DOP2019000179A - Estrategia optimizada para modificaciones de omisión de exones mediante el uso de crispr/cas9 con secuencias guía triples - Google Patents

Estrategia optimizada para modificaciones de omisión de exones mediante el uso de crispr/cas9 con secuencias guía triples

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Publication number
DOP2019000179A
DOP2019000179A DO2019000179A DO2019000179A DOP2019000179A DO P2019000179 A DOP2019000179 A DO P2019000179A DO 2019000179 A DO2019000179 A DO 2019000179A DO 2019000179 A DO2019000179 A DO 2019000179A DO P2019000179 A DOP2019000179 A DO P2019000179A
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Dominican Republic
Prior art keywords
cas9
crispr
modifications
guide sequences
dmd
Prior art date
Application number
DO2019000179A
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English (en)
Spanish (es)
Inventor
Amoasii Leonela
Olson Eric
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Publication of DOP2019000179A publication Critical patent/DOP2019000179A/es

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DO2019000179A 2017-01-05 2019-07-05 Estrategia optimizada para modificaciones de omisión de exones mediante el uso de crispr/cas9 con secuencias guía triples DOP2019000179A (es)

Applications Claiming Priority (4)

Application Number Priority Date Filing Date Title
US201762442606P 2017-01-05 2017-01-05
US201762544449P 2017-08-11 2017-08-11
US201762596298P 2017-12-08 2017-12-08
PCT/US2018/012558 WO2018129296A1 (en) 2017-01-05 2018-01-05 Optimized strategy for exon skipping modifications using crispr/cas9 with triple guide sequences

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DOP2019000179A true DOP2019000179A (es) 2019-11-15

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DO2019000179A DOP2019000179A (es) 2017-01-05 2019-07-05 Estrategia optimizada para modificaciones de omisión de exones mediante el uso de crispr/cas9 con secuencias guía triples

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US (1) US20190338311A1 (enExample)
EP (1) EP3565897B1 (enExample)
JP (1) JP2020503869A (enExample)
KR (1) KR102606174B1 (enExample)
CN (1) CN110506115A (enExample)
AU (1) AU2018205521A1 (enExample)
BR (1) BR112019013962A2 (enExample)
CA (1) CA3048635A1 (enExample)
CL (1) CL2019001882A1 (enExample)
CO (1) CO2019008181A2 (enExample)
CR (1) CR20190326A (enExample)
DK (1) DK3565897T3 (enExample)
DO (1) DOP2019000179A (enExample)
EC (1) ECSP19056408A (enExample)
IL (1) IL267786A (enExample)
JO (1) JOP20190166A1 (enExample)
MA (1) MA47239A (enExample)
MX (1) MX2019008064A (enExample)
PE (1) PE20191357A1 (enExample)
PH (1) PH12019501561A1 (enExample)
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EP4479536A1 (en) * 2022-02-17 2024-12-25 The Board Of Regents Of The University Of Texas System Crispr/spcas9 variant and methods for enhanced correcton of duchenne muscular dystrophy mutations
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