JP2018538261A5 - - Google Patents
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- JP2018538261A5 JP2018538261A5 JP2018524411A JP2018524411A JP2018538261A5 JP 2018538261 A5 JP2018538261 A5 JP 2018538261A5 JP 2018524411 A JP2018524411 A JP 2018524411A JP 2018524411 A JP2018524411 A JP 2018524411A JP 2018538261 A5 JP2018538261 A5 JP 2018538261A5
- Authority
- JP
- Japan
- Prior art keywords
- composition
- item
- subject
- seq
- recombinant aav
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
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Priority Applications (1)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| JP2021086103A JP7307121B2 (ja) | 2015-11-12 | 2021-05-21 | 筋ジストロフィーの治療方法 |
Applications Claiming Priority (5)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201562254539P | 2015-11-12 | 2015-11-12 | |
| US62/254,539 | 2015-11-12 | ||
| US201662419793P | 2016-11-09 | 2016-11-09 | |
| US62/419,793 | 2016-11-09 | ||
| PCT/US2016/061703 WO2017083776A1 (en) | 2015-11-12 | 2016-11-11 | Methods of treating muscular dystrophy |
Related Child Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2021086103A Division JP7307121B2 (ja) | 2015-11-12 | 2021-05-21 | 筋ジストロフィーの治療方法 |
Publications (3)
| Publication Number | Publication Date |
|---|---|
| JP2018538261A JP2018538261A (ja) | 2018-12-27 |
| JP2018538261A5 true JP2018538261A5 (https=) | 2019-12-19 |
| JP6889717B2 JP6889717B2 (ja) | 2021-06-18 |
Family
ID=58696162
Family Applications (3)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2018524411A Active JP6889717B2 (ja) | 2015-11-12 | 2016-11-11 | 筋ジストロフィーの治療方法 |
| JP2021086103A Active JP7307121B2 (ja) | 2015-11-12 | 2021-05-21 | 筋ジストロフィーの治療方法 |
| JP2023076538A Withdrawn JP2023099184A (ja) | 2015-11-12 | 2023-05-08 | 筋ジストロフィーの治療方法 |
Family Applications After (2)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2021086103A Active JP7307121B2 (ja) | 2015-11-12 | 2021-05-21 | 筋ジストロフィーの治療方法 |
| JP2023076538A Withdrawn JP2023099184A (ja) | 2015-11-12 | 2023-05-08 | 筋ジストロフィーの治療方法 |
Country Status (21)
| Country | Link |
|---|---|
| US (2) | US11820972B2 (https=) |
| EP (1) | EP3373980B1 (https=) |
| JP (3) | JP6889717B2 (https=) |
| KR (1) | KR102821290B1 (https=) |
| CN (1) | CN108883200B (https=) |
| AU (3) | AU2016354561B2 (https=) |
| BR (1) | BR112018009657A2 (https=) |
| CA (1) | CA3005240A1 (https=) |
| CO (1) | CO2018005928A2 (https=) |
| DK (1) | DK3373980T3 (https=) |
| EA (1) | EA201891134A1 (https=) |
| ES (1) | ES3034857T3 (https=) |
| FI (1) | FI3373980T3 (https=) |
| HR (1) | HRP20250923T1 (https=) |
| IL (1) | IL259178B (https=) |
| MX (1) | MX2018005882A (https=) |
| RU (1) | RU2761264C2 (https=) |
| SG (1) | SG11201803971UA (https=) |
| TN (2) | TN2018000163A1 (https=) |
| WO (1) | WO2017083776A1 (https=) |
| ZA (1) | ZA201803080B (https=) |
Families Citing this family (8)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| WO2019012336A2 (en) | 2017-03-17 | 2019-01-17 | Newcastle University | ADENO-ASSOCIATED VIRAL VECTOR DELIVERY OF A MICRO-DYSTROPHIN FRAGMENT FOR TREATING MUSCLE DYSTROPHY |
| EP3687565A1 (en) | 2017-09-27 | 2020-08-05 | Alexion Pharmaceuticals, Inc. | Methods of improving cardiovascular function and treating cardiovascular disease using a recombinant ectonucleotide pyrophosphatase phosphodiesterase (npp1) |
| AU2018351528B2 (en) | 2017-10-20 | 2025-02-27 | Research Institute At Nationwide Children's Hospital | Methods and materials for NT-3 gene therapy |
| CN120393053A (zh) | 2018-06-18 | 2025-08-01 | 全国儿童医院研究所 | 用于治疗肌营养不良的肌肉特异性微小肌营养不良蛋白的腺相关病毒载体递送 |
| AU2019419494B2 (en) * | 2018-12-31 | 2026-03-26 | Research Institute At Nationwide Children's Hospital | DUX4 RNA silencing using RNA targeting CRISPR-Cas13b |
| EP4164668A1 (en) | 2020-06-15 | 2023-04-19 | Research Institute at Nationwide Children's Hospital | Adeno-associated virus vector delivery for muscular dystrophies |
| KR102732922B1 (ko) * | 2021-10-29 | 2024-11-20 | 충남대학교 산학협력단 | 과산화수소수 처리에 의해 유용성분 함량이 증진된 상추의 재배방법 |
| CN117223686B (zh) * | 2023-11-15 | 2024-01-23 | 四川省农业机械科学研究院 | 一种扩座除砂一体化蚕盘及养蚕方法 |
Family Cites Families (19)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| IE58011B1 (en) | 1983-05-27 | 1993-06-16 | Texas A & M Univ Sys | Method for producing a recombinant baculovirus expression vector |
| ZA848495B (en) | 1984-01-31 | 1985-09-25 | Idaho Res Found | Production of polypeptides in insect cells |
| US6204059B1 (en) | 1994-06-30 | 2001-03-20 | University Of Pittsburgh | AAV capsid vehicles for molecular transfer |
| AU2002248297A1 (en) | 2001-01-05 | 2002-07-16 | Children's Hospital, Inc. | Aav2 vectors and methods |
| WO2003074714A1 (en) | 2002-03-05 | 2003-09-12 | Stichting Voor De Technische Wetenschappen | Baculovirus expression system |
| JP2006121961A (ja) | 2004-10-28 | 2006-05-18 | Univ Of Tokushima | 顎骨骨幹異形成症ｇｄｄの原因遺伝子ｇｄｄ１とその用途 |
| US20100120627A1 (en) | 2006-08-02 | 2010-05-13 | Abdelmajid Belouchi | Genemap of the human genes associated with psoriasis |
| FR2919305B1 (fr) | 2007-07-26 | 2009-09-18 | Genethon Ass Loi De 1901 | Vecteurs viraux adeno-associes pour l'expression de la dysferline. |
| GB0715087D0 (en) | 2007-08-03 | 2007-09-12 | Summit Corp Plc | Drug combinations for the treatment of duchenne muscular dystrophy |
| US20100026655A1 (en) | 2008-07-31 | 2010-02-04 | Avago Technologies Ecbu Ip (Singapore) Pte. Ltd. | Capacitive Touchscreen or Touchpad for Finger or Stylus |
| US8946451B2 (en) * | 2009-10-05 | 2015-02-03 | Catabasis Pharmaceuticals, Inc. | Lipoic acid acylated salicylate derivatives and their uses |
| KR20120099709A (ko) | 2009-11-03 | 2012-09-11 | 더 리전츠 오브 더 유니버시티 오브 캘리포니아 | 하나 이상의 표면 위의 아연 산화물 나노로드 어레이들을 이용하는 발광 다이오드 구조물 및 이러한 아연 산화물 나노로드 어레이들을 저비용으로 제조하는 방법 |
| US9434928B2 (en) * | 2011-11-23 | 2016-09-06 | Nationwide Children's Hospital, Inc. | Recombinant adeno-associated virus delivery of alpha-sarcoglycan polynucleotides |
| AU2013243948A1 (en) | 2012-04-02 | 2014-10-30 | Moderna Therapeutics, Inc. | Modified polynucleotides for the production of proteins associated with human disease |
| EP2893038A1 (en) | 2012-09-07 | 2015-07-15 | INSERM - Institut National de la Santé et de la Recherche Médicale | In vitro genetic diagnostic of inherited neuromuscular disorders |
| US9624282B2 (en) | 2012-11-26 | 2017-04-18 | The Curators Of The University Of Missouri | Microdystrophin peptides and methods for treating muscular dystrophy using the same |
| ITTO20130669A1 (it) | 2013-08-05 | 2015-02-06 | Consiglio Nazionale Ricerche | Vettore adeno-associato ricombinante muscolo-specifico e suo impiego nel trattamento di patologie muscolari |
| HUE037179T2 (hu) * | 2013-10-08 | 2018-08-28 | Ystem S R L | Gyógyászati kompozíciók izom-rendellenességek kezelésére |
| US9850497B2 (en) * | 2013-11-04 | 2017-12-26 | Regents Of The University Of Minnesota | Gene targeting methods and tools |
-
2016
- 2016-11-11 FI FIEP16865168.5T patent/FI3373980T3/fi active
- 2016-11-11 TN TNP/2018/000163A patent/TN2018000163A1/en unknown
- 2016-11-11 BR BR112018009657-1A patent/BR112018009657A2/pt active IP Right Grant
- 2016-11-11 CA CA3005240A patent/CA3005240A1/en active Pending
- 2016-11-11 DK DK16865168.5T patent/DK3373980T3/da active
- 2016-11-11 EP EP16865168.5A patent/EP3373980B1/en active Active
- 2016-11-11 RU RU2018121289A patent/RU2761264C2/ru active
- 2016-11-11 HR HRP20250923TT patent/HRP20250923T1/hr unknown
- 2016-11-11 KR KR1020187016152A patent/KR102821290B1/ko active Active
- 2016-11-11 IL IL259178A patent/IL259178B/en unknown
- 2016-11-11 MX MX2018005882A patent/MX2018005882A/es unknown
- 2016-11-11 CN CN201680079597.0A patent/CN108883200B/zh active Active
- 2016-11-11 JP JP2018524411A patent/JP6889717B2/ja active Active
- 2016-11-11 AU AU2016354561A patent/AU2016354561B2/en active Active
- 2016-11-11 ES ES16865168T patent/ES3034857T3/es active Active
- 2016-11-11 EA EA201891134A patent/EA201891134A1/ru unknown
- 2016-11-11 TN TNP/2019/000279A patent/TN2019000279A1/en unknown
- 2016-11-11 SG SG11201803971UA patent/SG11201803971UA/en unknown
- 2016-11-11 US US15/775,566 patent/US11820972B2/en active Active
- 2016-11-11 WO PCT/US2016/061703 patent/WO2017083776A1/en not_active Ceased
-
2018
- 2018-05-10 ZA ZA2018/03080A patent/ZA201803080B/en unknown
- 2018-06-08 CO CONC2018/0005928A patent/CO2018005928A2/es unknown
-
2021
- 2021-05-21 JP JP2021086103A patent/JP7307121B2/ja active Active
-
2022
- 2022-03-02 AU AU2022201427A patent/AU2022201427B2/en active Active
-
2023
- 2023-05-08 JP JP2023076538A patent/JP2023099184A/ja not_active Withdrawn
- 2023-11-17 US US18/513,227 patent/US20240191250A1/en active Pending
-
2025
- 2025-07-22 AU AU2025206419A patent/AU2025206419A1/en active Pending
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