JP2020105169A5 - - Google Patents

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Publication number
JP2020105169A5
JP2020105169A5 JP2019227342A JP2019227342A JP2020105169A5 JP 2020105169 A5 JP2020105169 A5 JP 2020105169A5 JP 2019227342 A JP2019227342 A JP 2019227342A JP 2019227342 A JP2019227342 A JP 2019227342A JP 2020105169 A5 JP2020105169 A5 JP 2020105169A5
Authority
JP
Japan
Prior art keywords
composition
lysosomal enzyme
expression vector
vlp
lysosomal
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2019227342A
Other languages
English (en)
Japanese (ja)
Other versions
JP2020105169A (ja
Filing date
Publication date
Priority claimed from PCT/EP2018/085699 external-priority patent/WO2020125962A1/en
Application filed filed Critical
Publication of JP2020105169A publication Critical patent/JP2020105169A/ja
Publication of JP2020105169A5 publication Critical patent/JP2020105169A5/ja
Pending legal-status Critical Current

Links

JP2019227342A 2018-12-18 2019-12-17 リソソーム蓄積症の処置のためのvlp Pending JP2020105169A (ja)

Applications Claiming Priority (4)

Application Number Priority Date Filing Date Title
PCT/EP2018/085699 WO2020125962A1 (en) 2018-12-18 2018-12-18 A novel drug delivery system and methods providing thereof
WOPCT/EP2018/085699 2018-12-18
WOPCT/EP2019/060814 2019-04-26
PCT/EP2019/060814 WO2020126116A1 (en) 2018-12-18 2019-04-26 Vlp for the treatment of a lysosomal storage disease

Publications (2)

Publication Number Publication Date
JP2020105169A JP2020105169A (ja) 2020-07-09
JP2020105169A5 true JP2020105169A5 (enExample) 2022-12-26

Family

ID=65009711

Family Applications (3)

Application Number Title Priority Date Filing Date
JP2019538254A Expired - Fee Related JP6884432B2 (ja) 2018-12-18 2018-12-18 新規薬物送達システムおよびそれを提供する方法
JP2019227342A Pending JP2020105169A (ja) 2018-12-18 2019-12-17 リソソーム蓄積症の処置のためのvlp
JP2022521659A Pending JP2022551531A (ja) 2018-12-18 2020-10-13 John CunninghamウイルスVLPを提供するための方法

Family Applications Before (1)

Application Number Title Priority Date Filing Date
JP2019538254A Expired - Fee Related JP6884432B2 (ja) 2018-12-18 2018-12-18 新規薬物送達システムおよびそれを提供する方法

Family Applications After (1)

Application Number Title Priority Date Filing Date
JP2022521659A Pending JP2022551531A (ja) 2018-12-18 2020-10-13 John CunninghamウイルスVLPを提供するための方法

Country Status (12)

Country Link
US (4) US11279938B2 (enExample)
EP (2) EP3688147B8 (enExample)
JP (3) JP6884432B2 (enExample)
CN (3) CN111587289B (enExample)
BR (3) BR112019014209A2 (enExample)
CA (3) CA3049197C (enExample)
DK (1) DK3688147T3 (enExample)
ES (1) ES2933275T3 (enExample)
HU (1) HUE060952T2 (enExample)
PL (1) PL3688147T3 (enExample)
SI (1) SI3688147T1 (enExample)
WO (4) WO2020125962A1 (enExample)

Families Citing this family (6)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US20230310652A1 (en) * 2020-05-22 2023-10-05 Neuway Pharma Gmbh Vlp for the treatment of leukodystrophies
WO2022227287A1 (zh) * 2021-04-25 2022-11-03 中南大学 Dnj及其衍生物在制备预防和/或治疗肺动脉高压药物中的应用
CN115448980A (zh) * 2021-06-08 2022-12-09 戴德森医疗财团法人嘉义基督教医院 表面链结标靶多肽的类病毒颗粒及其用途
EP4166672A1 (en) 2021-10-15 2023-04-19 NEUWAY Pharma GmbH A novel method for purification of protein- or peptide-based capsules
CN116554279A (zh) * 2022-01-28 2023-08-08 思凯生科有限公司 包含有专一性表达于前列腺细胞的表达质粒的类病毒颗粒及其用途
WO2024079361A1 (en) 2022-10-14 2024-04-18 Neuway Pharma Gmbh A PROTEIN- OR PEPTIDE-BASED CAPSULE (PPC), PREFERABLY A VLP, LOADED WITH A MESSENGER RNA (mRNA) AND A METHOD OF PRODUCTION AND PURIFICATION THEREOF

Family Cites Families (7)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
DE19543553B4 (de) 1995-11-22 2009-04-09 Deutsches Primatenzentrum Gmbh VP-Antigene des JC-Virus
ES2496493T3 (es) 2002-01-11 2014-09-19 Bioasis Technologies Inc. Uso de p97 como sistema de administración de enzimas para la administración de enzimas lisosómicas terapéuticas
US7442372B2 (en) 2003-08-29 2008-10-28 Biomarin Pharmaceutical Inc. Delivery of therapeutic compounds to the brain and other tissues
FR2920158B1 (fr) 2007-08-24 2010-03-12 Centre Nat Rech Scient Production de plasmides et expression de proteines recombinantes dans des cellules cultivees sans antibiotiques
EP2554664A1 (de) 2011-08-02 2013-02-06 Life Science Inkubator Verfahren zur Aufreinigung von Virus-ähnlichen Partikeln (VLP)
EP2636746A1 (en) 2012-03-06 2013-09-11 Life Science Inkubator A novel drug delivery system based on JCV-VLP
US11149285B2 (en) * 2014-05-14 2021-10-19 Universitat Autónoma De Barcelona Adenoassociated virus vectors for the treatment of lysosomal storage disorders

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