JP2025512534A5 - - Google Patents

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Publication number
JP2025512534A5
JP2025512534A5 JP2024560842A JP2024560842A JP2025512534A5 JP 2025512534 A5 JP2025512534 A5 JP 2025512534A5 JP 2024560842 A JP2024560842 A JP 2024560842A JP 2024560842 A JP2024560842 A JP 2024560842A JP 2025512534 A5 JP2025512534 A5 JP 2025512534A5
Authority
JP
Japan
Prior art keywords
seq
amino acid
positions
acid sequence
capsid polypeptide
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2024560842A
Other languages
English (en)
Japanese (ja)
Other versions
JP2025512534A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2023/065815 external-priority patent/WO2023201364A2/en
Publication of JP2025512534A publication Critical patent/JP2025512534A/ja
Publication of JP2025512534A5 publication Critical patent/JP2025512534A5/ja
Pending legal-status Critical Current

Links

JP2024560842A 2022-04-15 2023-04-14 カプシドバリアント及びそれを使用する方法 Pending JP2025512534A (ja)

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US202263331543P 2022-04-15 2022-04-15
US63/331,543 2022-04-15
US202363443262P 2023-02-03 2023-02-03
US63/443,262 2023-02-03
PCT/US2023/065815 WO2023201364A2 (en) 2022-04-15 2023-04-14 Capsid variants and methods of using the same

Publications (2)

Publication Number Publication Date
JP2025512534A JP2025512534A (ja) 2025-04-17
JP2025512534A5 true JP2025512534A5 (https=) 2026-04-21

Family

ID=88330421

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2024560842A Pending JP2025512534A (ja) 2022-04-15 2023-04-14 カプシドバリアント及びそれを使用する方法

Country Status (10)

Country Link
US (1) US20250250305A1 (https=)
EP (1) EP4508064A2 (https=)
JP (1) JP2025512534A (https=)
KR (1) KR20250011900A (https=)
CN (1) CN119630688A (https=)
AU (1) AU2023253718A1 (https=)
CA (1) CA3255976A1 (https=)
IL (1) IL316205A (https=)
MX (1) MX2024012615A (https=)
WO (1) WO2023201364A2 (https=)

Families Citing this family (1)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
CN120699111B (zh) * 2025-08-26 2025-12-30 朗信启昇(苏州)生物制药有限公司 增强型aav载体及其应用

Family Cites Families (4)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US11021519B2 (en) * 2015-03-02 2021-06-01 Adverum Biotechnologies, Inc. Compositions and methods for intravitreal delivery of polynucleotides to retinal cones
US11364308B2 (en) * 2016-05-13 2022-06-21 4D Molecular Therapeutics Inc. Adeno-associated virus variant capsids and methods of use thereof
JP2023535632A (ja) * 2020-07-27 2023-08-18 アンジャリウム バイオサイエンシズ エージー Dna分子の組成物、その作製方法、及びその使用方法
IL308987A (en) * 2021-06-03 2024-01-01 Dyno Therapeutics Inc Capsid variants and methods of using them

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