KR20230159471A - 우심실 부정맥성 심근병증의 유전자 치료 조성물 및 치료 - Google Patents
우심실 부정맥성 심근병증의 유전자 치료 조성물 및 치료 Download PDFInfo
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- KR20230159471A KR20230159471A KR1020237034942A KR20237034942A KR20230159471A KR 20230159471 A KR20230159471 A KR 20230159471A KR 1020237034942 A KR1020237034942 A KR 1020237034942A KR 20237034942 A KR20237034942 A KR 20237034942A KR 20230159471 A KR20230159471 A KR 20230159471A
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- pkp2
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- gene therapy
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- A61K48/0008—Medicinal preparations containing genetic material which is inserted into cells of the living body to treat genetic diseases; Gene therapy characterised by an aspect of the 'non-active' part of the composition delivered, e.g. wherein such 'non-active' part is not delivered simultaneously with the 'active' part of the composition
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- C07K14/46—Peptides having more than 20 amino acids; Gastrins; Somatostatins; Melanotropins; Derivatives thereof from animals; from humans from vertebrates
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| US202163163393P | 2021-03-19 | 2021-03-19 | |
| US63/163,393 | 2021-03-19 | ||
| PCT/EP2022/057145 WO2022195074A2 (en) | 2021-03-19 | 2022-03-18 | Gene therapy composition and treatment of right ventricular arrhythmogenic cardiomyopathy |
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| JP2023538519A (ja) | 2020-08-07 | 2023-09-08 | スペースクラフト セブン リミテッド ライアビリティ カンパニー | Ａａｖベクターを使用したプラコフィリン－２（ｐｋｐ２）遺伝子治療 |
| US11781156B2 (en) | 2020-10-09 | 2023-10-10 | Tenaya Therapeutics, Inc. | Plakophillin-2 gene therapy methods and compositions |
| IL301675A (en) | 2020-10-09 | 2023-05-01 | Tenaya Therapeutics Inc | Methods and preparations for placophilin-2 gene therapy |
| CN115851751A (zh) * | 2022-12-21 | 2023-03-28 | 百世诺（北京）医疗科技有限公司 | 肥厚型心肌病变异基因tnnt2及其应用 |
| WO2025189238A1 (en) * | 2024-03-12 | 2025-09-18 | Murdoch Children's Research Institute | Treatment methods for muscle-associated diseases |
| WO2025238184A1 (en) * | 2024-05-15 | 2025-11-20 | Stichting Amsterdam UMC | Scn10a-short gene therapy to restore cardiac impulse conduction and to protect against cardiac arrhythmia |
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| US12186369B2 (en) * | 2017-09-20 | 2025-01-07 | The Regents Of The University Of California | Gene therapy strategy to restore electrical and cardiac function, and cardiac structure, in arrhythmogenic right ventricular cardiomyopathy |
| US12098385B2 (en) * | 2017-09-20 | 2024-09-24 | The Regents Of The University Of California | Gene therapy strategy to restore cardiac electrical and structural function in arrhythmogenic right ventricular cardiomyopathy |
| CN109004092A (zh) | 2018-06-29 | 2018-12-14 | 云谷（固安）科技有限公司 | 有机电致发光器件和有机电致发光装置 |
| KR20220066914A (ko) * | 2019-09-20 | 2022-05-24 | 유씨엘 비즈니스 리미티드 | 부정맥 유발성 우심실 심근병증의 유전자 요법 조성물 및 치료 |
| JP2023538519A (ja) * | 2020-08-07 | 2023-09-08 | スペースクラフト セブン リミテッド ライアビリティ カンパニー | Ａａｖベクターを使用したプラコフィリン－２（ｐｋｐ２）遺伝子治療 |
| US11781156B2 (en) * | 2020-10-09 | 2023-10-10 | Tenaya Therapeutics, Inc. | Plakophillin-2 gene therapy methods and compositions |
| IL301675A (en) * | 2020-10-09 | 2023-05-01 | Tenaya Therapeutics Inc | Methods and preparations for placophilin-2 gene therapy |
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