JP2022521851A5 - - Google Patents
Info
- Publication number
- JP2022521851A5 JP2022521851A5 JP2021559062A JP2021559062A JP2022521851A5 JP 2022521851 A5 JP2022521851 A5 JP 2022521851A5 JP 2021559062 A JP2021559062 A JP 2021559062A JP 2021559062 A JP2021559062 A JP 2021559062A JP 2022521851 A5 JP2022521851 A5 JP 2022521851A5
- Authority
- JP
- Japan
- Prior art keywords
- cells
- use according
- raav8
- vector
- raav8 vector
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Priority Applications (1)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| JP2025083822A JP2025131621A (ja) | 2019-04-03 | 2025-05-20 | 眼の病態に対する遺伝子療法 |
Applications Claiming Priority (7)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201962828949P | 2019-04-03 | 2019-04-03 | |
| US62/828,949 | 2019-04-03 | ||
| US201962856533P | 2019-06-03 | 2019-06-03 | |
| US62/856,533 | 2019-06-03 | ||
| US201962946158P | 2019-12-10 | 2019-12-10 | |
| US62/946,158 | 2019-12-10 | ||
| PCT/US2020/026356 WO2020206098A1 (en) | 2019-04-03 | 2020-04-02 | Gene therapy for eye pathologies |
Related Child Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2025083822A Division JP2025131621A (ja) | 2019-04-03 | 2025-05-20 | 眼の病態に対する遺伝子療法 |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2022521851A JP2022521851A (ja) | 2022-04-12 |
| JP2022521851A5 true JP2022521851A5 (https=) | 2023-04-11 |
Family
ID=70480820
Family Applications (2)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2021559062A Pending JP2022521851A (ja) | 2019-04-03 | 2020-04-02 | 眼の病態に対する遺伝子療法 |
| JP2025083822A Pending JP2025131621A (ja) | 2019-04-03 | 2025-05-20 | 眼の病態に対する遺伝子療法 |
Family Applications After (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2025083822A Pending JP2025131621A (ja) | 2019-04-03 | 2025-05-20 | 眼の病態に対する遺伝子療法 |
Country Status (13)
| Country | Link |
|---|---|
| US (1) | US20220143221A1 (https=) |
| EP (2) | EP4667578A3 (https=) |
| JP (2) | JP2022521851A (https=) |
| KR (2) | KR20220004987A (https=) |
| CN (2) | CN113966236A (https=) |
| AU (1) | AU2020253462A1 (https=) |
| BR (1) | BR112021019825A2 (https=) |
| CA (1) | CA3135843A1 (https=) |
| IL (1) | IL286825A (https=) |
| MX (1) | MX2021011889A (https=) |
| SG (1) | SG11202110789VA (https=) |
| TW (1) | TW202102679A (https=) |
| WO (1) | WO2020206098A1 (https=) |
Families Citing this family (18)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| SG11201808426XA (en) | 2016-04-15 | 2018-10-30 | Univ Pennsylvania | Compositions for treatment of wet age-related macular degeneration |
| EP3727468A4 (en) | 2017-12-19 | 2021-09-22 | Akouos, Inc. | AAV-MEDIATED THERAPEUTIC ANTIBODIES DELIVERY TO THE INTERNAL EAR |
| US12558434B2 (en) | 2018-02-20 | 2026-02-24 | The Trustees Of The University Of Pennsylvania | Compositions for treatment of wet age-related macular degeneration |
| CA3136119A1 (en) * | 2019-04-10 | 2020-10-15 | University Of Utah Research Foundation | Htra1 modulation for treatment of amd |
| EP3752524A4 (en) * | 2019-04-27 | 2021-11-24 | Ocugen, Inc. | ADENO-ASSOCIATED VIRUS VECTOR MEDIATED GENE THERAPY FOR OPHTHALMIC DISEASE |
| US20230277685A1 (en) * | 2020-04-08 | 2023-09-07 | President And Fellows Of Harvard College | TGFß THERAPY FOR OCULAR AND NEURODEGENERATIVE DISEASES |
| CN111826386B (zh) * | 2020-07-30 | 2022-02-01 | 西南大学 | 一种调控棉花纤维呈色的融合基因及其表达载体和应用 |
| AU2021358781A1 (en) * | 2020-10-07 | 2023-05-18 | Tern Therapeutics, Llc | Gene therapy for ocular manifestations of cln2 disease |
| IL303317A (en) | 2020-12-01 | 2023-07-01 | Akouos Inc | ANTI-NATURAL ANTIBODY STRUCTURES AND RELATED METHODS FOR THE TREATMENT OF SYMPTOMS ASSOCIATED WITH VESTIBULAR SWANNOMA |
| CN116964209A (zh) * | 2021-02-12 | 2023-10-27 | 格雷菲克斯公司 | 视网膜疾病的基因治疗 |
| US20240316219A1 (en) * | 2021-05-03 | 2024-09-26 | North Carolina State University | Compositions and methods related to the treatment of ocular diseases in equines |
| JP2024525183A (ja) * | 2021-06-18 | 2024-07-10 | イカロベック リミテッド | 網膜障害 |
| JP2025503637A (ja) * | 2022-01-09 | 2025-02-04 | クリヤ セラピューティクス, インコーポレイテッド | 治療用抗igf-1r抗体をコードする核酸の送達のためのベクター構築物およびそれを使用する方法 |
| CN115137553A (zh) * | 2022-07-11 | 2022-10-04 | 上海市同济医院 | 一种免造孔视网膜下液排出装置 |
| JPWO2024048688A1 (https=) * | 2022-08-31 | 2024-03-07 | ||
| IL319873A (en) | 2022-09-30 | 2025-05-01 | Regenxbio Inc | Treatment of eye diseases with recombinant viral vectors containing anti-VEGF FAB |
| CN116965768B (zh) * | 2023-07-07 | 2024-01-19 | 中山大学中山眼科中心 | 一种自动定量分析眼内前房炎症程度的系统 |
| WO2026011181A1 (en) * | 2024-07-05 | 2026-01-08 | Wisconsin Alumni Research Foundation | Design and application of novel photoreceptor-specific promoters for retinal gene therapy applications |
Family Cites Families (48)
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| US878575A (en) | 1906-12-31 | 1908-02-11 | Isaac Stevenson | Ore dredging and separating apparatus. |
| EP0804561B1 (en) | 1993-02-12 | 2009-12-30 | The Board Of Trustees Of The Leland Stanford Junior University | Regulated transcription of targeted genes and other biological events |
| AU719001B2 (en) | 1994-12-29 | 2000-05-04 | Massachusetts Institute Of Technology | Chimeric DNA-binding proteins |
| WO1996041865A1 (en) | 1995-06-07 | 1996-12-27 | Ariad Gene Therapeutics, Inc. | Rapamcycin-based regulation of biological events |
| JP2003524368A (ja) | 1997-08-26 | 2003-08-19 | アリアド ジーン セラピューティクス インコーポレイテッド | ニ量化ドメイン、三量化ドメインまたは四量化ドメインおよび補足的非相同転写活性化ドメイン、転写抑制ドメイン、dna結合ドメインまたはリガンド結合ドメインを含む融合蛋白 |
| JP2001514007A (ja) | 1997-08-27 | 2001-09-11 | アリアド ジーン セラピューティクス インコーポレイテッド | キメラ転写アクチベーター、ならびにそれに関連する組成物および使用 |
| JP2002508971A (ja) | 1998-01-15 | 2002-03-26 | アリアド・ジーン・セラピューティクス・インコーポレーテッド | 多量体キメラ蛋白質を使用する生物学的イベントの調節 |
| JP2002503667A (ja) | 1998-02-13 | 2002-02-05 | プレジデント・アンド・フェローズ・オブ・ハーバード・カレッジ | 新規な二量体化剤、その製造および使用 |
| CA2379166C (en) | 1999-08-09 | 2013-03-26 | Targeted Genetics Corporation | Enhancement of expression of a single-stranded, heterologous nucleotide sequence from recombinant viral vectors by designing the sequence such that it forms instrastrand base pairs |
| US7067526B1 (en) | 1999-08-24 | 2006-06-27 | Ariad Gene Therapeutics, Inc. | 28-epirapalogs |
| MX359371B (es) | 2001-11-13 | 2018-09-25 | Univ Pennsylvania | Un metodo para detectar y/o identificar secuencias del virus adeno-asociado y aislamiento de secuencias novedosas identificadas de ese modo. |
| PT1453547T (pt) | 2001-12-17 | 2016-12-28 | Univ Pennsylvania | Sequências do vírus adeno-associado (aav) do serotipo 8, vetores contendo as mesmas, e utilizações destas |
| US20040208847A1 (en) * | 2003-03-28 | 2004-10-21 | Fabienne Rolling | Method and vectors for selectively transducing retinal pigment epithelium cells |
| EP2345731B1 (en) | 2003-09-30 | 2015-10-21 | The Trustees of the University of Pennsylvania | Adeno-associated virus (AAV) clades, sequences, vectors containing same, and uses thereof |
| ES2525067T3 (es) | 2005-04-07 | 2014-12-17 | The Trustees Of The University Of Pennsylvania | Método de incremento de la función de un vector de AAV |
| JP4495210B2 (ja) | 2005-06-09 | 2010-06-30 | パナソニック株式会社 | 振幅誤差補償装置及び直交度誤差補償装置 |
| US20070202186A1 (en) * | 2006-02-22 | 2007-08-30 | Iscience Interventional Corporation | Apparatus and formulations for suprachoroidal drug delivery |
| US8734809B2 (en) | 2009-05-28 | 2014-05-27 | University Of Massachusetts | AAV's and uses thereof |
| KR20130050939A (ko) * | 2010-04-12 | 2013-05-16 | 가부시키가이샤 아루떼꾸 우에노 | 망막 질환의 치료 방법 및 이를 위한 안과용 조성물 |
| US8927514B2 (en) | 2010-04-30 | 2015-01-06 | City Of Hope | Recombinant adeno-associated vectors for targeted treatment |
| US8628966B2 (en) | 2010-04-30 | 2014-01-14 | City Of Hope | CD34-derived recombinant adeno-associated vectors for stem cell transduction and systemic therapeutic gene transfer |
| WO2012057363A1 (ja) | 2010-10-27 | 2012-05-03 | 学校法人自治医科大学 | 神経系細胞への遺伝子導入のためのアデノ随伴ウイルスビリオン |
| WO2012109570A1 (en) | 2011-02-10 | 2012-08-16 | The University Of North Carolina At Chapel Hill | Viral vectors with modified transduction profiles and methods of making and using the same |
| CN105755044A (zh) | 2011-04-22 | 2016-07-13 | 加利福尼亚大学董事会 | 具有变异衣壳的腺相关病毒病毒体及其使用方法 |
| EP2559443A1 (en) * | 2011-08-16 | 2013-02-20 | INSERM (Institut National de la Santé et de la Recherche Médicale) | Methods and pharmaceutical compositions for the treatment of an ocular disease in a subject |
| ES2857773T5 (es) | 2011-08-24 | 2024-06-04 | Univ Leland Stanford Junior | Nuevas proteínas de la cápside de AAV para la transferencia de ácidos nucleicos |
| WO2013170078A1 (en) | 2012-05-09 | 2013-11-14 | Oregon Health & Science University | Adeno associated virus plasmids and vectors |
| US9393370B2 (en) | 2012-05-24 | 2016-07-19 | Altaviz Llc | Viscous fluid injector |
| CA2905952A1 (en) | 2013-03-13 | 2014-10-02 | The Children's Hospital Of Philadelphia | Adeno-associated virus vectors and methods of use thereof |
| ES2739288T3 (es) | 2013-09-13 | 2020-01-30 | California Inst Of Techn | Recuperación selectiva |
| CN106232618A (zh) | 2013-10-11 | 2016-12-14 | 马萨诸塞眼科耳科诊所 | 预测祖先病毒序列的方法及其用途 |
| WO2015164757A1 (en) | 2014-04-25 | 2015-10-29 | Oregon Health & Science University | Methods of viral neutralizing antibody epitope mapping |
| US10064752B2 (en) * | 2014-09-11 | 2018-09-04 | Orbit Biomedical Limited | Motorized suprachoroidal injection of therapeutic agent |
| CN107249522B (zh) | 2014-09-19 | 2021-04-20 | 奥叙拉尔有限公司 | 眼科递送装置 |
| US11071643B2 (en) | 2014-11-28 | 2021-07-27 | Visionisti Oy | Ocular therapeutics tool |
| AU2016219789B2 (en) * | 2015-02-20 | 2021-03-25 | Fondazione Telethon | Methods and compositions for treating genetic eye diseases |
| US11154420B2 (en) | 2015-09-17 | 2021-10-26 | Oxular Limited | Ophthalmic injection device |
| GB201519086D0 (en) * | 2015-10-28 | 2015-12-09 | Syncona Partners Llp | Gene Therapy |
| USD878575S1 (en) | 2015-11-24 | 2020-03-17 | Visionisti Oy | Hand operated medical instrument |
| CA3010862A1 (en) * | 2016-01-08 | 2017-07-13 | Clearside Biomedical, Inc. | Methods and devices for treating posterior ocular disorderswith aflibercept and other biologics |
| WO2017158365A2 (en) | 2016-03-16 | 2017-09-21 | Oxular Limited | Ophthalmic delivery device and ophthalmic active agent containing compositions |
| KR20240005973A (ko) | 2016-04-15 | 2024-01-12 | 리젠엑스바이오 인크. | 완전히-인간형의 번역후 변형된 항-VEGF Fab를 이용한 눈 질환의 치료 |
| SG11201808426XA (en) | 2016-04-15 | 2018-10-30 | Univ Pennsylvania | Compositions for treatment of wet age-related macular degeneration |
| IL316926A (en) * | 2017-05-11 | 2025-01-01 | Univ Pennsylvania | Gene therapy for neuronal ceroid lipofuscinosis |
| EP3687464A4 (en) * | 2017-09-27 | 2021-09-29 | REGENXBIO Inc. | TREATMENT OF EYE DISEASES WITH A TOTALLY HUMAN POST-TRANSLATION MODIFIED ANTI-VEGF FAB |
| US11071824B2 (en) | 2017-11-04 | 2021-07-27 | Altaviz, Llc | Injection devices and methods for making and using them |
| US10912883B2 (en) | 2017-11-04 | 2021-02-09 | Altaviz, Llc | Gas-powered fluid injection system |
| JP2022527116A (ja) * | 2019-04-08 | 2022-05-30 | ザ・チルドレンズ・ホスピタル・オブ・フィラデルフィア | Tpp1を発現するaavの投与による眼のリソソーム蓄積症の治療 |
-
2020
- 2020-04-02 WO PCT/US2020/026356 patent/WO2020206098A1/en not_active Ceased
- 2020-04-02 EP EP25210112.6A patent/EP4667578A3/en active Pending
- 2020-04-02 CA CA3135843A patent/CA3135843A1/en active Pending
- 2020-04-02 MX MX2021011889A patent/MX2021011889A/es unknown
- 2020-04-02 US US17/600,377 patent/US20220143221A1/en active Pending
- 2020-04-02 CN CN202080041009.0A patent/CN113966236A/zh active Pending
- 2020-04-02 KR KR1020217035262A patent/KR20220004987A/ko not_active Ceased
- 2020-04-02 CN CN202511459925.7A patent/CN121371216A/zh active Pending
- 2020-04-02 JP JP2021559062A patent/JP2022521851A/ja active Pending
- 2020-04-02 AU AU2020253462A patent/AU2020253462A1/en active Pending
- 2020-04-02 KR KR1020267005110A patent/KR20260033621A/ko active Pending
- 2020-04-02 BR BR112021019825A patent/BR112021019825A2/pt unknown
- 2020-04-02 EP EP20723243.0A patent/EP3946467A1/en not_active Withdrawn
- 2020-04-02 SG SG11202110789VA patent/SG11202110789VA/en unknown
- 2020-04-06 TW TW109111508A patent/TW202102679A/zh unknown
-
2021
- 2021-09-29 IL IL286825A patent/IL286825A/en unknown
-
2025
- 2025-05-20 JP JP2025083822A patent/JP2025131621A/ja active Pending
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