JP2022505173A5 - - Google Patents

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Publication number
JP2022505173A5
JP2022505173A5 JP2021521116A JP2021521116A JP2022505173A5 JP 2022505173 A5 JP2022505173 A5 JP 2022505173A5 JP 2021521116 A JP2021521116 A JP 2021521116A JP 2021521116 A JP2021521116 A JP 2021521116A JP 2022505173 A5 JP2022505173 A5 JP 2022505173A5
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JP
Japan
Prior art keywords
grna
dna endonuclease
nucleic acid
functional derivative
goi
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JP2021521116A
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English (en)
Japanese (ja)
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JP7520826B2 (ja
JP2022505173A (ja
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Priority claimed from PCT/US2019/056779 external-priority patent/WO2020081843A1/en
Publication of JP2022505173A publication Critical patent/JP2022505173A/ja
Publication of JP2022505173A5 publication Critical patent/JP2022505173A5/ja
Priority to JP2024110847A priority Critical patent/JP2024161350A/ja
Application granted granted Critical
Publication of JP7520826B2 publication Critical patent/JP7520826B2/ja
Active legal-status Critical Current
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JP2021521116A 2018-10-17 2019-10-17 導入遺伝子を送達するための組成物および方法 Active JP7520826B2 (ja)

Priority Applications (1)

Application Number Priority Date Filing Date Title
JP2024110847A JP2024161350A (ja) 2018-10-17 2024-07-10 導入遺伝子を送達するための組成物および方法

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201862747128P 2018-10-17 2018-10-17
US62/747,128 2018-10-17
PCT/US2019/056779 WO2020081843A1 (en) 2018-10-17 2019-10-17 Compositions and methods for delivering transgenes

Related Child Applications (1)

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JP2024110847A Division JP2024161350A (ja) 2018-10-17 2024-07-10 導入遺伝子を送達するための組成物および方法

Publications (3)

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JP2022505173A JP2022505173A (ja) 2022-01-14
JP2022505173A5 true JP2022505173A5 (enExample) 2022-11-30
JP7520826B2 JP7520826B2 (ja) 2024-07-23

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JP2021521116A Active JP7520826B2 (ja) 2018-10-17 2019-10-17 導入遺伝子を送達するための組成物および方法
JP2024110847A Withdrawn JP2024161350A (ja) 2018-10-17 2024-07-10 導入遺伝子を送達するための組成物および方法

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Country Status (11)

Country Link
US (1) US20210348159A1 (enExample)
EP (1) EP3867377A1 (enExample)
JP (2) JP7520826B2 (enExample)
KR (1) KR20210096088A (enExample)
CN (1) CN113366106A (enExample)
AU (1) AU2019362000A1 (enExample)
BR (1) BR112021007403A2 (enExample)
CA (1) CA3116885A1 (enExample)
IL (1) IL282369A (enExample)
MX (1) MX2021004455A (enExample)
WO (1) WO2020081843A1 (enExample)

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MX2021015122A (es) 2019-06-07 2022-04-06 Regeneron Pharma Animales no humanos que comprenden un locus de albumina humanizado.
US12521451B2 (en) 2019-11-08 2026-01-13 Regeneron Pharmaceuticals, Inc. CRISPR and AAV strategies for x-linked juvenile retinoschisis therapy
MX2023004811A (es) * 2020-10-26 2023-06-29 Res Institute At Nationwide Children´S Hospital Células nk del receptor de antígeno quimérico (car) y usos de las mismas.
CN114496063B (zh) * 2022-01-13 2023-05-23 北京博康健基因科技有限公司 基于天然氨基酸序列的信号肽设计与二级结构从头算建模方法和装置
EP4547230A1 (en) * 2022-06-29 2025-05-07 Juno Therapeutics, Inc. Lipid nanoparticles for delivery of nucleic acids
CN117384880A (zh) * 2022-07-08 2024-01-12 北京干细胞与再生医学研究院 工程化的核酸修饰编辑器
CN117947040A (zh) * 2022-10-31 2024-04-30 苏州荷光科汇生物科技有限公司 用于目的基因的表达盒及其应用
WO2024157194A1 (en) * 2023-01-25 2024-08-02 Crispr Therapeutics Ag Methods and assays for off-target analysis
CN116970087B (zh) * 2023-05-11 2025-01-24 百葵锐(深圳)生物科技有限公司 一种可用于植物叶面定向结合及递送的蛋白rna复合物
EP4574975A1 (en) 2023-12-20 2025-06-25 Bayer AG Compositions and methods for delivering transgenes
WO2026064425A2 (en) 2024-09-17 2026-03-26 Dxome Co., Ltd. Mirror image crispr-cas compositions

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