JP2021519065A5 - - Google Patents

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Publication number
JP2021519065A5
JP2021519065A5 JP2020551357A JP2020551357A JP2021519065A5 JP 2021519065 A5 JP2021519065 A5 JP 2021519065A5 JP 2020551357 A JP2020551357 A JP 2020551357A JP 2020551357 A JP2020551357 A JP 2020551357A JP 2021519065 A5 JP2021519065 A5 JP 2021519065A5
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JP
Japan
Prior art keywords
bone
nucleic acids
inhibitory nucleic
nucleic acid
target
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Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2020551357A
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English (en)
Japanese (ja)
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JP2021519065A (ja
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Publication date
Application filed filed Critical
Priority claimed from PCT/US2019/023759 external-priority patent/WO2019183605A1/en
Publication of JP2021519065A publication Critical patent/JP2021519065A/ja
Publication of JP2021519065A5 publication Critical patent/JP2021519065A5/ja
Pending legal-status Critical Current

Links

JP2020551357A 2018-03-23 2019-03-22 骨障害を処置するための遺伝子治療法 Pending JP2021519065A (ja)

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US201862647595P 2018-03-23 2018-03-23
US62/647,595 2018-03-23
US201962799843P 2019-02-01 2019-02-01
US62/799,843 2019-02-01
PCT/US2019/023759 WO2019183605A1 (en) 2018-03-23 2019-03-22 Gene therapeutics for treating bone disorders

Publications (2)

Publication Number Publication Date
JP2021519065A JP2021519065A (ja) 2021-08-10
JP2021519065A5 true JP2021519065A5 (https=) 2022-03-30

Family

ID=67986628

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2020551357A Pending JP2021519065A (ja) 2018-03-23 2019-03-22 骨障害を処置するための遺伝子治療法

Country Status (8)

Country Link
US (2) US12194108B2 (https=)
EP (2) EP4169576A1 (https=)
JP (1) JP2021519065A (https=)
KR (1) KR20200135433A (https=)
CN (1) CN112368051A (https=)
AU (1) AU2019237514A1 (https=)
CA (1) CA3094217A1 (https=)
WO (1) WO2019183605A1 (https=)

Families Citing this family (8)

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CN113913463B (zh) * 2021-09-19 2023-08-18 郭保生 抑制sost基因表达的重组质粒及其骨靶向重组腺相关病毒与应用
US20250388925A1 (en) * 2021-11-04 2025-12-25 University Of Massachusetts Wnt-modulating gene silencers as bone anabolic therapy for osteoporosis and critical-sized bone defect
WO2024220463A2 (en) * 2023-04-17 2024-10-24 University Of Massachusetts Aav5 capsid with non-canonical amino acid incorporation and uses thereof
CN118453845B (zh) * 2024-05-30 2025-02-14 山东第一医科大学附属省立医院(山东省立医院) 提高dj-1基因表达量的试剂在制备抗血管钙化药物中的应用
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CN121249673B (zh) * 2025-12-05 2026-04-07 北京大学第三医院(北京大学第三临床医学院) 一种靶向ybx1的骨关节炎治疗与诊断产品及应用

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