AU2020395113A1 - Therapeutic editing - Google Patents
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- AU2020395113A1 AU2020395113A1 AU2020395113A AU2020395113A AU2020395113A1 AU 2020395113 A1 AU2020395113 A1 AU 2020395113A1 AU 2020395113 A AU2020395113 A AU 2020395113A AU 2020395113 A AU2020395113 A AU 2020395113A AU 2020395113 A1 AU2020395113 A1 AU 2020395113A1
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Applications Claiming Priority (13)
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| US201962942667P | 2019-12-02 | 2019-12-02 | |
| US201962942693P | 2019-12-02 | 2019-12-02 | |
| US201962942683P | 2019-12-02 | 2019-12-02 | |
| US62/942,693 | 2019-12-02 | ||
| US62/942,683 | 2019-12-02 | ||
| US62/942,667 | 2019-12-02 | ||
| US202063022727P | 2020-05-11 | 2020-05-11 | |
| US63/022,727 | 2020-05-11 | ||
| US202063030165P | 2020-05-26 | 2020-05-26 | |
| US63/030,165 | 2020-05-26 | ||
| US202063112286P | 2020-11-11 | 2020-11-11 | |
| US63/112,286 | 2020-11-11 | ||
| PCT/US2020/062756 WO2021113270A1 (en) | 2019-12-02 | 2020-12-01 | Therapeutic editing |
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| AU2020395113A1 true AU2020395113A1 (en) | 2022-06-09 |
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| JP (1) | JP2023504314A (https=) |
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| AU (1) | AU2020395113A1 (https=) |
| CA (1) | CA3159944A1 (https=) |
| WO (1) | WO2021113270A1 (https=) |
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| GB201808146D0 (en) | 2018-05-18 | 2018-07-11 | Proqr Therapeutics Ii Bv | Stereospecific Linkages in RNA Editing Oligonucleotides |
| WO2021113270A1 (en) | 2019-12-02 | 2021-06-10 | Shape Therapeutics Inc. | Therapeutic editing |
| MX2022006991A (es) * | 2019-12-09 | 2022-08-25 | Astellas Pharma Inc | Arn guía antisentido con región funcional añadida para editar arn blanco. |
| CN115777020A (zh) * | 2020-04-22 | 2023-03-10 | 塑造治疗公司 | 使用snrna组分的组合物和方法 |
| WO2022103852A1 (en) * | 2020-11-11 | 2022-05-19 | Shape Therapeutics Inc. | Rna-editing compositions and methods of use |
| EP4359525A1 (en) * | 2021-06-21 | 2024-05-01 | uniQure biopharma B.V. | Gene constructs for silencing alpha-synuclein and uses thereof |
| WO2023278436A1 (en) * | 2021-06-29 | 2023-01-05 | Shape Therapeutics Inc. | Engineered guide rnas and polynucleotides |
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| WO2023020574A1 (en) * | 2021-08-18 | 2023-02-23 | Peking University | Engineered adar-recruiting rnas and methods of use thereof |
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