JP2025165939A5 - - Google Patents
Info
- Publication number
- JP2025165939A5 JP2025165939A5 JP2025115513A JP2025115513A JP2025165939A5 JP 2025165939 A5 JP2025165939 A5 JP 2025165939A5 JP 2025115513 A JP2025115513 A JP 2025115513A JP 2025115513 A JP2025115513 A JP 2025115513A JP 2025165939 A5 JP2025165939 A5 JP 2025165939A5
- Authority
- JP
- Japan
- Prior art keywords
- salt
- double
- rnai agent
- pharmaceutical composition
- stranded rnai
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Applications Claiming Priority (7)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201562199563P | 2015-07-31 | 2015-07-31 | |
| US62/199,563 | 2015-07-31 | ||
| US201662287518P | 2016-01-27 | 2016-01-27 | |
| US62/287,518 | 2016-01-27 | ||
| JP2018504819A JP6896703B2 (ja) | 2015-07-31 | 2016-07-28 | ＴＴＲ関連疾患を治療または予防するためのトランスサイレチン（ＴＴＲ）ｉＲＮＡ組成物およびその使用方法 |
| JP2021096344A JP7417559B2 (ja) | 2015-07-31 | 2021-06-09 | ＴＴＲ関連疾患を治療または予防するためのトランスサイレチン（ＴＴＲ）ｉＲＮＡ組成物およびその使用方法 |
| JP2023199064A JP7711150B2 (ja) | 2015-07-31 | 2023-11-24 | ＴＴＲ関連疾患を治療または予防するためのトランスサイレチン（ＴＴＲ）ｉＲＮＡ組成物およびその使用方法 |
Related Parent Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2023199064A Division JP7711150B2 (ja) | 2015-07-31 | 2023-11-24 | ＴＴＲ関連疾患を治療または予防するためのトランスサイレチン（ＴＴＲ）ｉＲＮＡ組成物およびその使用方法 |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2025165939A JP2025165939A (ja) | 2025-11-05 |
| JP2025165939A5 true JP2025165939A5 (enExample) | 2026-02-19 |
Family
ID=56682264
Family Applications (4)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2018504819A Active JP6896703B2 (ja) | 2015-07-31 | 2016-07-28 | ＴＴＲ関連疾患を治療または予防するためのトランスサイレチン（ＴＴＲ）ｉＲＮＡ組成物およびその使用方法 |
| JP2021096344A Active JP7417559B2 (ja) | 2015-07-31 | 2021-06-09 | ＴＴＲ関連疾患を治療または予防するためのトランスサイレチン（ＴＴＲ）ｉＲＮＡ組成物およびその使用方法 |
| JP2023199064A Active JP7711150B2 (ja) | 2015-07-31 | 2023-11-24 | ＴＴＲ関連疾患を治療または予防するためのトランスサイレチン（ＴＴＲ）ｉＲＮＡ組成物およびその使用方法 |
| JP2025115513A Pending JP2025165939A (ja) | 2015-07-31 | 2025-07-09 | ＴＴＲ関連疾患を治療または予防するためのトランスサイレチン（ＴＴＲ）ｉＲＮＡ組成物およびその使用方法 |
Family Applications Before (3)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2018504819A Active JP6896703B2 (ja) | 2015-07-31 | 2016-07-28 | ＴＴＲ関連疾患を治療または予防するためのトランスサイレチン（ＴＴＲ）ｉＲＮＡ組成物およびその使用方法 |
| JP2021096344A Active JP7417559B2 (ja) | 2015-07-31 | 2021-06-09 | ＴＴＲ関連疾患を治療または予防するためのトランスサイレチン（ＴＴＲ）ｉＲＮＡ組成物およびその使用方法 |
| JP2023199064A Active JP7711150B2 (ja) | 2015-07-31 | 2023-11-24 | ＴＴＲ関連疾患を治療または予防するためのトランスサイレチン（ＴＴＲ）ｉＲＮＡ組成物およびその使用方法 |
Country Status (35)
Families Citing this family (33)
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| KR20220152270A (ko) | 2020-03-06 | 2022-11-15 | 알닐람 파마슈티칼스 인코포레이티드 | 트랜스티레틴 (ttr)의 발현을 억제하기 위한 조성물 및 방법 |
| JP2024518374A (ja) | 2021-05-03 | 2024-05-01 | アルナイラム ファーマシューティカルズ， インコーポレイテッド | トランスサイレチン（ｔｔｒ）媒介性アミロイドーシスを治療するための組成物および方法 |
| EP4351541A2 (en) | 2021-06-08 | 2024-04-17 | Alnylam Pharmaceuticals, Inc. | Compositions and methods for treating or preventing stargardt's disease and/or retinal binding protein 4 (rbp4)-associated disorders |
| CA3227852A1 (en) | 2021-08-03 | 2023-02-09 | Alnylam Pharmaceuticals, Inc. | Transthyretin (ttr) irna compositions and methods of use thereof |
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