HK1250924A1 - 用於基因治疗的经修饰的弗里德赖希共济失调基因及载体 - Google Patents

用於基因治疗的经修饰的弗里德赖希共济失调基因及载体 Download PDF

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HK1250924A1
HK1250924A1 HK18110376.3A HK18110376A HK1250924A1 HK 1250924 A1 HK1250924 A1 HK 1250924A1 HK 18110376 A HK18110376 A HK 18110376A HK 1250924 A1 HK1250924 A1 HK 1250924A1
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nucleic acid
seq
sequence
vector
fxn
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HK18110376.3A
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R‧J‧萨穆尔斯基
R‧J‧薩穆爾斯基
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竹治疗股份有限公司
竹治療股份有限公司
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HK18110376.3A 2015-11-05 2016-11-01 用於基因治疗的经修饰的弗里德赖希共济失调基因及载体 HK1250924A1 (zh)

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US201562251288P 2015-11-05 2015-11-05
US62/251,288 2015-11-05
US201662411980P 2016-10-24 2016-10-24
US62/411,980 2016-10-24
PCT/IB2016/056572 WO2017077451A1 (en) 2015-11-05 2016-11-01 Modified friedreich ataxia genes and vectors for gene therapy

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HK1250924A1 true HK1250924A1 (zh) 2019-01-18

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EP (1) EP3370778A1 (enExample)
JP (2) JP6767483B2 (enExample)
KR (2) KR102200642B1 (enExample)
CN (1) CN108348621A (enExample)
AU (2) AU2016347887B2 (enExample)
BR (1) BR112018007453A2 (enExample)
CA (1) CA2947584A1 (enExample)
CO (1) CO2018004564A2 (enExample)
HK (1) HK1250924A1 (enExample)
IL (1) IL259141A (enExample)
MX (1) MX2018005084A (enExample)
PE (1) PE20181156A1 (enExample)
PH (1) PH12018500964A1 (enExample)
RU (2) RU2021102893A (enExample)
SG (2) SG11201802408RA (enExample)
TW (2) TWI743442B (enExample)
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TWI743442B (zh) 2021-10-21
US20170128528A1 (en) 2017-05-11
SG11201802408RA (en) 2018-05-30
RU2021102893A (ru) 2021-03-03
KR20180077275A (ko) 2018-07-06
CN108348621A (zh) 2018-07-31
JP2018531609A (ja) 2018-11-01
EP3370778A1 (en) 2018-09-12
TWI654301B (zh) 2019-03-21
TW201723179A (zh) 2017-07-01
PE20181156A1 (es) 2018-07-19
AU2020200976A1 (en) 2020-02-27
CO2018004564A2 (es) 2018-12-14
IL259141A (en) 2018-06-28
KR20210005994A (ko) 2021-01-15
RU2743792C2 (ru) 2021-02-26
CA2947584A1 (en) 2017-05-05
US20200384073A1 (en) 2020-12-10
JP6767483B2 (ja) 2020-10-14
AU2020200976B2 (en) 2021-09-30
KR102200642B1 (ko) 2021-01-12
RU2018116076A (ru) 2019-10-28
AU2016347887B2 (en) 2019-11-14
US10548947B2 (en) 2020-02-04
PH12018500964A1 (en) 2018-11-12
TW201920673A (zh) 2019-06-01
AU2016347887A1 (en) 2018-04-19
RU2018116076A3 (enExample) 2020-08-21
WO2017077451A1 (en) 2017-05-11
MX2018005084A (es) 2019-05-16
JP2021019591A (ja) 2021-02-18
BR112018007453A2 (pt) 2018-10-23
SG10201912763QA (en) 2020-02-27

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