JP2024519888A5 - - Google Patents

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Publication number
JP2024519888A5
JP2024519888A5 JP2023571788A JP2023571788A JP2024519888A5 JP 2024519888 A5 JP2024519888 A5 JP 2024519888A5 JP 2023571788 A JP2023571788 A JP 2023571788A JP 2023571788 A JP2023571788 A JP 2023571788A JP 2024519888 A5 JP2024519888 A5 JP 2024519888A5
Authority
JP
Japan
Prior art keywords
retinal
capsid protein
polynucleotides
seq
sequence
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2023571788A
Other languages
English (en)
Japanese (ja)
Other versions
JP2024519888A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/CN2022/095422 external-priority patent/WO2022247917A1/zh
Publication of JP2024519888A publication Critical patent/JP2024519888A/ja
Publication of JP2024519888A5 publication Critical patent/JP2024519888A5/ja
Pending legal-status Critical Current

Links

JP2023571788A 2021-05-28 2022-05-27 カプシド変異を有する組換えアデノ随伴ウイルス及びその応用 Pending JP2024519888A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
CN202110594986 2021-05-28
CN202110594986.X 2021-05-28
PCT/CN2022/095422 WO2022247917A1 (zh) 2021-05-28 2022-05-27 衣壳变异的重组腺相关病毒及其应用

Publications (2)

Publication Number Publication Date
JP2024519888A JP2024519888A (ja) 2024-05-21
JP2024519888A5 true JP2024519888A5 (https=) 2025-06-09

Family

ID=84228446

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2023571788A Pending JP2024519888A (ja) 2021-05-28 2022-05-27 カプシド変異を有する組換えアデノ随伴ウイルス及びその応用

Country Status (11)

Country Link
US (1) US20240252679A1 (https=)
EP (1) EP4349852A4 (https=)
JP (1) JP2024519888A (https=)
KR (1) KR20240014477A (https=)
CN (1) CN117157309A (https=)
AU (1) AU2022281825A1 (https=)
BR (1) BR112023024375A2 (https=)
CA (1) CA3219898A1 (https=)
MX (1) MX2023014041A (https=)
TW (1) TW202313096A (https=)
WO (1) WO2022247917A1 (https=)

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CN118359687A (zh) * 2023-01-18 2024-07-19 上海朗昇生物科技有限公司 一种新衣壳蛋白变体以及其用途
CN118420721A (zh) * 2023-01-31 2024-08-02 上海朗昇生物科技有限公司 一种组织嗜性的腺相关病毒衣壳及其用途
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TW202508610A (zh) 2023-08-23 2025-03-01 大陸商上海瑞宏迪醫藥有限公司 醫藥組成物及其用途
CN119569833A (zh) * 2023-09-06 2025-03-07 北京锦篮基因科技有限公司 靶向骨骼肌的aav衣壳蛋白变体及其用途
CN119569834A (zh) * 2023-09-06 2025-03-07 北京锦篮基因科技有限公司 靶向心肌细胞的aav衣壳蛋白变体及其用途
CN120230798A (zh) * 2023-12-29 2025-07-01 上海朗昇生物科技有限公司 用于视网膜基因递送的重组腺相关病毒载体及其应用
WO2026033140A1 (en) * 2024-08-09 2026-02-12 Revvity Gene Delivery Gmbh Variant aav capsid polypeptides targeting the eye
CN119039401B (zh) * 2024-08-19 2025-04-11 广州派真生物技术有限公司 腺相关病毒突变体及其应用
CN118754952B (zh) * 2024-09-06 2025-01-10 上海玮美基因科技有限责任公司 一种新型腺相关病毒及其应用
CN120118955A (zh) * 2025-03-05 2025-06-10 广州派真生物技术有限公司 一种高产aav的包装质粒及应用

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