JP2021515572A5 - - Google Patents

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Publication number
JP2021515572A5
JP2021515572A5 JP2020548674A JP2020548674A JP2021515572A5 JP 2021515572 A5 JP2021515572 A5 JP 2021515572A5 JP 2020548674 A JP2020548674 A JP 2020548674A JP 2020548674 A JP2020548674 A JP 2020548674A JP 2021515572 A5 JP2021515572 A5 JP 2021515572A5
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JP
Japan
Prior art keywords
aavrh74
modified
recombinant
cells
item
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Granted
Application number
JP2020548674A
Other languages
English (en)
Japanese (ja)
Other versions
JP2021515572A (ja
JP7304878B2 (ja
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Publication date
Application filed filed Critical
Priority claimed from PCT/US2019/022353 external-priority patent/WO2019178412A1/en
Publication of JP2021515572A publication Critical patent/JP2021515572A/ja
Publication of JP2021515572A5 publication Critical patent/JP2021515572A5/ja
Priority to JP2023104920A priority Critical patent/JP2023115149A/ja
Application granted granted Critical
Publication of JP7304878B2 publication Critical patent/JP7304878B2/ja
Priority to JP2024117744A priority patent/JP2024144521A/ja
Active legal-status Critical Current
Anticipated expiration legal-status Critical

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JP2020548674A 2018-03-16 2019-03-14 キャプシド改変による組織特異的遺伝子送達の増加 Active JP7304878B2 (ja)

Priority Applications (2)

Application Number Priority Date Filing Date Title
JP2023104920A JP2023115149A (ja) 2018-03-16 2023-06-27 キャプシド改変による組織特異的遺伝子送達の増加
JP2024117744A JP2024144521A (ja) 2018-03-16 2024-07-23 キャプシド改変による組織特異的遺伝子送達の増加

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201862644317P 2018-03-16 2018-03-16
US62/644,317 2018-03-16
PCT/US2019/022353 WO2019178412A1 (en) 2018-03-16 2019-03-14 Increasing tissue specific gene delivery by capsid modification

Related Child Applications (1)

Application Number Title Priority Date Filing Date
JP2023104920A Division JP2023115149A (ja) 2018-03-16 2023-06-27 キャプシド改変による組織特異的遺伝子送達の増加

Publications (3)

Publication Number Publication Date
JP2021515572A JP2021515572A (ja) 2021-06-24
JP2021515572A5 true JP2021515572A5 (https=) 2022-03-03
JP7304878B2 JP7304878B2 (ja) 2023-07-07

Family

ID=67906893

Family Applications (3)

Application Number Title Priority Date Filing Date
JP2020548674A Active JP7304878B2 (ja) 2018-03-16 2019-03-14 キャプシド改変による組織特異的遺伝子送達の増加
JP2023104920A Pending JP2023115149A (ja) 2018-03-16 2023-06-27 キャプシド改変による組織特異的遺伝子送達の増加
JP2024117744A Pending JP2024144521A (ja) 2018-03-16 2024-07-23 キャプシド改変による組織特異的遺伝子送達の増加

Family Applications After (2)

Application Number Title Priority Date Filing Date
JP2023104920A Pending JP2023115149A (ja) 2018-03-16 2023-06-27 キャプシド改変による組織特異的遺伝子送達の増加
JP2024117744A Pending JP2024144521A (ja) 2018-03-16 2024-07-23 キャプシド改変による組織特異的遺伝子送達の増加

Country Status (11)

Country Link
US (2) US12385062B2 (https=)
EP (1) EP3765624A4 (https=)
JP (3) JP7304878B2 (https=)
KR (3) KR20250111395A (https=)
CN (2) CN111819286B (https=)
AU (2) AU2019234918C1 (https=)
BR (1) BR112020018354A2 (https=)
CA (3) CA3293599A1 (https=)
IL (2) IL317905A (https=)
SG (1) SG11202008687XA (https=)
WO (1) WO2019178412A1 (https=)

Families Citing this family (12)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
ES2865487T3 (es) 2015-09-28 2021-10-15 Univ North Carolina Chapel Hill Métodos y composiciones para vectores virales que evaden los anticuerpos
EP3765624A4 (en) * 2018-03-16 2022-05-25 Research Institute at Nationwide Children's Hospital Increasing tissue specific gene delivery by capsid modification
EP3774852A1 (en) 2018-04-03 2021-02-17 Stridebio, Inc. Antibody-evading virus vectors
MX2020010465A (es) 2018-04-03 2021-01-08 Vectores de virus para direccionamiento a tejidos oftalmicos.
AU2019247748A1 (en) 2018-04-03 2020-10-08 Ginkgo Bioworks, Inc. Antibody-evading virus vectors
AR118465A1 (es) 2019-03-21 2021-10-06 Stridebio Inc Vectores de virus adenoasociados recombinantes
US12611436B2 (en) 2019-10-17 2026-04-28 Sarepta Therapeutics, Inc. AAV transfer cassette
JP2022551739A (ja) 2019-10-17 2022-12-13 ストライドバイオ,インコーポレイテッド ニーマン・ピック病c型の治療のためのアデノ随伴ウイルスベクター
AU2021328475A1 (en) 2020-08-19 2023-03-16 Sarepta Therapeutics, Inc. Adeno-associated virus vectors for treatment of Rett syndrome
US20240299586A1 (en) * 2021-05-06 2024-09-12 The Regents Of The University Of California Novel aav serotypes derived from a library screen
WO2023196862A1 (en) 2022-04-06 2023-10-12 Genzyme Corporation Targeted gene therapy for dm-1 myotonic dystrophy
US20240384271A1 (en) * 2023-04-05 2024-11-21 Genzyme Corporation Targeted gene therapy for dm-1 myotonic dystrophy

Family Cites Families (12)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US5846782A (en) * 1995-11-28 1998-12-08 Genvec, Inc. Targeting adenovirus with use of constrained peptide motifs
EP2345731B1 (en) * 2003-09-30 2015-10-21 The Trustees of the University of Pennsylvania Adeno-associated virus (AAV) clades, sequences, vectors containing same, and uses thereof
WO2012109570A1 (en) 2011-02-10 2012-08-16 The University Of North Carolina At Chapel Hill Viral vectors with modified transduction profiles and methods of making and using the same
NZ701693A (en) * 2012-04-18 2017-02-24 The Children’S Hospital Of Philadelphia Composition and methods for highly efficient gene transfer using aav capsid variants
IL297919A (en) * 2013-07-22 2023-01-01 Childrens Hospital Philadelphia Variant aav and compositions, methods and uses for gene transfer to cells, organs and tissues
GB201403684D0 (en) * 2014-03-03 2014-04-16 King S College London Vector
CN107073051B (zh) * 2014-10-21 2021-08-24 马萨诸塞大学 重组aav变体及其用途
ES2865487T3 (es) * 2015-09-28 2021-10-15 Univ North Carolina Chapel Hill Métodos y composiciones para vectores virales que evaden los anticuerpos
ES2977730T3 (es) * 2016-04-15 2024-08-29 Res Inst Nationwide Childrens Hospital Administración de microARN-29 y micro-distrofina por virus adenoasociado para tratar la distrofia muscular
US11364308B2 (en) * 2016-05-13 2022-06-21 4D Molecular Therapeutics Inc. Adeno-associated virus variant capsids and methods of use thereof
EP3765624A4 (en) * 2018-03-16 2022-05-25 Research Institute at Nationwide Children's Hospital Increasing tissue specific gene delivery by capsid modification
BR112021003174A2 (pt) * 2018-08-30 2021-05-11 Research Institute At Nationwide Children's Hospital terapia gênica para o tratamento de galactosemia

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