JP2025514313A5 - - Google Patents

Info

Publication number
JP2025514313A5
JP2025514313A5 JP2024563594A JP2024563594A JP2025514313A5 JP 2025514313 A5 JP2025514313 A5 JP 2025514313A5 JP 2024563594 A JP2024563594 A JP 2024563594A JP 2024563594 A JP2024563594 A JP 2024563594A JP 2025514313 A5 JP2025514313 A5 JP 2025514313A5
Authority
JP
Japan
Prior art keywords
aav
raav
nucleic acid
expression vector
fviii
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2024563594A
Other languages
English (en)
Japanese (ja)
Other versions
JP2025514313A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/RU2023/050094 external-priority patent/WO2023211316A1/en
Publication of JP2025514313A publication Critical patent/JP2025514313A/ja
Publication of JP2025514313A5 publication Critical patent/JP2025514313A5/ja
Pending legal-status Critical Current

Links

JP2024563594A 2022-04-28 2023-04-18 Fviii-bddをコードするコドン最適化型核酸 Pending JP2025514313A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
RU2022111734A RU2808564C2 (ru) 2022-04-28 Кодон-оптимизированная нуклеиновая кислота, которая кодирует белок фактора свёртывания крови VIII c делетированным B доменом, и ее применение
RU2022111734 2022-04-28
PCT/RU2023/050094 WO2023211316A1 (en) 2022-04-28 2023-04-18 Codon-optimized nucleic acid encoding the fviii-bdd

Publications (2)

Publication Number Publication Date
JP2025514313A JP2025514313A (ja) 2025-05-02
JP2025514313A5 true JP2025514313A5 (https=) 2026-04-28

Family

ID=88482201

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2024563594A Pending JP2025514313A (ja) 2022-04-28 2023-04-18 Fviii-bddをコードするコドン最適化型核酸

Country Status (20)

Country Link
US (1) US20250282847A1 (https=)
EP (1) EP4514836A1 (https=)
JP (1) JP2025514313A (https=)
KR (1) KR20250007615A (https=)
CN (1) CN116970629A (https=)
AR (1) AR129163A1 (https=)
AU (1) AU2023261338A1 (https=)
CA (1) CA3250665A1 (https=)
CL (1) CL2024003296A1 (https=)
CO (1) CO2024014690A2 (https=)
CR (1) CR20240524A (https=)
IL (1) IL316584A (https=)
JO (1) JOP20240241A1 (https=)
MA (1) MA68586A1 (https=)
MX (1) MX2024013280A (https=)
PE (1) PE20251838A1 (https=)
PY (1) PY2331315A (https=)
TW (1) TW202346601A (https=)
UY (1) UY40241A (https=)
WO (1) WO2023211316A1 (https=)

Family Cites Families (3)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
PE20231949A1 (es) * 2015-10-30 2023-12-05 Spark Therapeutics Inc VARIANTES DEL FACTOR VIII REDUCIDO CON CpG, COMPOSICIONES Y METODOS Y USOS PARA EL TRATAMIENTO DE TRASTORNOS DE LA HEMOSTASIA
EA202190827A1 (ru) * 2015-11-13 2021-11-30 Баксалта Инкорпорейтед Вирусные векторы, кодирующие рекомбинантные варианты fviii с повышенной экспрессией для генной терапии гемофилии a
BR112021003399A2 (pt) * 2018-08-24 2021-05-18 Spark Therapeutics, Inc. sequências de promotores otimizadas, construtos de expressão livres de íntron e métodos de uso

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