JP2023539368A5 - - Google Patents

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Publication number
JP2023539368A5
JP2023539368A5 JP2023514414A JP2023514414A JP2023539368A5 JP 2023539368 A5 JP2023539368 A5 JP 2023539368A5 JP 2023514414 A JP2023514414 A JP 2023514414A JP 2023514414 A JP2023514414 A JP 2023514414A JP 2023539368 A5 JP2023539368 A5 JP 2023539368A5
Authority
JP
Japan
Prior art keywords
nucleotide sequence
seq
sequence
nucleic acid
vector
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2023514414A
Other languages
English (en)
Japanese (ja)
Other versions
JP2023539368A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2021/048267 external-priority patent/WO2022051232A1/en
Publication of JP2023539368A publication Critical patent/JP2023539368A/ja
Publication of JP2023539368A5 publication Critical patent/JP2023539368A5/ja
Pending legal-status Critical Current

Links

JP2023514414A 2020-09-02 2021-08-30 コドン最適化したrpgrorf15遺伝子およびその使用 Pending JP2023539368A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202063073843P 2020-09-02 2020-09-02
US63/073,843 2020-09-02
PCT/US2021/048267 WO2022051232A1 (en) 2020-09-02 2021-08-30 Codon optimized rpgrorf 15 genes and uses thereof

Publications (2)

Publication Number Publication Date
JP2023539368A JP2023539368A (ja) 2023-09-13
JP2023539368A5 true JP2023539368A5 (https=) 2024-09-06

Family

ID=80358240

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2023514414A Pending JP2023539368A (ja) 2020-09-02 2021-08-30 コドン最適化したrpgrorf15遺伝子およびその使用

Country Status (10)

Country Link
US (3) US20230340042A1 (https=)
EP (1) EP4208156A4 (https=)
JP (1) JP2023539368A (https=)
KR (1) KR102825852B1 (https=)
CN (1) CN116782886A (https=)
AU (1) AU2021337530B2 (https=)
BR (1) BR112023003834A2 (https=)
CA (1) CA3191540A1 (https=)
IL (1) IL300785B2 (https=)
WO (1) WO2022051232A1 (https=)

Families Citing this family (4)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
IL300785B2 (en) * 2020-09-02 2025-04-01 4D Molecular Therapeutics Inc RPGRORF 15-codon-specific genes and their uses
CN117165596A (zh) * 2022-05-27 2023-12-05 武汉纽福斯生物科技有限公司 编码rpgr的核酸及其应用
EP4696540A1 (en) 2023-05-11 2026-02-18 LG Energy Solution, Ltd. Computing system for providing energy management service connected with autonomous driving, operation method of computing system and vehicle
CN121693566A (zh) * 2023-07-28 2026-03-17 瑞泽恩制药公司 使用bGH-SV40L串联PolyA在单向基因插入期间增强转基因表达

Family Cites Families (10)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
WO2003031569A2 (en) * 2001-10-10 2003-04-17 Centocor, Inc. Nucleic acid vaccines using tumor antigen encoding nucleic acids with cytokine adjuvant encoding nucleic acid
US9163259B2 (en) * 2012-05-04 2015-10-20 Novartis Ag Viral vectors for the treatment of retinal dystrophy
EP2872183B1 (en) * 2012-07-11 2018-09-26 The Trustees Of The University Of Pennsylvania Aav-mediated gene therapy for rpgr x-linked retinal degeneration
US9534225B2 (en) * 2014-04-15 2017-01-03 Applied Genetic Technologies Corporation Codon optimized nucleic acid encoding a retinitis pigmentosa gtpase regulator (RPGR)
GB201516066D0 (en) * 2015-09-10 2015-10-28 Young & Co Llp D Treatment of retinitis pigmentosa
US11364308B2 (en) * 2016-05-13 2022-06-21 4D Molecular Therapeutics Inc. Adeno-associated virus variant capsids and methods of use thereof
GB201704192D0 (en) * 2017-03-16 2017-05-03 Nightstarx Ltd Treatment of Retinitis Pigmentosa
US20210348193A1 (en) 2018-09-21 2021-11-11 Nightstarx Limited Compositions and methods for treating retinitis pigmentosa
CN113952472A (zh) * 2020-07-21 2022-01-21 英斯培瑞有限公司 用于治疗眼部疾病的组合物和方法
IL300785B2 (en) * 2020-09-02 2025-04-01 4D Molecular Therapeutics Inc RPGRORF 15-codon-specific genes and their uses

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