KR102606174B1 - 트리플 가이드 서열을 지닌 crispr/cas9를 사용한 엑손 스키핑 변형을 위한 최적화된 전략 - Google Patents

트리플 가이드 서열을 지닌 crispr/cas9를 사용한 엑손 스키핑 변형을 위한 최적화된 전략 Download PDF

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KR102606174B1
KR102606174B1 KR1020197022753A KR20197022753A KR102606174B1 KR 102606174 B1 KR102606174 B1 KR 102606174B1 KR 1020197022753 A KR1020197022753 A KR 1020197022753A KR 20197022753 A KR20197022753 A KR 20197022753A KR 102606174 B1 KR102606174 B1 KR 102606174B1
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레오넬라 아모아시
에릭 올슨
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더 보드 오브 리젠츠 오브 더 유니버시티 오브 텍사스 시스템
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KR1020197022753A 2017-01-05 2018-01-05 트리플 가이드 서열을 지닌 crispr/cas9를 사용한 엑손 스키핑 변형을 위한 최적화된 전략 Active KR102606174B1 (ko)

Applications Claiming Priority (7)

Application Number Priority Date Filing Date Title
US201762442606P 2017-01-05 2017-01-05
US62/442,606 2017-01-05
US201762544449P 2017-08-11 2017-08-11
US62/544,449 2017-08-11
US201762596298P 2017-12-08 2017-12-08
US62/596,298 2017-12-08
PCT/US2018/012558 WO2018129296A1 (en) 2017-01-05 2018-01-05 Optimized strategy for exon skipping modifications using crispr/cas9 with triple guide sequences

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KR20190100967A KR20190100967A (ko) 2019-08-29
KR102606174B1 true KR102606174B1 (ko) 2023-11-27

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