JP2022541740A5 - - Google Patents

Info

Publication number
JP2022541740A5
JP2022541740A5 JP2022500900A JP2022500900A JP2022541740A5 JP 2022541740 A5 JP2022541740 A5 JP 2022541740A5 JP 2022500900 A JP2022500900 A JP 2022500900A JP 2022500900 A JP2022500900 A JP 2022500900A JP 2022541740 A5 JP2022541740 A5 JP 2022541740A5
Authority
JP
Japan
Application number
JP2022500900A
Other languages
Japanese (ja)
Other versions
JPWO2021007278A5 (https=
JP2022541740A (ja
JP7586886B2 (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2020/041122 external-priority patent/WO2021007278A1/en
Publication of JP2022541740A publication Critical patent/JP2022541740A/ja
Publication of JP2022541740A5 publication Critical patent/JP2022541740A5/ja
Publication of JPWO2021007278A5 publication Critical patent/JPWO2021007278A5/ja
Priority to JP2024194073A priority Critical patent/JP2025024002A/ja
Application granted granted Critical
Publication of JP7586886B2 publication Critical patent/JP7586886B2/ja
Active legal-status Critical Current
Anticipated expiration legal-status Critical

Links

JP2022500900A 2019-07-08 2020-07-08 改善されたmRNA装填脂質ナノ粒子、およびそれを作製するプロセス Active JP7586886B2 (ja)

Priority Applications (1)

Application Number Priority Date Filing Date Title
JP2024194073A JP2025024002A (ja) 2019-07-08 2024-11-06 改善されたmRNA装填脂質ナノ粒子、およびそれを作製するプロセス

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201962871513P 2019-07-08 2019-07-08
US62/871,513 2019-07-08
PCT/US2020/041122 WO2021007278A1 (en) 2019-07-08 2020-07-08 Improved mrna-loaded lipid nanoparticles and processes of making the same

Related Child Applications (1)

Application Number Title Priority Date Filing Date
JP2024194073A Division JP2025024002A (ja) 2019-07-08 2024-11-06 改善されたmRNA装填脂質ナノ粒子、およびそれを作製するプロセス

Publications (4)

Publication Number Publication Date
JP2022541740A JP2022541740A (ja) 2022-09-27
JP2022541740A5 true JP2022541740A5 (https=) 2023-06-30
JPWO2021007278A5 JPWO2021007278A5 (https=) 2023-06-30
JP7586886B2 JP7586886B2 (ja) 2024-11-19

Family

ID=71784731

Family Applications (2)

Application Number Title Priority Date Filing Date
JP2022500900A Active JP7586886B2 (ja) 2019-07-08 2020-07-08 改善されたmRNA装填脂質ナノ粒子、およびそれを作製するプロセス
JP2024194073A Pending JP2025024002A (ja) 2019-07-08 2024-11-06 改善されたmRNA装填脂質ナノ粒子、およびそれを作製するプロセス

Family Applications After (1)

Application Number Title Priority Date Filing Date
JP2024194073A Pending JP2025024002A (ja) 2019-07-08 2024-11-06 改善されたmRNA装填脂質ナノ粒子、およびそれを作製するプロセス

Country Status (9)

Country Link
US (1) US20230181483A1 (https=)
EP (2) EP4467653B1 (https=)
JP (2) JP7586886B2 (https=)
KR (1) KR20220078557A (https=)
CN (2) CN114390921B (https=)
AU (1) AU2020311364B2 (https=)
CA (1) CA3146369A1 (https=)
ES (1) ES2992127T3 (https=)
WO (1) WO2021007278A1 (https=)

Families Citing this family (17)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
WO2019046809A1 (en) 2017-08-31 2019-03-07 Modernatx, Inc. METHODS OF MANUFACTURING LIPID NANOPARTICLES
US20230181483A1 (en) * 2019-07-08 2023-06-15 Translate Bio, Inc. Improved mrna-loaded lipid nanoparticles and processes of making the same
US12053551B2 (en) 2019-12-20 2024-08-06 Translate Bio, Inc. Process of preparing mRNA-loaded lipid nanoparticles
JP2024527940A (ja) * 2021-07-26 2024-07-26 モデルナティエックス インコーポレイテッド ペイロード分子を気道上皮に送達するための脂質ナノ粒子組成物を調製するプロセス
MX2024002726A (es) 2021-09-03 2024-03-20 CureVac SE Nuevas nanoparticulas lipidicas para la administracion de acidos nucleicos.
KR20230053998A (ko) 2021-10-15 2023-04-24 (주)지노믹트리 mRNA 발현을 위한 유전자 구조체
WO2023073228A1 (en) 2021-10-29 2023-05-04 CureVac SE Improved circular rna for expressing therapeutic proteins
US20250099614A1 (en) 2022-01-28 2025-03-27 CureVac SE Nucleic acid encoded transcription factor inhibitors
WO2023227608A1 (en) 2022-05-25 2023-11-30 Glaxosmithkline Biologicals Sa Nucleic acid based vaccine encoding an escherichia coli fimh antigenic polypeptide
US20260069713A1 (en) 2022-08-29 2026-03-12 Vivasor, Inc. Lipid-Coated Nanoparticles
WO2024089638A1 (en) 2022-10-28 2024-05-02 Glaxosmithkline Biologicals Sa Nucleic acid based vaccine
KR20250153298A (ko) 2023-03-08 2025-10-24 큐어백 에스이 핵산 전달을 위한 신규의 지질 나노입자 제형
WO2024230934A1 (en) 2023-05-11 2024-11-14 CureVac SE Therapeutic nucleic acid for the treatment of ophthalmic diseases
EP4722368A1 (en) 2023-05-26 2026-04-08 Samsung Biologics Co., Ltd. Novel nucleic acid construct comprising poly(a) tail having secondary or tertiary structure and uses thereof
KR20250018367A (ko) 2023-07-28 2025-02-05 한국과학기술원 히스톤 코드 리더 도메인을 포함하는 폴리펩티드 및 이의 용도
TW202543583A (zh) * 2024-03-01 2025-11-16 加拿大商阿奎特斯醫療公司 用於將治療劑包覆於脂質奈米顆粒中之材料及方法
CN121265551A (zh) * 2024-07-02 2026-01-06 苏州星核迪赛生物技术有限公司 一种靶向肝实质细胞的核酸递送载体及其应用

Family Cites Families (46)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US1580968A (en) 1923-01-26 1926-04-13 Brazza Ascanio Di Firearm with screwed barrel detachable by hand or permanently fixed
US4458066A (en) 1980-02-29 1984-07-03 University Patents, Inc. Process for preparing polynucleotides
US4500707A (en) 1980-02-29 1985-02-19 University Patents, Inc. Nucleosides useful in the preparation of polynucleotides
US5132418A (en) 1980-02-29 1992-07-21 University Patents, Inc. Process for preparing polynucleotides
US4973679A (en) 1981-03-27 1990-11-27 University Patents, Inc. Process for oligonucleo tide synthesis using phosphormidite intermediates
US4668777A (en) 1981-03-27 1987-05-26 University Patents, Inc. Phosphoramidite nucleoside compounds
US4415732A (en) 1981-03-27 1983-11-15 University Patents, Inc. Phosphoramidite compounds and processes
US4401796A (en) 1981-04-30 1983-08-30 City Of Hope Research Institute Solid-phase synthesis of polynucleotides
US4373071A (en) 1981-04-30 1983-02-08 City Of Hope Research Institute Solid-phase synthesis of polynucleotides
US4897355A (en) 1985-01-07 1990-01-30 Syntex (U.S.A.) Inc. N[ω,(ω-1)-dialkyloxy]- and N-[ω,(ω-1)-dialkenyloxy]-alk-1-yl-N,N,N-tetrasubstituted ammonium lipids and uses therefor
US5153319A (en) 1986-03-31 1992-10-06 University Patents, Inc. Process for preparing polynucleotides
US5262530A (en) 1988-12-21 1993-11-16 Applied Biosystems, Inc. Automated system for polynucleotide synthesis and purification
US5047524A (en) 1988-12-21 1991-09-10 Applied Biosystems, Inc. Automated system for polynucleotide synthesis and purification
FR2645866B1 (fr) 1989-04-17 1991-07-05 Centre Nat Rech Scient Nouvelles lipopolyamines, leur preparation et leur emploi
US5334761A (en) 1992-08-28 1994-08-02 Life Technologies, Inc. Cationic lipids
US5885613A (en) 1994-09-30 1999-03-23 The University Of British Columbia Bilayer stabilizing components and their use in forming programmable fusogenic liposomes
US5700642A (en) 1995-05-22 1997-12-23 Sri International Oligonucleotide sizing using immobilized cleavable primers
US5744335A (en) 1995-09-19 1998-04-28 Mirus Corporation Process of transfecting a cell with a polynucleotide mixed with an amphipathic compound and a DNA-binding protein
US7799565B2 (en) 2004-06-07 2010-09-21 Protiva Biotherapeutics, Inc. Lipid encapsulated interfering RNA
CN104119242B (zh) 2008-10-09 2017-07-07 泰米拉制药公司 改善的氨基脂质和递送核酸的方法
ES2646630T3 (es) 2008-11-07 2017-12-14 Massachusetts Institute Of Technology Lipidoides aminoalcohólicos y usos de los mismos
MX342785B (es) 2009-06-10 2016-10-12 Alnylam Pharmaceuticals Inc Formulacion mejorada de lipido.
HUE042177T2 (hu) 2009-12-01 2019-06-28 Translate Bio Inc Szteroidszármazék mRNS szállítására humán genetikai betegségekben
EP3354644A1 (en) 2011-06-08 2018-08-01 Translate Bio, Inc. Cleavable lipids
KR102451116B1 (ko) 2011-10-27 2022-10-06 메사추세츠 인스티튜트 오브 테크놀로지 약물 캡슐화 마이크로스피어를 형성할 수 있는, n-말단 상에 관능화된 아미노산 유도체
ES2762873T3 (es) 2012-03-29 2020-05-26 Translate Bio Inc Lípidos catiónicos ionizables
ES2895651T3 (es) 2013-12-19 2022-02-22 Novartis Ag Lípidos y composiciones lipídicas para la administración de agentes activos
JP6557722B2 (ja) 2014-05-30 2019-08-07 シャイアー ヒューマン ジェネティック セラピーズ インコーポレイテッド 核酸の送達のための生分解性脂質
SMT202200502T1 (it) 2014-06-25 2023-01-13 Acuitas Therapeutics Inc Nuovi lipidi e formulazioni di nanoparticelle lipidiche per l'erogazione di acidi nucleici
US9840479B2 (en) 2014-07-02 2017-12-12 Massachusetts Institute Of Technology Polyamine-fatty acid derived lipidoids and uses thereof
BR112016030852A2 (pt) 2014-07-02 2018-01-16 Shire Human Genetic Therapies encapsulação de rna mensageiro
US20180000953A1 (en) 2015-01-21 2018-01-04 Moderna Therapeutics, Inc. Lipid nanoparticle compositions
WO2016118725A1 (en) 2015-01-23 2016-07-28 Moderna Therapeutics, Inc. Lipid nanoparticle compositions
ES2949540T3 (es) * 2015-06-19 2023-09-29 Massachusetts Inst Technology 2,5-piperazinadionas sustituidas con alquenilo y su uso en composiciones para suministrar un agente a un sujeto o una célula
LT3313829T (lt) 2015-06-29 2024-08-12 Acuitas Therapeutics Inc. Lipidai ir lipidų nanodalelių sudėtys, skirtos nukleorūgščių tiekimui
EP4286012A3 (en) 2015-09-17 2024-05-29 ModernaTX, Inc. Compounds and compositions for intracellular delivery of therapeutic agents
IL307179A (en) 2015-10-28 2023-11-01 Acuitas Therapeutics Inc Novel lipids and lipid nanoparticle formulations for delivery of nucleic acids
EP3397613A1 (en) 2015-12-30 2018-11-07 Acuitas Therapeutics Inc. Lipids and lipid nanoparticle formulations for delivery of nucleic acids
TWI773666B (zh) 2016-03-30 2022-08-11 美商英特利亞醫療公司 Crispr/cas 組分之脂質奈米粒子調配物
EP3315125A1 (en) * 2016-10-31 2018-05-02 Silence Therapeutics (London) Ltd Lipid nanoparticle formulation
WO2018089801A1 (en) 2016-11-10 2018-05-17 Translate Bio, Inc. Improved process of preparing mrna-loaded lipid nanoparticles
MX2019005470A (es) 2016-11-10 2019-11-21 Translate Bio Inc Formulación de nanopartículas lipídicas basadas en ice mejorada para el suministro de arnm.
MA47824A (fr) 2017-03-07 2020-01-15 Translate Bio Inc Administration polyanionique d'acides nucléiques
MX2021005482A (es) * 2018-11-09 2021-09-08 Translate Bio Inc Lípidos de 2,5-dioxopiperazina con porciones éster, tioéster, disulfuro y anhidrido intercaladas.
WO2020097511A2 (en) * 2018-11-09 2020-05-14 Translate Bio, Inc. Messenger rna therapy for treatment of ocular diseases
US20230181483A1 (en) * 2019-07-08 2023-06-15 Translate Bio, Inc. Improved mrna-loaded lipid nanoparticles and processes of making the same

Similar Documents

Publication Publication Date Title
JP2022541740A5 (https=)
CN306795917S (https=)
CN306354922S (https=)
CN305592520S (https=)
CN305595195S (https=)
CN305793831S (https=)
CN305794045S (https=)
CN306160326S (https=)
CN306183828S (https=)
CN306192882S (https=)
CN306198580S (https=)
CN306239187S (https=)
CN306268929S (https=)
CN306269363S (https=)
CN306290921S (https=)
CN306293412S (https=)
CN306294351S (https=)
CN306294559S (https=)
CN306297189S (https=)
CN306297668S (https=)
CN306298558S (https=)
CN306300495S (https=)
CN306300717S (https=)
CN306301622S (https=)
CN306304469S (https=)