CA3048635A1 - Optimized strategy for exon skipping modifications using crispr/cas9 with triple guide sequences - Google Patents

Optimized strategy for exon skipping modifications using crispr/cas9 with triple guide sequences Download PDF

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CA3048635A1
CA3048635A1 CA3048635A CA3048635A CA3048635A1 CA 3048635 A1 CA3048635 A1 CA 3048635A1 CA 3048635 A CA3048635 A CA 3048635A CA 3048635 A CA3048635 A CA 3048635A CA 3048635 A1 CA3048635 A1 CA 3048635A1
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sequence encoding
promoter
sequence
nucleic acid
vector
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Leonela AMOASII
Eric Olson
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University of Texas System
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University of Texas System
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CA3048635A 2017-01-05 2018-01-05 Optimized strategy for exon skipping modifications using crispr/cas9 with triple guide sequences Pending CA3048635A1 (en)

Applications Claiming Priority (7)

Application Number Priority Date Filing Date Title
US201762442606P 2017-01-05 2017-01-05
US62/442,606 2017-01-05
US201762544449P 2017-08-11 2017-08-11
US62/544,449 2017-08-11
US201762596298P 2017-12-08 2017-12-08
US62/596,298 2017-12-08
PCT/US2018/012558 WO2018129296A1 (en) 2017-01-05 2018-01-05 Optimized strategy for exon skipping modifications using crispr/cas9 with triple guide sequences

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CA3048635A1 true CA3048635A1 (en) 2018-07-12

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CA3048635A Pending CA3048635A1 (en) 2017-01-05 2018-01-05 Optimized strategy for exon skipping modifications using crispr/cas9 with triple guide sequences

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US (1) US20190338311A1 (enExample)
EP (1) EP3565897B1 (enExample)
JP (1) JP2020503869A (enExample)
KR (1) KR102606174B1 (enExample)
CN (1) CN110506115A (enExample)
AU (1) AU2018205521A1 (enExample)
BR (1) BR112019013962A2 (enExample)
CA (1) CA3048635A1 (enExample)
CL (1) CL2019001882A1 (enExample)
CO (1) CO2019008181A2 (enExample)
CR (1) CR20190326A (enExample)
DK (1) DK3565897T3 (enExample)
DO (1) DOP2019000179A (enExample)
EC (1) ECSP19056408A (enExample)
IL (1) IL267786A (enExample)
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MA (1) MA47239A (enExample)
MX (1) MX2019008064A (enExample)
PE (1) PE20191357A1 (enExample)
PH (1) PH12019501561A1 (enExample)
SG (1) SG11201906147VA (enExample)
WO (1) WO2018129296A1 (enExample)

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