JP2018519835A5 - - Google Patents

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JP2018519835A5
JP2018519835A5 JP2018500697A JP2018500697A JP2018519835A5 JP 2018519835 A5 JP2018519835 A5 JP 2018519835A5 JP 2018500697 A JP2018500697 A JP 2018500697A JP 2018500697 A JP2018500697 A JP 2018500697A JP 2018519835 A5 JP2018519835 A5 JP 2018519835A5
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seq
nucleic acid
acid molecule
stranded nucleic
isolated double
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JP2018500697A
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JP6983752B2 (ja
JP2018519835A (ja
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Priority claimed from PCT/US2016/041095 external-priority patent/WO2017007813A1/en
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JP2018500697A 2015-07-06 2016-07-06 スーパーオキシドディスムターゼ1(sod1)を標的とする核酸分子 Expired - Fee Related JP6983752B2 (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201562189050P 2015-07-06 2015-07-06
US62/189,050 2015-07-06
PCT/US2016/041095 WO2017007813A1 (en) 2015-07-06 2016-07-06 Nucleic acid molecules targeting superoxide dismutase 1 (sod1)

Publications (3)

Publication Number Publication Date
JP2018519835A JP2018519835A (ja) 2018-07-26
JP2018519835A5 true JP2018519835A5 (enExample) 2019-08-15
JP6983752B2 JP6983752B2 (ja) 2021-12-17

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JP2018500697A Expired - Fee Related JP6983752B2 (ja) 2015-07-06 2016-07-06 スーパーオキシドディスムターゼ1(sod1)を標的とする核酸分子

Country Status (7)

Country Link
US (1) US11001845B2 (enExample)
EP (2) EP3862005A1 (enExample)
JP (1) JP6983752B2 (enExample)
KR (1) KR20180026739A (enExample)
CN (1) CN108135923B (enExample)
CA (1) CA2991598A1 (enExample)
WO (1) WO2017007813A1 (enExample)

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KR20180026739A (ko) 2015-07-06 2018-03-13 알엑스아이 파마슈티칼스 코포레이션 슈퍼옥시드 디스뮤타제 1 (sod1)을 표적화하는 핵산 분자
US11021707B2 (en) 2015-10-19 2021-06-01 Phio Pharmaceuticals Corp. Reduced size self-delivering nucleic acid compounds targeting long non-coding RNA
EP3612152A4 (en) 2017-04-19 2021-02-17 Phio Pharmaceuticals Corp. TOPICAL ADMINISTRATION OF NUCLEIC ACID COMPOUNDS
EP4055166A2 (en) * 2019-11-06 2022-09-14 Alnylam Pharmaceuticals, Inc. Extrahepatic delivery
EP4291654A2 (en) * 2021-02-12 2023-12-20 Alnylam Pharmaceuticals, Inc. Superoxide dismutase 1 (sod1) irna compositions and methods of use thereof for treating or preventing superoxide dismutase 1- (sod1-) associated neurodegenerative diseases
US20250297258A1 (en) * 2021-07-07 2025-09-25 Ractigen Therapeutics Oligonucleotide-based delivery vehicle for oligonucleotides agents and methods of use thereof
CN120202298A (zh) * 2023-08-29 2025-06-24 石药集团中奇制药技术(石家庄)有限公司 一种抑制sod1基因表达的dsRNA分子及其应用

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