483B2 (https=)
KR (2) KR102200642B1 (https=)
CN (1) CN108348621A (https=)
AU (2) AU2016347887B2 (https=)
BR (1) BR112018007453A2 (https=)
CA (1) CA2947584A1 (https=)
CO (1) CO2018004564A2 (https=)
HK (1) HK1250924A1 (https=)
IL (1) IL259141A (https=)
MX (1) MX2018005084A (https=)
PE (1) PE20181156A1 (https=)
PH (1) PH12018500964A1 (https=)
RU (2) RU2021102893A (https=)
SG (2) SG11201802408RA (https=)
TW (2) TWI654301B (https=)
WO (1) WO2017077451A1 (https=)

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