KR20230161535A - 신규 아데노-관련 바이러스 캡시드 단백질 - Google Patents

신규 아데노-관련 바이러스 캡시드 단백질 Download PDF

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KR20230161535A
KR20230161535A KR1020237039466A KR20237039466A KR20230161535A KR 20230161535 A KR20230161535 A KR 20230161535A KR 1020237039466 A KR1020237039466 A KR 1020237039466A KR 20237039466 A KR20237039466 A KR 20237039466A KR 20230161535 A KR20230161535 A KR 20230161535A
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피터 카메론 콜로시
마이클 로취리
로버트 엔지
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바이오마린 파머수티컬 인크.
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    • C12N15/63Introduction of foreign genetic material using vectors; Vectors; Use of hosts therefor; Regulation of expression
    • C12N15/79Vectors or expression systems specially adapted for eukaryotic hosts
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    • C12N15/86Viral vectors
    • AHUMAN NECESSITIES
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    • A61MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61PSPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
    • A61P21/00Drugs for disorders of the muscular or neuromuscular system
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    • C07K14/435Peptides having more than 20 amino acids; Gastrins; Somatostatins; Melanotropins; Derivatives thereof from animals; from humans
    • C07K14/46Peptides having more than 20 amino acids; Gastrins; Somatostatins; Melanotropins; Derivatives thereof from animals; from humans from vertebrates
    • C07K14/47Peptides having more than 20 amino acids; Gastrins; Somatostatins; Melanotropins; Derivatives thereof from animals; from humans from vertebrates from mammals
    • C07K14/4701Peptides having more than 20 amino acids; Gastrins; Somatostatins; Melanotropins; Derivatives thereof from animals; from humans from vertebrates from mammals not used
    • C07K14/4707Muscular dystrophy
    • AHUMAN NECESSITIES
    • A61MEDICAL OR VETERINARY SCIENCE; HYGIENE
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    • C12N2750/14011Parvoviridae
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    • C12N2750/00011Details
    • C12N2750/14011Parvoviridae
    • C12N2750/14111Dependovirus, e.g. adenoassociated viruses
    • C12N2750/14141Use of virus, viral particle or viral elements as a vector
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    • C12N2750/00011Details
    • C12N2750/14011Parvoviridae
    • C12N2750/14111Dependovirus, e.g. adenoassociated viruses
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    • C12N2750/14011Parvoviridae
    • C12N2750/14111Dependovirus, e.g. adenoassociated viruses
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    • C12N2799/00Uses of viruses
    • C12N2799/02Uses of viruses as vector
    • C12N2799/021Uses of viruses as vector for the expression of a heterologous nucleic acid
    • C12N2799/025Uses of viruses as vector for the expression of a heterologous nucleic acid where the vector is derived from a parvovirus

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  • Animal Behavior & Ethology (AREA)
  • Pharmacology & Pharmacy (AREA)
  • Veterinary Medicine (AREA)
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  • Proteomics, Peptides & Aminoacids (AREA)
  • Gastroenterology & Hepatology (AREA)
  • Microbiology (AREA)
  • Physics & Mathematics (AREA)
  • Plant Pathology (AREA)
  • Orthopedic Medicine & Surgery (AREA)
  • Nuclear Medicine, Radiotherapy & Molecular Imaging (AREA)
  • General Chemical & Material Sciences (AREA)
  • Chemical Kinetics & Catalysis (AREA)
  • Physical Education & Sports Medicine (AREA)
  • Neurology (AREA)
  • Epidemiology (AREA)
  • Toxicology (AREA)
  • Micro-Organisms Or Cultivation Processes Thereof (AREA)
  • Medicines Containing Material From Animals Or Micro-Organisms (AREA)
  • Peptides Or Proteins (AREA)
  • Medicines That Contain Protein Lipid Enzymes And Other Medicines (AREA)
  • Saccharide Compounds (AREA)
KR1020237039466A 2016-07-26 2017-07-25 신규 아데노-관련 바이러스 캡시드 단백질 Abandoned KR20230161535A (ko)

Applications Claiming Priority (4)

Application Number Priority Date Filing Date Title
US201662366838P 2016-07-26 2016-07-26
US62/366,838 2016-07-26
KR1020197001930A KR102604510B1 (ko) 2016-07-26 2017-07-25 신규 아데노-관련 바이러스 캡시드 단백질
PCT/US2017/043703 WO2018022608A2 (en) 2016-07-26 2017-07-25 Novel adeno-associated virus capsid proteins

Related Parent Applications (1)

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KR1020197001930A Division KR102604510B1 (ko) 2016-07-26 2017-07-25 신규 아데노-관련 바이러스 캡시드 단백질

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KR20230161535A true KR20230161535A (ko) 2023-11-27

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KR1020237039466A Abandoned KR20230161535A (ko) 2016-07-26 2017-07-25 신규 아데노-관련 바이러스 캡시드 단백질
KR1020197001930A Active KR102604510B1 (ko) 2016-07-26 2017-07-25 신규 아데노-관련 바이러스 캡시드 단백질

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Country Status (15)

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US (3) US11584780B2 (enExample)
EP (1) EP3491008A2 (enExample)
JP (4) JP6994018B2 (enExample)
KR (2) KR20230161535A (enExample)
CN (1) CN109715650B (enExample)
AU (2) AU2017301600B2 (enExample)
BR (1) BR112019001532A2 (enExample)
CA (1) CA3031026A1 (enExample)
CL (6) CL2019000167A1 (enExample)
IL (2) IL305149A (enExample)
MX (1) MX2019000962A (enExample)
PE (1) PE20190401A1 (enExample)
PH (1) PH12019500068A1 (enExample)
SG (1) SG11201811603WA (enExample)
WO (1) WO2018022608A2 (enExample)

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