SA519401379B1 - علاج فيروس مرتبط بغدة لمرض هنتنجتون - Google Patents

علاج فيروس مرتبط بغدة لمرض هنتنجتون

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Publication number
SA519401379B1
SA519401379B1 SA519401379A SA519401379A SA519401379B1 SA 519401379 B1 SA519401379 B1 SA 519401379B1 SA 519401379 A SA519401379 A SA 519401379A SA 519401379 A SA519401379 A SA 519401379A SA 519401379 B1 SA519401379 B1 SA 519401379B1
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Saudi Arabia
Prior art keywords
disease
huntington
adeno
associated virus
virus treatment
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SA519401379A
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English (en)
Inventor
نيل ارونين
اديث ال بفيستير
كريستيان مويلير
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يونيفيرسيتى اوف ماساشوسيتس
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Application filed by يونيفيرسيتى اوف ماساشوسيتس filed Critical يونيفيرسيتى اوف ماساشوسيتس
Publication of SA519401379B1 publication Critical patent/SA519401379B1/ar

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    • C12N2750/14011—Parvoviridae
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    • C12N2800/10—Plasmid DNA
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  • Health & Medical Sciences (AREA)
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Abstract

يتعلق الكشف الحالي بتركيبات وطرق مفيدة لمعالجة مرض هنتنجتون Huntington's disease. في بعض النماذج، يوفر الكشف الحالي أحماض نووية تداخلية interfering nucleic acids (على سبيل المثال، أحماض ريبوزية نووية ميكروية micro Ribonucleic acids (miRNAs)) والتي تستهدف جين هنتنجتون huntingtin gene (htt) وطرق لمعالجة مرض هنتنجتون باستخدام تلك الأحماض. شكل1
SA519401379A 2016-09-22 2019-03-21 علاج فيروس مرتبط بغدة لمرض هنتنجتون SA519401379B1 (ar)

Applications Claiming Priority (2)

Application Number Priority Date Filing Date Title
US201662398487P 2016-09-22 2016-09-22
PCT/US2017/052902 WO2018057855A1 (en) 2016-09-22 2017-09-22 Aav treatment of huntington's disease

Publications (1)

Publication Number Publication Date
SA519401379B1 true SA519401379B1 (ar) 2022-08-07

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ID=61691085

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SA519401379A SA519401379B1 (ar) 2016-09-22 2019-03-21 علاج فيروس مرتبط بغدة لمرض هنتنجتون

Country Status (18)

Country Link
US (4) US10457940B2 (ar)
EP (1) EP3515505A4 (ar)
JP (3) JP6884430B2 (ar)
KR (1) KR102271675B1 (ar)
CN (2) CN110035776B (ar)
AU (1) AU2017330411B2 (ar)
BR (2) BR122020019033B1 (ar)
CA (1) CA3037929A1 (ar)
CL (1) CL2019000732A1 (ar)
CO (1) CO2019003846A2 (ar)
IL (2) IL265528B2 (ar)
MX (2) MX2019003376A (ar)
MY (1) MY195386A (ar)
PE (1) PE20191351A1 (ar)
PH (1) PH12019500626A1 (ar)
RU (1) RU2749971C2 (ar)
SA (1) SA519401379B1 (ar)
WO (1) WO2018057855A1 (ar)

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TW202132567A (zh) * 2019-11-01 2021-09-01 美商阿尼拉製藥公司 亨汀頓蛋白（ＨＴＴ）ｉＲＮＡ劑組成物及其使用方法
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