JP2020537637A5 - - Google Patents

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JP2020537637A5
JP2020537637A5 JP2020516820A JP2020516820A JP2020537637A5 JP 2020537637 A5 JP2020537637 A5 JP 2020537637A5 JP 2020516820 A JP2020516820 A JP 2020516820A JP 2020516820 A JP2020516820 A JP 2020516820A JP 2020537637 A5 JP2020537637 A5 JP 2020537637A5
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suspension
immunosuppressant
raav
use according
hids
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JP2020516820A
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JP7449223B2 (ja
JP2020537637A (ja
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Priority claimed from PCT/US2018/052129 external-priority patent/WO2019060662A1/en
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Priority to JP2024031557A priority Critical patent/JP2024063154A/ja
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JP2020516820A 2017-09-22 2018-09-21 ムコ多糖症ii型を治療するための遺伝子療法 Active JP7449223B2 (ja)

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JP2024031557A JP2024063154A (ja) 2017-09-22 2024-03-01 ムコ多糖症ii型を治療するための遺伝子療法

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Application Number Priority Date Filing Date Title
US201762561769P 2017-09-22 2017-09-22
US201762562179P 2017-09-22 2017-09-22
US62/561,769 2017-09-22
US62/562,179 2017-09-22
US201762573841P 2017-10-18 2017-10-18
US62/573,841 2017-10-18
PCT/US2018/052129 WO2019060662A1 (en) 2017-09-22 2018-09-21 GENE THERAPY FOR THE TREATMENT OF MUCOPOLYSACCHARIDOSE TYPE II

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JP2020537637A JP2020537637A (ja) 2020-12-24
JP2020537637A5 true JP2020537637A5 (https=) 2021-10-21
JP7449223B2 JP7449223B2 (ja) 2024-03-13

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JP2024031557A Pending JP2024063154A (ja) 2017-09-22 2024-03-01 ムコ多糖症ii型を治療するための遺伝子療法

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US (3) US11819539B2 (https=)
EP (1) EP3684938A1 (https=)
JP (2) JP7449223B2 (https=)
KR (2) KR20250161673A (https=)
AU (1) AU2018335752B2 (https=)
BR (1) BR112020005249A2 (https=)
CA (1) CA3076036A1 (https=)
IL (1) IL273427B2 (https=)
SG (1) SG11202002457RA (https=)
TW (1) TWI835747B (https=)
WO (1) WO2019060662A1 (https=)

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KR102719222B1 (ko) 2017-05-11 2024-10-21 더 트러스티스 오브 더 유니버시티 오브 펜실베니아 신경 세로이드 지질갈색소증에 대한 유전자 요법
MA50016A (fr) 2017-07-06 2020-07-08 Univ Pennsylvania Thérapie génique médiée par aav9 pour traiter la mucopolysaccharidose de type i
TWI835747B (zh) 2017-09-22 2024-03-21 賓州大學委員會 用於治療黏多醣病 ii 型之基因治療
IL280198B2 (en) 2018-07-18 2026-01-01 Regenxbio Inc Treatment of mucopolysaccharidosis I with fully glycosylated human iduronidase-alpha-L (idus)
US20240084917A1 (en) 2019-10-07 2024-03-14 Wartsila Services Switzerland Ltd. Step lift control of hydraulically actuated popped valves
WO2021150570A1 (en) 2020-01-22 2021-07-29 Regenxbio Inc. Treatment of mucopolysaccharidosis i with fully-human glycosylated human alpha-l-iduronidase (idua)

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