JP2024119900A5 - - Google Patents
Download PDFInfo
- Publication number
- JP2024119900A5 JP2024119900A5 JP2024091467A JP2024091467A JP2024119900A5 JP 2024119900 A5 JP2024119900 A5 JP 2024119900A5 JP 2024091467 A JP2024091467 A JP 2024091467A JP 2024091467 A JP2024091467 A JP 2024091467A JP 2024119900 A5 JP2024119900 A5 JP 2024119900A5
- Authority
- JP
- Japan
- Prior art keywords
- pharmaceutical composition
- promoter
- casq2
- patient
- ryr2
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Applications Claiming Priority (4)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| IT102018000004253 | 2018-04-05 | ||
| IT102018000004253A IT201800004253A1 (it) | 2018-04-05 | 2018-04-05 | Composizioni e metodi per il trattamento della tachicardia ventricolare polimorfa catecolaminergica dominante ereditaria. |
| PCT/IB2019/052817 WO2019193563A1 (en) | 2018-04-05 | 2019-04-05 | Compositions and methods for the treatment of dominantly-inherited catecholaminergic polymorphic ventricular tachycardia |
| JP2020552905A JP7500429B2 (ja) | 2018-04-05 | 2019-04-05 | 優性遺伝性カテコラミン誘発多形性心室頻拍の治療のための組成物および方法 |
Related Parent Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2020552905A Division JP7500429B2 (ja) | 2018-04-05 | 2019-04-05 | 優性遺伝性カテコラミン誘発多形性心室頻拍の治療のための組成物および方法 |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2024119900A JP2024119900A (ja) | 2024-09-03 |
| JP2024119900A5 true JP2024119900A5 (https=) | 2025-02-12 |
Family
ID=66554445
Family Applications (2)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2020552905A Active JP7500429B2 (ja) | 2018-04-05 | 2019-04-05 | 優性遺伝性カテコラミン誘発多形性心室頻拍の治療のための組成物および方法 |
| JP2024091467A Pending JP2024119900A (ja) | 2018-04-05 | 2024-06-05 | 優性遺伝性カテコラミン誘発多形性心室頻拍の治療のための組成物および方法 |
Family Applications Before (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2020552905A Active JP7500429B2 (ja) | 2018-04-05 | 2019-04-05 | 優性遺伝性カテコラミン誘発多形性心室頻拍の治療のための組成物および方法 |
Country Status (13)
| Country | Link |
|---|---|
| US (1) | US20210030894A1 (https=) |
| EP (2) | EP3773744B1 (https=) |
| JP (2) | JP7500429B2 (https=) |
| AU (2) | AU2019249374B2 (https=) |
| CA (1) | CA3094141A1 (https=) |
| DK (1) | DK3773744T3 (https=) |
| ES (1) | ES2988961T3 (https=) |
| FI (1) | FI3773744T3 (https=) |
| IL (2) | IL315337A (https=) |
| IT (1) | IT201800004253A1 (https=) |
| PL (1) | PL3773744T3 (https=) |
| PT (1) | PT3773744T (https=) |
| WO (1) | WO2019193563A1 (https=) |
Families Citing this family (2)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| CA3186584A1 (en) * | 2020-07-08 | 2022-01-13 | Children's Medical Center Corporation | Mybpc3 polypeptides and uses thereof |
| CN113957075B (zh) * | 2021-11-22 | 2023-04-07 | 百世诺(北京)医学检验实验室有限公司 | 突变的遗传性心律失常基因及其应用 |
Family Cites Families (24)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US5139941A (en) | 1985-10-31 | 1992-08-18 | University Of Florida Research Foundation, Inc. | AAV transduction vectors |
| US5766960A (en) | 1987-07-27 | 1998-06-16 | Australian Membrane And Biotechnology Research Institute | Receptor membranes |
| US5143854A (en) | 1989-06-07 | 1992-09-01 | Affymax Technologies N.V. | Large scale photolithographic solid phase synthesis of polypeptides and receptor binding screening thereof |
| US5466468A (en) | 1990-04-03 | 1995-11-14 | Ciba-Geigy Corporation | Parenterally administrable liposome formulation comprising synthetic lipids |
| US5173414A (en) | 1990-10-30 | 1992-12-22 | Applied Immune Sciences, Inc. | Production of recombinant adeno-associated virus vectors |
| DK0752248T3 (da) | 1992-11-13 | 2000-11-13 | Idec Pharma Corp | Terapeutisk anvendelse af kimæriske og radioaktivt mærkede antistoffer mod humant B-lymfocytbegrænset differentieringsantig |
| US5869305A (en) | 1992-12-04 | 1999-02-09 | The University Of Pittsburgh | Recombinant viral vector system |
| US6204059B1 (en) | 1994-06-30 | 2001-03-20 | University Of Pittsburgh | AAV capsid vehicles for molecular transfer |
| US6001650A (en) | 1995-08-03 | 1999-12-14 | Avigen, Inc. | High-efficiency wild-type-free AAV helper functions |
| US5801030A (en) | 1995-09-01 | 1998-09-01 | Genvec, Inc. | Methods and vectors for site-specific recombination |
| US6268210B1 (en) | 1998-05-27 | 2001-07-31 | Hyseq, Inc. | Sandwich arrays of biological compounds |
| US6232068B1 (en) | 1999-01-22 | 2001-05-15 | Rosetta Inpharmatics, Inc. | Monitoring of gene expression by detecting hybridization to nucleic acid arrays using anti-heteronucleic acid antibodies |
| DE10120829A1 (de) | 2000-04-27 | 2001-12-20 | Max Delbrueck Centrum | Sleeping Beauty, ein Transposonvektor mit breitem Wirtsbereich für die genetische Transformation bei Wirbeltieren |
| JP5170934B2 (ja) | 2001-08-16 | 2013-03-27 | ザ・トラステイーズ・オブ・ザ・ユニバーシテイ・オブ・ペンシルベニア | 改良ｄｎａリポフェクションならびに／または徐放性プロドラッグおよび薬物療法のための試薬の合成と使用 |
| ES2582091T3 (es) | 2005-10-18 | 2016-09-09 | Precision Biosciences | Meganucleasas diseñadas racionalmente con especificidad de secuencia y afinidad de unión a ADN alteradas |
| US7741529B1 (en) | 2006-05-04 | 2010-06-22 | Priori Silvia G | Transgenic animal model for catecholaminergic polymorphic ventricular tachycardia (CPVT) and use thereof |
| EP1995316A1 (de) | 2007-05-25 | 2008-11-26 | Qiagen GmbH | Verfahren zur schonenden Zellaufreinigung, Zellgewinnung und Transfektion von Zellen |
| EP2009095A1 (en) | 2007-06-28 | 2008-12-31 | Innovalor AG | Method of generating glucose-responsive cells |
| EP2215223B1 (en) | 2007-10-31 | 2013-05-01 | Precision Biosciences, Inc. | Rationally-designed single-chain meganucleases with non-palindromic recognition sequences |
| WO2010085699A2 (en) | 2009-01-23 | 2010-07-29 | The Johns Hopkins University | Mammalian piggybac transposon and methods of use |
| US8859517B2 (en) * | 2011-08-08 | 2014-10-14 | Fondazione Salvatore Maugeri Clinica Del Lavoro E Della Riabilitazione | Method of gene transfer for the treatment of recessive catecholaminergic polymorphic ventricular tachycardia (CPVT) |
| US8697359B1 (en) | 2012-12-12 | 2014-04-15 | The Broad Institute, Inc. | CRISPR-Cas systems and methods for altering expression of gene products |
| WO2016083625A1 (en) * | 2014-11-28 | 2016-06-02 | Institut National De La Sante Et De La Recherche Medicale (Inserm) | Nucleic acid encoding triadin for the prevention and/or treatment of heart failure |
| WO2017141157A1 (en) * | 2016-02-15 | 2017-08-24 | Istituti Clinici Scientifici Maugeri Spa Sb | Method of allele specific silencing for the treatment of autosomal dominant catecholaminergic polymorphic ventricular tachycardia (cpvt) |
-
2018
- 2018-04-05 IT IT102018000004253A patent/IT201800004253A1/it unknown
-
2019
- 2019-04-05 IL IL315337A patent/IL315337A/en unknown
- 2019-04-05 JP JP2020552905A patent/JP7500429B2/ja active Active
- 2019-04-05 PT PT197246069T patent/PT3773744T/pt unknown
- 2019-04-05 PL PL19724606.9T patent/PL3773744T3/pl unknown
- 2019-04-05 ES ES19724606T patent/ES2988961T3/es active Active
- 2019-04-05 DK DK19724606.9T patent/DK3773744T3/da active
- 2019-04-05 US US17/045,289 patent/US20210030894A1/en active Pending
- 2019-04-05 FI FIEP19724606.9T patent/FI3773744T3/fi active
- 2019-04-05 EP EP19724606.9A patent/EP3773744B1/en active Active
- 2019-04-05 IL IL277635A patent/IL277635B2/en unknown
- 2019-04-05 EP EP24160383.6A patent/EP4356727A3/en active Pending
- 2019-04-05 AU AU2019249374A patent/AU2019249374B2/en active Active
- 2019-04-05 CA CA3094141A patent/CA3094141A1/en active Pending
- 2019-04-05 WO PCT/IB2019/052817 patent/WO2019193563A1/en not_active Ceased
-
2024
- 2024-06-05 JP JP2024091467A patent/JP2024119900A/ja active Pending
-
2026
- 2026-03-31 AU AU2026202418A patent/AU2026202418A1/en active Pending
Similar Documents
| Publication | Publication Date | Title |
|---|---|---|
| JP2024119900A5 (https=) | ||
| JP2022068181A5 (https=) | ||
| JP2021522173A5 (https=) | ||
| JP2023534999A5 (https=) | ||
| JP2024009857A5 (https=) | ||
| JP2020522269A5 (https=) | ||
| JP2021512649A5 (https=) | ||
| JP2020533959A5 (https=) | ||
| US20040180440A1 (en) | Modified AAV | |
| CN108348621A (zh) | 用于基因治疗的经修饰的弗里德赖希共济失调基因及载体 | |
| JP2024523707A5 (https=) | ||
| JP2023537358A5 (https=) | ||
| JP2022511453A5 (https=) | ||
| JP2023524024A5 (https=) | ||
| KR102621134B1 (ko) | 알데히드 데히드로게나제 결핍의 치료를 위한 유전자 요법 | |
| JP2022541793A5 (https=) | ||
| JP2023537980A5 (https=) | ||
| JP2023059858A5 (https=) | ||
| JP2024546103A (ja) | Ａａｖベクターを用いたジャンクトフィリン－２（ｊｐｈ２）遺伝子治療 | |
| US20250283111A1 (en) | Recombinant adeno-associated viral vector for gene delivery | |
| JP2021534766A5 (https=) | ||
| CN118159656A (zh) | 肌营养不良的治疗 | |
| JP2024119900A (ja) | 優性遺伝性カテコラミン誘発多形性心室頻拍の治療のための組成物および方法 | |
| TW202129002A (zh) | 用於myh7關聯之心肌病之基因療法組合物及治療 | |
| JP2022554141A5 (https=) |