SG10201909381WA - Production of oversized adeno-associated vectors - Google Patents

Production of oversized adeno-associated vectors

Info

Publication number
SG10201909381WA
SG10201909381WA SG10201909381WA SG10201909381WA SG 10201909381W A SG10201909381W A SG 10201909381WA SG 10201909381W A SG10201909381W A SG 10201909381WA SG 10201909381W A SG10201909381W A SG 10201909381WA
Authority
SG
Singapore
Prior art keywords
oversized
adeno
aav
production
associated vectors
Prior art date
Application number
Other languages
English (en)
Inventor
Sirkka Kyostio-Moore
David Souza
Karen Vincent
Original Assignee
Genzyme Corp
Priority date (The priority date is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the date listed.)
Filing date
Publication date
Family has litigation
First worldwide family litigation filed litigation Critical https://patents.darts-ip.com/?family=56943906&utm_source=google_patent&utm_medium=platform_link&utm_campaign=public_patent_search&patent=SG10201909381W(A) "Global patent litigation dataset” by Darts-ip is licensed under a Creative Commons Attribution 4.0 International License.
Application filed by Genzyme Corp filed Critical Genzyme Corp
Publication of SG10201909381WA publication Critical patent/SG10201909381WA/en

Links

Classifications

    • A—HUMAN NECESSITIES
    • A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61K—PREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
    • A61K38/00—Medicinal preparations containing peptides
    • A61K38/16—Peptides having more than 20 amino acids; Gastrins; Somatostatins; Melanotropins; Derivatives thereof
    • A61K38/17—Peptides having more than 20 amino acids; Gastrins; Somatostatins; Melanotropins; Derivatives thereof from animals; from humans
    • A61K38/1703—Peptides having more than 20 amino acids; Gastrins; Somatostatins; Melanotropins; Derivatives thereof from animals; from humans from vertebrates
    • A61K38/1709—Peptides having more than 20 amino acids; Gastrins; Somatostatins; Melanotropins; Derivatives thereof from animals; from humans from vertebrates from mammals
    • A—HUMAN NECESSITIES
    • A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61P—SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
    • A61P11/00—Drugs for disorders of the respiratory system
    • A—HUMAN NECESSITIES
    • A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61P—SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
    • A61P21/00—Drugs for disorders of the muscular or neuromuscular system
    • C—CHEMISTRY; METALLURGY
    • C07—ORGANIC CHEMISTRY
    • C07K—PEPTIDES
    • C07K14/00—Peptides having more than 20 amino acids; Gastrins; Somatostatins; Melanotropins; Derivatives thereof
    • C07K14/435—Peptides having more than 20 amino acids; Gastrins; Somatostatins; Melanotropins; Derivatives thereof from animals; from humans
    • C07K14/745—Blood coagulation or fibrinolysis factors
    • C07K14/755—Factors VIII, e.g. factor VIII C (AHF), factor VIII Ag (VWF)
    • C—CHEMISTRY; METALLURGY
    • C12—BIOCHEMISTRY; BEER; SPIRITS; WINE; VINEGAR; MICROBIOLOGY; ENZYMOLOGY; MUTATION OR GENETIC ENGINEERING
    • C12N—MICROORGANISMS OR ENZYMES; COMPOSITIONS THEREOF; PROPAGATING, PRESERVING, OR MAINTAINING MICROORGANISMS; MUTATION OR GENETIC ENGINEERING; CULTURE MEDIA
    • C12N15/00—Mutation or genetic engineering; DNA or RNA concerning genetic engineering, vectors, e.g. plasmids, or their isolation, preparation or purification; Use of hosts therefor
    • C12N15/09—Recombinant DNA-technology
    • C12N15/63—Introduction of foreign genetic material using vectors; Vectors; Use of hosts therefor; Regulation of expression
    • C12N15/79—Vectors or expression systems specially adapted for eukaryotic hosts
    • C12N15/85—Vectors or expression systems specially adapted for eukaryotic hosts for animal cells
    • C12N15/86—Viral vectors
    • C—CHEMISTRY; METALLURGY
    • C12—BIOCHEMISTRY; BEER; SPIRITS; WINE; VINEGAR; MICROBIOLOGY; ENZYMOLOGY; MUTATION OR GENETIC ENGINEERING
    • C12N—MICROORGANISMS OR ENZYMES; COMPOSITIONS THEREOF; PROPAGATING, PRESERVING, OR MAINTAINING MICROORGANISMS; MUTATION OR GENETIC ENGINEERING; CULTURE MEDIA
    • C12N7/00—Viruses; Bacteriophages; Compositions thereof; Preparation or purification thereof
    • C—CHEMISTRY; METALLURGY
    • C12—BIOCHEMISTRY; BEER; SPIRITS; WINE; VINEGAR; MICROBIOLOGY; ENZYMOLOGY; MUTATION OR GENETIC ENGINEERING
    • C12N—MICROORGANISMS OR ENZYMES; COMPOSITIONS THEREOF; PROPAGATING, PRESERVING, OR MAINTAINING MICROORGANISMS; MUTATION OR GENETIC ENGINEERING; CULTURE MEDIA
    • C12N2710/00—MICROORGANISMS OR ENZYMES; COMPOSITIONS THEREOF; PROPAGATING, PRESERVING, OR MAINTAINING MICROORGANISMS; MUTATION OR GENETIC ENGINEERING; CULTURE MEDIA dsDNA viruses
    • C12N2710/00011—Details
    • C12N2710/10011—Adenoviridae
    • C12N2710/10041—Use of virus, viral particle or viral elements as a vector
    • C—CHEMISTRY; METALLURGY
    • C12—BIOCHEMISTRY; BEER; SPIRITS; WINE; VINEGAR; MICROBIOLOGY; ENZYMOLOGY; MUTATION OR GENETIC ENGINEERING
    • C12N—MICROORGANISMS OR ENZYMES; COMPOSITIONS THEREOF; PROPAGATING, PRESERVING, OR MAINTAINING MICROORGANISMS; MUTATION OR GENETIC ENGINEERING; CULTURE MEDIA
    • C12N2750/00—MICROORGANISMS OR ENZYMES; COMPOSITIONS THEREOF; PROPAGATING, PRESERVING, OR MAINTAINING MICROORGANISMS; MUTATION OR GENETIC ENGINEERING; CULTURE MEDIA ssDNA viruses
    • C12N2750/00011—Details
    • C12N2750/14011—Parvoviridae
    • C12N2750/14111—Dependovirus, e.g. adenoassociated viruses
    • C12N2750/14141—Use of virus, viral particle or viral elements as a vector
    • C12N2750/14143—Use of virus, viral particle or viral elements as a vector viral genome or elements thereof as genetic vector
    • C—CHEMISTRY; METALLURGY
    • C12—BIOCHEMISTRY; BEER; SPIRITS; WINE; VINEGAR; MICROBIOLOGY; ENZYMOLOGY; MUTATION OR GENETIC ENGINEERING
    • C12N—MICROORGANISMS OR ENZYMES; COMPOSITIONS THEREOF; PROPAGATING, PRESERVING, OR MAINTAINING MICROORGANISMS; MUTATION OR GENETIC ENGINEERING; CULTURE MEDIA
    • C12N2750/00—MICROORGANISMS OR ENZYMES; COMPOSITIONS THEREOF; PROPAGATING, PRESERVING, OR MAINTAINING MICROORGANISMS; MUTATION OR GENETIC ENGINEERING; CULTURE MEDIA ssDNA viruses
    • C12N2750/00011—Details
    • C12N2750/14011—Parvoviridae
    • C12N2750/14111—Dependovirus, e.g. adenoassociated viruses
    • C12N2750/14151—Methods of production or purification of viral material
    • C12N2750/14152—Methods of production or purification of viral material relating to complementing cells and packaging systems for producing virus or viral particles

Landscapes

  • Health & Medical Sciences (AREA)
  • Life Sciences & Earth Sciences (AREA)
  • Chemical & Material Sciences (AREA)
  • Organic Chemistry (AREA)
  • Genetics & Genomics (AREA)
  • Engineering & Computer Science (AREA)
  • Bioinformatics & Cheminformatics (AREA)
  • Zoology (AREA)
  • General Health & Medical Sciences (AREA)
  • Wood Science & Technology (AREA)
  • Medicinal Chemistry (AREA)
  • Biotechnology (AREA)
  • General Engineering & Computer Science (AREA)
  • Biomedical Technology (AREA)
  • Biochemistry (AREA)
  • Molecular Biology (AREA)
  • Biophysics (AREA)
  • Microbiology (AREA)
  • Virology (AREA)
  • Pharmacology & Pharmacy (AREA)
  • Veterinary Medicine (AREA)
  • Public Health (AREA)
  • Animal Behavior & Ethology (AREA)
  • Proteomics, Peptides & Aminoacids (AREA)
  • Immunology (AREA)
  • Gastroenterology & Hepatology (AREA)
  • Nuclear Medicine, Radiotherapy & Molecular Imaging (AREA)
  • Chemical Kinetics & Catalysis (AREA)
  • General Chemical & Material Sciences (AREA)
  • Plant Pathology (AREA)
  • Physics & Mathematics (AREA)
  • Hematology (AREA)
  • Toxicology (AREA)
  • Neurology (AREA)
  • Epidemiology (AREA)
  • Orthopedic Medicine & Surgery (AREA)
  • Marine Sciences & Fisheries (AREA)
  • Physical Education & Sports Medicine (AREA)
  • Pulmonology (AREA)
  • Micro-Organisms Or Cultivation Processes Thereof (AREA)
SG10201909381W 2015-04-08 2016-04-07 Production of oversized adeno-associated vectors SG10201909381WA (en)

Applications Claiming Priority (2)

Application Number Priority Date Filing Date Title
US201562144862P 2015-04-08 2015-04-08
US201562220067P 2015-09-17 2015-09-17

Publications (1)

Publication Number Publication Date
SG10201909381WA true SG10201909381WA (en) 2019-11-28

Family

ID=56943906

Family Applications (3)

Application Number Title Priority Date Filing Date
SG10201909381W SG10201909381WA (en) 2015-04-08 2016-04-07 Production of oversized adeno-associated vectors
SG10201912912QA SG10201912912QA (en) 2015-04-08 2016-04-07 Production of oversized adeno-associated vectors
SG11201708203UA SG11201708203UA (en) 2015-04-08 2016-04-07 Production of oversized adeno-associated vectors

Family Applications After (2)

Application Number Title Priority Date Filing Date
SG10201912912QA SG10201912912QA (en) 2015-04-08 2016-04-07 Production of oversized adeno-associated vectors
SG11201708203UA SG11201708203UA (en) 2015-04-08 2016-04-07 Production of oversized adeno-associated vectors

Country Status (27)

Country Link
US (1) US10815497B2 (https=)
EP (2) EP3280799B1 (https=)
JP (3) JP6878299B2 (https=)
KR (2) KR20250126875A (https=)
CN (1) CN107864657A (https=)
AU (3) AU2016245806A1 (https=)
BR (1) BR112017021505A2 (https=)
CA (1) CA2982123A1 (https=)
CL (1) CL2017002537A1 (https=)
CO (1) CO2017011344A2 (https=)
CR (1) CR20170505A (https=)
DK (1) DK3280799T3 (https=)
EA (1) EA201792236A1 (https=)
EC (1) ECSP17074016A (https=)
ES (1) ES3008382T3 (https=)
GT (1) GT201700214A (https=)
HU (1) HUE069779T2 (https=)
IL (3) IL294965A (https=)
MX (1) MX2017012935A (https=)
PE (1) PE20171800A1 (https=)
PH (1) PH12017501836A1 (https=)
PL (1) PL3280799T3 (https=)
SG (3) SG10201909381WA (https=)
TN (1) TN2017000431A1 (https=)
TW (1) TWI707951B (https=)
UY (1) UY36611A (https=)
WO (1) WO2016164609A2 (https=)

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IL254933B (en) 2021-06-30
JP2018510648A (ja) 2018-04-19
KR20170133500A (ko) 2017-12-05
MX2017012935A (es) 2018-02-12
UY36611A (es) 2016-11-30
PL3280799T3 (pl) 2025-04-14
SG10201912912QA (en) 2020-02-27
WO2016164609A2 (en) 2016-10-13
EP3280799B1 (en) 2024-10-30
KR102848324B1 (ko) 2025-08-20
IL254933A0 (en) 2017-12-31
AU2022203942A1 (en) 2022-06-23
CR20170505A (es) 2018-01-26
US10815497B2 (en) 2020-10-27
BR112017021505A2 (pt) 2018-07-03
ECSP17074016A (es) 2018-02-28
HUE069779T2 (hu) 2025-04-28
CN107864657A (zh) 2018-03-30
IL294965A (en) 2022-09-01
JP6878299B2 (ja) 2021-05-26
AU2022203942B2 (en) 2023-12-14
CO2017011344A2 (es) 2018-03-28
CL2017002537A1 (es) 2018-05-11
CA2982123A1 (en) 2016-10-13
NZ774736A (en) 2024-08-30
EA201792236A1 (ru) 2018-03-30
PH12017501836A1 (en) 2018-04-23
GT201700214A (es) 2018-10-24
US20190048362A1 (en) 2019-02-14
TWI707951B (zh) 2020-10-21
EP4512429A2 (en) 2025-02-26
JP2023116678A (ja) 2023-08-22
DK3280799T3 (da) 2025-01-27
IL283291B (en) 2022-08-01
SG11201708203UA (en) 2017-11-29
HK1246339A1 (en) 2018-09-07
WO2016164609A3 (en) 2016-12-15
ES3008382T3 (en) 2025-03-24
KR20250126875A (ko) 2025-08-25
NZ737009A (en) 2024-01-26
EP3280799A2 (en) 2018-02-14
EP4512429A3 (en) 2025-05-21
TW201710498A (zh) 2017-03-16
IL283291A (en) 2021-07-29
PE20171800A1 (es) 2017-12-28
AU2024201619A1 (en) 2024-03-28
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TN2017000431A1 (en) 2019-04-12
JP2021118724A (ja) 2021-08-12

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