JP2023539367A5 - - Google Patents

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Publication number
JP2023539367A5
JP2023539367A5 JP2023514413A JP2023514413A JP2023539367A5 JP 2023539367 A5 JP2023539367 A5 JP 2023539367A5 JP 2023514413 A JP2023514413 A JP 2023514413A JP 2023514413 A JP2023514413 A JP 2023514413A JP 2023539367 A5 JP2023539367 A5 JP 2023539367A5
Authority
JP
Japan
Prior art keywords
nucleotide sequence
seq
nucleic acid
sequence
vector
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2023514413A
Other languages
English (en)
Japanese (ja)
Other versions
JP2023539367A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2021/048510 external-priority patent/WO2022051294A1/en
Publication of JP2023539367A publication Critical patent/JP2023539367A/ja
Publication of JP2023539367A5 publication Critical patent/JP2023539367A5/ja
Pending legal-status Critical Current

Links

JP2023514413A 2020-09-02 2021-08-31 コドン最適化したrep1遺伝子およびその使用 Pending JP2023539367A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202063073837P 2020-09-02 2020-09-02
US63/073,837 2020-09-02
PCT/US2021/048510 WO2022051294A1 (en) 2020-09-02 2021-08-31 Codon optimized rep1 genes and uses thereof

Publications (2)

Publication Number Publication Date
JP2023539367A JP2023539367A (ja) 2023-09-13
JP2023539367A5 true JP2023539367A5 (https=) 2024-09-09

Family

ID=80356143

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2023514413A Pending JP2023539367A (ja) 2020-09-02 2021-08-31 コドン最適化したrep1遺伝子およびその使用

Country Status (10)

Country Link
US (4) US11357870B2 (https=)
EP (1) EP4208182A4 (https=)
JP (1) JP2023539367A (https=)
KR (1) KR102888699B1 (https=)
CN (1) CN116806158A (https=)
AU (1) AU2021337580B2 (https=)
BR (1) BR112023003840A2 (https=)
CA (1) CA3191545A1 (https=)
IL (1) IL300752A (https=)
WO (1) WO2022051294A1 (https=)

Families Citing this family (2)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
WO2026030354A2 (en) * 2024-07-29 2026-02-05 Remedium Bio, Inc. Optimized dna cassettes for gene therapy
CN119736306B (zh) * 2025-02-26 2025-09-12 上海奥浦迈生物科技股份有限公司 一种Noggin蛋白的表达载体及其应用

Family Cites Families (4)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
CA3008264A1 (en) * 2015-12-14 2017-06-22 The Trustees Of The University Of Pennsylvania Gene therapy for ocular disorders
WO2017191274A2 (en) * 2016-05-04 2017-11-09 Curevac Ag Rna encoding a therapeutic protein
JP7766393B2 (ja) * 2017-06-14 2025-11-10 ザ・トラステイーズ・オブ・ザ・ユニバーシテイ・オブ・ペンシルベニア 眼疾患のための遺伝子療法
WO2019195729A1 (en) * 2018-04-05 2019-10-10 Nightstarx Ltd. Aav compositions, methods of making and methods of use

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