JP2024512483A5 - - Google Patents
Info
- Publication number
- JP2024512483A5 JP2024512483A5 JP2023557131A JP2023557131A JP2024512483A5 JP 2024512483 A5 JP2024512483 A5 JP 2024512483A5 JP 2023557131 A JP2023557131 A JP 2023557131A JP 2023557131 A JP2023557131 A JP 2023557131A JP 2024512483 A5 JP2024512483 A5 JP 2024512483A5
- Authority
- JP
- Japan
- Prior art keywords
- pkp2
- fold
- cardiomyocytes
- gene therapy
- isoform
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US202163163393P | 2021-03-19 | 2021-03-19 | |
| US63/163,393 | 2021-03-19 | ||
| PCT/EP2022/057145 WO2022195074A2 (en) | 2021-03-19 | 2022-03-18 | Gene therapy composition and treatment of right ventricular arrhythmogenic cardiomyopathy |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2024512483A JP2024512483A (ja) | 2024-03-19 |
| JP2024512483A5 true JP2024512483A5 (https=) | 2025-03-27 |
Family
ID=81384690
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2023557131A Pending JP2024512483A (ja) | 2021-03-19 | 2022-03-18 | 遺伝子治療組成物及び不整脈原性右室心筋症の治療 |
Country Status (12)
| Country | Link |
|---|---|
| US (1) | US20240042059A1 (https=) |
| EP (1) | EP4308172A2 (https=) |
| JP (1) | JP2024512483A (https=) |
| KR (1) | KR20230159471A (https=) |
| CN (1) | CN117715660A (https=) |
| AU (1) | AU2022239846A1 (https=) |
| BR (1) | BR112023018944A2 (https=) |
| CA (1) | CA3212043A1 (https=) |
| IL (1) | IL305959A (https=) |
| MX (1) | MX2023011035A (https=) |
| TW (1) | TW202300180A (https=) |
| WO (1) | WO2022195074A2 (https=) |
Families Citing this family (7)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| EP3947700A4 (en) | 2019-04-01 | 2023-01-04 | Tenaya Therapeutics, Inc. | Adeno-associated virus with engineered capsid |
| KR20230043869A (ko) | 2020-08-07 | 2023-03-31 | 스페이스크래프트 세븐, 엘엘씨 | Aav 벡터를 사용한 플라코필린-2(pkp2) 유전자 요법 |
| BR112023006305A2 (pt) * | 2020-10-09 | 2023-05-09 | Tenaya Therapeutics Inc | Métodos e composições de terapia gênica com placofilina-2 |
| US11781156B2 (en) | 2020-10-09 | 2023-10-10 | Tenaya Therapeutics, Inc. | Plakophillin-2 gene therapy methods and compositions |
| CN115851751A (zh) * | 2022-12-21 | 2023-03-28 | 百世诺（北京）医疗科技有限公司 | 肥厚型心肌病变异基因tnnt2及其应用 |
| WO2025189238A1 (en) * | 2024-03-12 | 2025-09-18 | Murdoch Children's Research Institute | Treatment methods for muscle-associated diseases |
| WO2025238184A1 (en) * | 2024-05-15 | 2025-11-20 | Stichting Amsterdam UMC | Scn10a-short gene therapy to restore cardiac impulse conduction and to protect against cardiac arrhythmia |
Family Cites Families (7)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US12098385B2 (en) * | 2017-09-20 | 2024-09-24 | The Regents Of The University Of California | Gene therapy strategy to restore cardiac electrical and structural function in arrhythmogenic right ventricular cardiomyopathy |
| ES2976559T3 (es) * | 2017-09-20 | 2024-08-05 | Univ California | Terapia génica con conexina 43 para restaurar la función eléctrica y cardíaca y la estructura cardíaca, en la miocardiopatía arritmogénica del ventrículo derecho |
| CN109004092A (zh) | 2018-06-29 | 2018-12-14 | 云谷（固安）科技有限公司 | 有机电致发光器件和有机电致发光装置 |
| TWI897882B (zh) * | 2019-09-20 | 2025-09-21 | 英商Ｕｃｌ商業有限責任公司 | 右心室心律失常性心肌病之基因療法組合物及治療 |
| KR20230043869A (ko) * | 2020-08-07 | 2023-03-31 | 스페이스크래프트 세븐, 엘엘씨 | Aav 벡터를 사용한 플라코필린-2(pkp2) 유전자 요법 |
| BR112023006305A2 (pt) | 2020-10-09 | 2023-05-09 | Tenaya Therapeutics Inc | Métodos e composições de terapia gênica com placofilina-2 |
| US11781156B2 (en) * | 2020-10-09 | 2023-10-10 | Tenaya Therapeutics, Inc. | Plakophillin-2 gene therapy methods and compositions |
-
2022
- 2022-03-18 AU AU2022239846A patent/AU2022239846A1/en active Pending
- 2022-03-18 KR KR1020237034942A patent/KR20230159471A/ko active Pending
- 2022-03-18 MX MX2023011035A patent/MX2023011035A/es unknown
- 2022-03-18 JP JP2023557131A patent/JP2024512483A/ja active Pending
- 2022-03-18 WO PCT/EP2022/057145 patent/WO2022195074A2/en not_active Ceased
- 2022-03-18 TW TW111110077A patent/TW202300180A/zh unknown
- 2022-03-18 CN CN202280034403.0A patent/CN117715660A/zh active Pending
- 2022-03-18 CA CA3212043A patent/CA3212043A1/en active Pending
- 2022-03-18 IL IL305959A patent/IL305959A/en unknown
- 2022-03-18 EP EP22718072.6A patent/EP4308172A2/en active Pending
- 2022-03-18 US US18/282,061 patent/US20240042059A1/en active Pending
- 2022-03-18 BR BR112023018944A patent/BR112023018944A2/pt unknown
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