JP2019513393A5 - - Google Patents

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JP2019513393A5
JP2019513393A5 JP2018553951A JP2018553951A JP2019513393A5 JP 2019513393 A5 JP2019513393 A5 JP 2019513393A5 JP 2018553951 A JP2018553951 A JP 2018553951A JP 2018553951 A JP2018553951 A JP 2018553951A JP 2019513393 A5 JP2019513393 A5 JP 2019513393A5
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composition
recombinant aav
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muscular dystrophy
vector
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JP2018553951A
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Japanese (ja)
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JP2019513393A (ja
JP7078546B2 (ja
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Priority claimed from PCT/US2017/027636 external-priority patent/WO2017181015A1/en
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Publication of JP2019513393A5 publication Critical patent/JP2019513393A5/ja
Priority to JP2021190072A priority Critical patent/JP7431789B2/ja
Application granted granted Critical
Publication of JP7078546B2 publication Critical patent/JP7078546B2/ja
Priority to JP2023201579A priority patent/JP7833440B2/ja
Priority to JP2025075669A priority patent/JP2025118741A/ja
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JP2018553951A 2016-04-15 2017-04-14 筋ジストロフィーを治療するためのマイクロジストロフィンのアデノ随伴ウイルスベクター送達 Active JP7078546B2 (ja)

Priority Applications (3)

Application Number Priority Date Filing Date Title
JP2021190072A JP7431789B2 (ja) 2016-04-15 2021-11-24 筋ジストロフィーを治療するためのマイクロジストロフィンのアデノ随伴ウイルスベクター送達
JP2023201579A JP7833440B2 (ja) 2016-04-15 2023-11-29 筋ジストロフィーを治療するためのマイクロジストロフィンのアデノ随伴ウイルスベクター送達
JP2025075669A JP2025118741A (ja) 2016-04-15 2025-04-30 筋ジストロフィーを治療するためのマイクロジストロフィンのアデノ随伴ウイルスベクター送達

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US201662323163P 2016-04-15 2016-04-15
US62/323,163 2016-04-15
US201762473253P 2017-03-17 2017-03-17
US62/473,253 2017-03-17
PCT/US2017/027636 WO2017181015A1 (en) 2016-04-15 2017-04-14 Adeno-associated virus vector delivery of micro-dystrophin to treat muscular dystrophy

Related Child Applications (1)

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JP2021190072A Division JP7431789B2 (ja) 2016-04-15 2021-11-24 筋ジストロフィーを治療するためのマイクロジストロフィンのアデノ随伴ウイルスベクター送達

Publications (3)

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JP2019513393A JP2019513393A (ja) 2019-05-30
JP2019513393A5 true JP2019513393A5 (https=) 2020-05-28
JP7078546B2 JP7078546B2 (ja) 2022-05-31

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ID=60041940

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Application Number Title Priority Date Filing Date
JP2018553951A Active JP7078546B2 (ja) 2016-04-15 2017-04-14 筋ジストロフィーを治療するためのマイクロジストロフィンのアデノ随伴ウイルスベクター送達
JP2018553882A Active JP7153562B2 (ja) 2016-04-15 2017-04-14 筋ジストロフィーを治療するためのマイクロｒｎａ－２９のアデノ随伴ウイルスベクター送達
JP2018553928A Active JP7189771B2 (ja) 2016-04-15 2017-04-14 筋ジストロフィーを治療するためのマイクロｒｎａ－２９およびマイクロジストロフィンのアデノ随伴ウイルスベクター送達
JP2021190072A Active JP7431789B2 (ja) 2016-04-15 2021-11-24 筋ジストロフィーを治療するためのマイクロジストロフィンのアデノ随伴ウイルスベクター送達
JP2023201579A Active JP7833440B2 (ja) 2016-04-15 2023-11-29 筋ジストロフィーを治療するためのマイクロジストロフィンのアデノ随伴ウイルスベクター送達
JP2025075669A Pending JP2025118741A (ja) 2016-04-15 2025-04-30 筋ジストロフィーを治療するためのマイクロジストロフィンのアデノ随伴ウイルスベクター送達

Family Applications After (5)

Application Number Title Priority Date Filing Date
JP2018553882A Active JP7153562B2 (ja) 2016-04-15 2017-04-14 筋ジストロフィーを治療するためのマイクロｒｎａ－２９のアデノ随伴ウイルスベクター送達
JP2018553928A Active JP7189771B2 (ja) 2016-04-15 2017-04-14 筋ジストロフィーを治療するためのマイクロｒｎａ－２９およびマイクロジストロフィンのアデノ随伴ウイルスベクター送達
JP2021190072A Active JP7431789B2 (ja) 2016-04-15 2021-11-24 筋ジストロフィーを治療するためのマイクロジストロフィンのアデノ随伴ウイルスベクター送達
JP2023201579A Active JP7833440B2 (ja) 2016-04-15 2023-11-29 筋ジストロフィーを治療するためのマイクロジストロフィンのアデノ随伴ウイルスベクター送達
JP2025075669A Pending JP2025118741A (ja) 2016-04-15 2025-04-30 筋ジストロフィーを治療するためのマイクロジストロフィンのアデノ随伴ウイルスベクター送達

Country Status (26)

Country Link
US (7) US11406717B2 (https=)
EP (5) EP4541894A3 (https=)
JP (6) JP7078546B2 (https=)
KR (3) KR102649707B1 (https=)
CN (2) CN118895311A (https=)
AU (4) AU2017250791B2 (https=)
CA (2) CA3020999A1 (https=)
CO (1) CO2018012084A2 (https=)
DK (1) DK3442602T3 (https=)
ES (3) ES2985822T3 (https=)
FI (1) FI3442602T3 (https=)
HR (1) HRP20250541T1 (https=)
HU (1) HUE071243T2 (https=)
IL (3) IL302200B2 (https=)
LT (1) LT3442602T (https=)
MA (2) MA44683B1 (https=)
MD (1) MD3442602T2 (https=)
MX (2) MX2018012604A (https=)
MY (2) MY209041A (https=)
PL (1) PL3442602T3 (https=)
PT (1) PT3442602T (https=)
RS (1) RS66847B1 (https=)
SG (1) SG11201808941PA (https=)
SI (1) SI3442602T1 (https=)
WO (3) WO2017181015A1 (https=)
ZA (2) ZA201806746B (https=)

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CN111733185A (zh) * 2020-06-30 2020-10-02 华南农业大学 通过Mdfi基因编辑来实现动物肉品质改良的方法和应用
EP3936616A1 (en) * 2020-07-10 2022-01-12 Charité - Universitätsmedizin Berlin Microrna-targeted therapy for cardiac repair
KR20240095165A (ko) 2021-08-11 2024-06-25 솔리드 바이오사이언시즈 인크. 근이영양증의 치료
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JP2023059858A (ja) 2021-10-15 2023-04-27 リサーチ インスティチュート アット ネイションワイド チルドレンズ ホスピタル 自己相補的アデノ随伴ウイルスベクター及び筋ジストロフィーの治療におけるその使用
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