JP2025514313A5 - - Google Patents
Info
- Publication number
- JP2025514313A5 JP2025514313A5 JP2024563594A JP2024563594A JP2025514313A5 JP 2025514313 A5 JP2025514313 A5 JP 2025514313A5 JP 2024563594 A JP2024563594 A JP 2024563594A JP 2024563594 A JP2024563594 A JP 2024563594A JP 2025514313 A5 JP2025514313 A5 JP 2025514313A5
- Authority
- JP
- Japan
- Prior art keywords
- aav
- raav
- nucleic acid
- expression vector
- fviii
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| RU2022111734A RU2808564C2 (ru) | 2022-04-28 | Кодон-оптимизированная нуклеиновая кислота, которая кодирует белок фактора свёртывания крови VIII c делетированным B доменом, и ее применение | |
| RU2022111734 | 2022-04-28 | ||
| PCT/RU2023/050094 WO2023211316A1 (en) | 2022-04-28 | 2023-04-18 | Codon-optimized nucleic acid encoding the fviii-bdd |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2025514313A JP2025514313A (ja) | 2025-05-02 |
| JP2025514313A5 true JP2025514313A5 (https=) | 2026-04-28 |
Family
ID=88482201
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2024563594A Pending JP2025514313A (ja) | 2022-04-28 | 2023-04-18 | Fviii-bddをコードするコドン最適化型核酸 |
Country Status (20)
| Country | Link |
|---|---|
| US (1) | US20250282847A1 (https=) |
| EP (1) | EP4514836A1 (https=) |
| JP (1) | JP2025514313A (https=) |
| KR (1) | KR20250007615A (https=) |
| CN (1) | CN116970629A (https=) |
| AR (1) | AR129163A1 (https=) |
| AU (1) | AU2023261338A1 (https=) |
| CA (1) | CA3250665A1 (https=) |
| CL (1) | CL2024003296A1 (https=) |
| CO (1) | CO2024014690A2 (https=) |
| CR (1) | CR20240524A (https=) |
| IL (1) | IL316584A (https=) |
| JO (1) | JOP20240241A1 (https=) |
| MA (1) | MA68586A1 (https=) |
| MX (1) | MX2024013280A (https=) |
| PE (1) | PE20251838A1 (https=) |
| PY (1) | PY2331315A (https=) |
| TW (1) | TW202346601A (https=) |
| UY (1) | UY40241A (https=) |
| WO (1) | WO2023211316A1 (https=) |
Family Cites Families (3)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| PE20231949A1 (es) * | 2015-10-30 | 2023-12-05 | Spark Therapeutics Inc | VARIANTES DEL FACTOR VIII REDUCIDO CON CpG, COMPOSICIONES Y METODOS Y USOS PARA EL TRATAMIENTO DE TRASTORNOS DE LA HEMOSTASIA |
| EA202190827A1 (ru) * | 2015-11-13 | 2021-11-30 | Баксалта Инкорпорейтед | Вирусные векторы, кодирующие рекомбинантные варианты fviii с повышенной экспрессией для генной терапии гемофилии a |
| BR112021003399A2 (pt) * | 2018-08-24 | 2021-05-18 | Spark Therapeutics, Inc. | sequências de promotores otimizadas, construtos de expressão livres de íntron e métodos de uso |
-
2023
- 2023-04-18 KR KR1020247039728A patent/KR20250007615A/ko active Pending
- 2023-04-18 EP EP23796916.7A patent/EP4514836A1/en active Pending
- 2023-04-18 AU AU2023261338A patent/AU2023261338A1/en active Pending
- 2023-04-18 CA CA3250665A patent/CA3250665A1/en active Pending
- 2023-04-18 US US18/859,760 patent/US20250282847A1/en active Pending
- 2023-04-18 IL IL316584A patent/IL316584A/en unknown
- 2023-04-18 CR CR20240524A patent/CR20240524A/es unknown
- 2023-04-18 MA MA68586A patent/MA68586A1/fr unknown
- 2023-04-18 WO PCT/RU2023/050094 patent/WO2023211316A1/en not_active Ceased
- 2023-04-18 PE PE2024002342A patent/PE20251838A1/es unknown
- 2023-04-18 JP JP2024563594A patent/JP2025514313A/ja active Pending
- 2023-04-19 TW TW112114534A patent/TW202346601A/zh unknown
- 2023-04-26 UY UY0001040241A patent/UY40241A/es unknown
- 2023-04-27 CN CN202310468975.6A patent/CN116970629A/zh active Pending
- 2023-04-27 AR ARP230101022A patent/AR129163A1/es unknown
- 2023-04-27 PY PY202302331315A patent/PY2331315A/es unknown
-
2024
- 2024-10-27 JO JOJO/P/2024/0241A patent/JOP20240241A1/ar unknown
- 2024-10-28 CL CL2024003296A patent/CL2024003296A1/es unknown
- 2024-10-28 MX MX2024013280A patent/MX2024013280A/es unknown
- 2024-10-28 CO CONC2024/0014690A patent/CO2024014690A2/es unknown
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