JP2020537637A5 - - Google Patents

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JP2020537637A5
JP2020537637A5 JP2020516820A JP2020516820A JP2020537637A5 JP 2020537637 A5 JP2020537637 A5 JP 2020537637A5 JP 2020516820 A JP2020516820 A JP 2020516820A JP 2020516820 A JP2020516820 A JP 2020516820A JP 2020537637 A5 JP2020537637 A5 JP 2020537637A5
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suspension
immunosuppressant
raav
use according
hids
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JP2020516820A
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JP2020537637A (ja
JP7449223B2 (ja
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Priority claimed from PCT/US2018/052129 external-priority patent/WO2019060662A1/en
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Priority to JP2024031557A priority Critical patent/JP2024063154A/ja
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JP2020516820A 2017-09-22 2018-09-21 ムコ多糖症ii型を治療するための遺伝子療法 Active JP7449223B2 (ja)

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JP2024031557A JP2024063154A (ja) 2017-09-22 2024-03-01 ムコ多糖症ii型を治療するための遺伝子療法

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Application Number Priority Date Filing Date Title
US201762561769P 2017-09-22 2017-09-22
US201762562179P 2017-09-22 2017-09-22
US62/561,769 2017-09-22
US62/562,179 2017-09-22
US201762573841P 2017-10-18 2017-10-18
US62/573,841 2017-10-18
PCT/US2018/052129 WO2019060662A1 (en) 2017-09-22 2018-09-21 GENE THERAPY FOR THE TREATMENT OF MUCOPOLYSACCHARIDOSE TYPE II

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JP2020537637A JP2020537637A (ja) 2020-12-24
JP2020537637A5 true JP2020537637A5 (https=) 2021-10-21
JP7449223B2 JP7449223B2 (ja) 2024-03-13

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JP2020516820A Active JP7449223B2 (ja) 2017-09-22 2018-09-21 ムコ多糖症ii型を治療するための遺伝子療法
JP2024031557A Pending JP2024063154A (ja) 2017-09-22 2024-03-01 ムコ多糖症ii型を治療するための遺伝子療法

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US (3) US11819539B2 (https=)
EP (1) EP3684938A1 (https=)
JP (2) JP7449223B2 (https=)
KR (2) KR102883778B1 (https=)
AU (1) AU2018335752B2 (https=)
BR (1) BR112020005249A2 (https=)
CA (1) CA3076036A1 (https=)
IL (1) IL273427B2 (https=)
SG (1) SG11202002457RA (https=)
TW (1) TWI835747B (https=)
WO (1) WO2019060662A1 (https=)

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CN115820740A (zh) * 2021-09-16 2023-03-21 北京锦篮基因科技有限公司 用于治疗ⅱ型粘多糖贮积症的重组腺相关病毒载体及其应用
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