CN115227709A - 用于在对象中调节smn2剪接的组合物和方法 - Google Patents

用于在对象中调节smn2剪接的组合物和方法 Download PDF

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Publication number
CN115227709A
CN115227709A CN202210540428.XA CN202210540428A CN115227709A CN 115227709 A CN115227709 A CN 115227709A CN 202210540428 A CN202210540428 A CN 202210540428A CN 115227709 A CN115227709 A CN 115227709A
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certain embodiments
subject
antisense
dose
administration
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Chinese (zh)
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C·F·班尼特
G·洪
F·里戈
A·R·克莱纳
Y·华
M·A·帕西尼
L·史哈布丁
S·H·程
K·W·克令格
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Bojian Massachusetts Co ltd
Cold Spring Harbor Laboratory
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Bojian Massachusetts Co ltd
Cold Spring Harbor Laboratory
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Application filed by Bojian Massachusetts Co ltd, Cold Spring Harbor Laboratory filed Critical Bojian Massachusetts Co ltd
Publication of CN115227709A publication Critical patent/CN115227709A/zh
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CN202210540428.XA 2009-06-17 2010-06-17 用于在对象中调节smn2剪接的组合物和方法 Pending CN115227709A (zh)

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Application Number Priority Date Filing Date Title
US21803109P 2009-06-17 2009-06-17
US61/218,031 2009-06-17
CN2010800368070A CN102665731A (zh) 2009-06-17 2010-06-17 用于在对象中调节smn2剪接的组合物和方法
PCT/US2010/039077 WO2010148249A1 (en) 2009-06-17 2010-06-17 Compositions and methods for modulation of smn2 splicing in a subject

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CN202210540428.XA Pending CN115227709A (zh) 2009-06-17 2010-06-17 用于在对象中调节smn2剪接的组合物和方法
CN2010800368070A Pending CN102665731A (zh) 2009-06-17 2010-06-17 用于在对象中调节smn2剪接的组合物和方法
CN201710003678.9A Active CN106983768B (zh) 2009-06-17 2010-06-17 用于在对象中调节smn2剪接的组合物和方法
CN202310217516.0A Pending CN116440150A (zh) 2009-06-17 2010-06-17 用于在对象中调节smn2剪接的组合物和方法
CN202210541466.7A Pending CN115227710A (zh) 2009-06-17 2010-06-17 用于在对象中调节smn2剪接的组合物和方法

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CN201710003678.9A Active CN106983768B (zh) 2009-06-17 2010-06-17 用于在对象中调节smn2剪接的组合物和方法
CN202310217516.0A Pending CN116440150A (zh) 2009-06-17 2010-06-17 用于在对象中调节smn2剪接的组合物和方法
CN202210541466.7A Pending CN115227710A (zh) 2009-06-17 2010-06-17 用于在对象中调节smn2剪接的组合物和方法

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US (5) US8980853B2 (OSRAM)
EP (4) EP3449926B1 (OSRAM)
JP (7) JP5707396B2 (OSRAM)
KR (8) KR20120093138A (OSRAM)
CN (5) CN115227709A (OSRAM)
AU (2) AU2010262862C1 (OSRAM)
CA (1) CA2765396C (OSRAM)
CY (2) CY1120807T1 (OSRAM)
DK (2) DK3449926T3 (OSRAM)
ES (2) ES2761614T3 (OSRAM)
HK (1) HK1246648B (OSRAM)
HR (2) HRP20181712T1 (OSRAM)
HU (2) HUE046966T2 (OSRAM)
IL (2) IL217014A (OSRAM)
LT (2) LT3305302T (OSRAM)
MX (3) MX361732B (OSRAM)
NO (1) NO2020008I1 (OSRAM)
NZ (2) NZ624712A (OSRAM)
PL (2) PL3449926T3 (OSRAM)
PT (2) PT3305302T (OSRAM)
RU (2) RU2683772C2 (OSRAM)
SI (2) SI3305302T1 (OSRAM)
SM (2) SMT202000020T1 (OSRAM)
TR (1) TR201816256T4 (OSRAM)
WO (1) WO2010148249A1 (OSRAM)

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