JPWO2020252129A5 - - Google Patents

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Publication number
JPWO2020252129A5
JPWO2020252129A5 JP2021573404A JP2021573404A JPWO2020252129A5 JP WO2020252129 A5 JPWO2020252129 A5 JP WO2020252129A5 JP 2021573404 A JP2021573404 A JP 2021573404A JP 2021573404 A JP2021573404 A JP 2021573404A JP WO2020252129 A5 JPWO2020252129 A5 JP WO2020252129A5
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JP
Japan
Prior art keywords
patient
medicament according
miglastat
administered
medicament
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Application number
JP2021573404A
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English (en)
Japanese (ja)
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JP7677910B2 (ja
JP2022536687A (ja
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Priority claimed from PCT/US2020/037174 external-priority patent/WO2020252129A1/en
Publication of JP2022536687A publication Critical patent/JP2022536687A/ja
Publication of JPWO2020252129A5 publication Critical patent/JPWO2020252129A5/ja
Priority to JP2025076158A priority Critical patent/JP2025131572A/ja
Application granted granted Critical
Publication of JP7677910B2 publication Critical patent/JP7677910B2/ja
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JP2021573404A 2019-06-11 2020-06-11 腎機能障害を有する患者のファブリー病を治療する方法 Active JP7677910B2 (ja)

Priority Applications (1)

Application Number Priority Date Filing Date Title
JP2025076158A JP2025131572A (ja) 2019-06-11 2025-05-01 腎機能障害を有する患者のファブリー病を治療する方法

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201962859904P 2019-06-11 2019-06-11
US62/859,904 2019-06-11
PCT/US2020/037174 WO2020252129A1 (en) 2019-06-11 2020-06-11 Methods of treating fabry disease in patients having renal impairment

Related Child Applications (1)

Application Number Title Priority Date Filing Date
JP2025076158A Division JP2025131572A (ja) 2019-06-11 2025-05-01 腎機能障害を有する患者のファブリー病を治療する方法

Publications (3)

Publication Number Publication Date
JP2022536687A JP2022536687A (ja) 2022-08-18
JPWO2020252129A5 true JPWO2020252129A5 (enExample) 2023-06-20
JP7677910B2 JP7677910B2 (ja) 2025-05-15

Family

ID=71950725

Family Applications (2)

Application Number Title Priority Date Filing Date
JP2021573404A Active JP7677910B2 (ja) 2019-06-11 2020-06-11 腎機能障害を有する患者のファブリー病を治療する方法
JP2025076158A Pending JP2025131572A (ja) 2019-06-11 2025-05-01 腎機能障害を有する患者のファブリー病を治療する方法

Family Applications After (1)

Application Number Title Priority Date Filing Date
JP2025076158A Pending JP2025131572A (ja) 2019-06-11 2025-05-01 腎機能障害を有する患者のファブリー病を治療する方法

Country Status (16)

Country Link
US (1) US20220313670A1 (enExample)
EP (1) EP3982962A1 (enExample)
JP (2) JP7677910B2 (enExample)
KR (1) KR20220019796A (enExample)
CN (1) CN114423427A (enExample)
AR (1) AR120055A1 (enExample)
AU (1) AU2020291002A1 (enExample)
BR (1) BR112021024886A2 (enExample)
CA (1) CA3141226A1 (enExample)
CL (1) CL2021003280A1 (enExample)
EA (1) EA202290024A1 (enExample)
IL (1) IL288677A (enExample)
MX (1) MX2021015352A (enExample)
PH (1) PH12021553102A1 (enExample)
TW (1) TW202112372A (enExample)
WO (1) WO2020252129A1 (enExample)

Families Citing this family (6)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
PL2533050T6 (pl) 2006-05-16 2016-05-31 Amicus Therapeutics Inc Możliwości leczenia choroby Fabry'ego
DK3470077T3 (da) 2008-02-12 2020-11-30 Amicus Therapeutics Inc Fremgangsmåde til forudsigelse af respons på behandling af sygdomme med farmakologiske chaperoner
CA3224546A1 (en) 2017-05-30 2018-12-06 Jeff Castelli Use of migalastat in the treatment of fabry patients having renal impairment
JP7555818B2 (ja) 2018-02-06 2024-09-25 アミカス セラピューティックス インコーポレイテッド 妊娠患者におけるファブリー病の治療のためのミガラスタットの使用
KR20220044560A (ko) 2019-08-07 2022-04-08 아미쿠스 세라퓨틱스, 인코포레이티드 Gla 유전자에 돌연변이를 갖는 환자에서 파브리 질병을 치료하는 방법
US11623916B2 (en) 2020-12-16 2023-04-11 Amicus Therapeutics, Inc. Highly purified batches of pharmaceutical grade migalastat and methods of producing the same

Family Cites Families (10)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US6274597B1 (en) 1998-06-01 2001-08-14 Mount Sinai School Of Medicine Of New York University Method of enhancing lysosomal α-Galactosidase A
AU2008232614A1 (en) 2007-03-30 2008-10-09 Amicus Therapeutics, Inc. Method for the treatment of Fabry disease using pharmacological chaperones
US9056101B2 (en) * 2007-04-26 2015-06-16 Amicus Therapeutics, Inc. Dosing regimens for the treatment of lysosomal storage diseases using pharmacological chaperones
DK3470077T3 (da) 2008-02-12 2020-11-30 Amicus Therapeutics Inc Fremgangsmåde til forudsigelse af respons på behandling af sygdomme med farmakologiske chaperoner
SG193379A1 (en) * 2011-03-11 2013-10-30 Amicus Therapeutics Inc Dosing regimens for the treatment of fabry disease
IL313907A (en) * 2016-07-19 2024-08-01 Amicus Therapeutics Inc Treatment of Fabry disease in patients experienced with ERT-NAIVE and ERT
MX2019008076A (es) * 2017-01-05 2019-08-29 Protalix Ltd Regimen terapeutico para el tratamiento de fabry usando alfa-galactosidasa estabilizada.
CA3224546A1 (en) * 2017-05-30 2018-12-06 Jeff Castelli Use of migalastat in the treatment of fabry patients having renal impairment
AR111971A1 (es) * 2017-05-30 2019-09-04 Amicus Therapeutics Inc Métodos para tratar pacientes con enfermedad de fabry que tienen insuficiencia renal
HUE069837T2 (hu) * 2017-05-30 2025-04-28 Amicus Therapeutics Inc Bizonyos mutációkat hordozó Fabry-kóros betegek kezelése

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