JP7042255B2 - ヒトｌｍｎａを標的にするオリゴヌクレオチド類縁体 - Google Patents

ヒトｌｍｎａを標的にするオリゴヌクレオチド類縁体 Download PDF

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JP7042255B2
JP7042255B2 JP2019508165A JP2019508165A JP7042255B2 JP 7042255 B2 JP7042255 B2 JP 7042255B2 JP 2019508165 A JP2019508165 A JP 2019508165A JP 2019508165 A JP2019508165 A JP 2019508165A JP 7042255 B2 JP7042255 B2 JP 7042255B2
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oligomers
oligomer
sequence
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JP2019514426A (ja
JP2019514426A5 (https=
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マイケル アール． エルドス，
フランシス エス． コリンズ，
カン カオ，
リシャルド コール，
リチャード キース ベストウィック，
レスリー ビー． ゴードン，
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US Department of Health and Human Services
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    • C12N2310/318—Chemical structure of the backbone where the PO2 is completely replaced, e.g. MMI or formacetal
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    • C12N2320/30—Special therapeutic applications
    • C12N2320/33—Alteration of splicing

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  • Nuclear Medicine, Radiotherapy & Molecular Imaging (AREA)
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JP2019508165A 2016-04-29 2017-04-28 ヒトｌｍｎａを標的にするオリゴヌクレオチド類縁体 Active JP7042255B2 (ja)

Priority Applications (1)

Application Number Priority Date Filing Date Title
JP2022000125A JP2022046725A (ja) 2016-04-29 2022-01-04 ヒトｌｍｎａを標的にするオリゴヌクレオチド類縁体

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Application Number Priority Date Filing Date Title
US201662330027P 2016-04-29 2016-04-29
US62/330,027 2016-04-29
PCT/US2017/030174 WO2017190041A1 (en) 2016-04-29 2017-04-28 Oligonucleotide analogues targeting human lmna

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JP2019514426A JP2019514426A (ja) 2019-06-06
JP2019514426A5 JP2019514426A5 (https=) 2020-05-21
JP7042255B2 true JP7042255B2 (ja) 2022-03-25

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JP2022000125A Pending JP2022046725A (ja) 2016-04-29 2022-01-04 ヒトｌｍｎａを標的にするオリゴヌクレオチド類縁体

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US (2) US10822608B2 (https=)
EP (1) EP3449000A1 (https=)
JP (2) JP7042255B2 (https=)
KR (1) KR102329187B1 (https=)
CN (1) CN109477109B (https=)
AU (2) AU2017258642B2 (https=)
CA (1) CA3022303A1 (https=)
CO (1) CO2018012873A2 (https=)
EA (1) EA201892467A1 (https=)
MA (1) MA45616A (https=)
MX (1) MX2018013157A (https=)
NZ (1) NZ747685A (https=)
SG (1) SG11201809468XA (https=)
WO (1) WO2017190041A1 (https=)

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