JP6767483B2 - 遺伝子療法のための、改変されたフリードライヒ運動失調症遺伝子およびベクター - Google Patents

遺伝子療法のための、改変されたフリードライヒ運動失調症遺伝子およびベクター Download PDF

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JP6767483B2
JP6767483B2 JP2018521395A JP2018521395A JP6767483B2 JP 6767483 B2 JP6767483 B2 JP 6767483B2 JP 2018521395 A JP2018521395 A JP 2018521395A JP 2018521395 A JP2018521395 A JP 2018521395A JP 6767483 B2 JP6767483 B2 JP 6767483B2
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ジェイ． サムルスキー リチャード
ジェイ． サムルスキー リチャード
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バンブー セラペウティクス インク
バンブー セラペウティクス インク
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JP2018521395A 2015-11-05 2016-11-01 遺伝子療法のための、改変されたフリードライヒ運動失調症遺伝子およびベクター Expired - Fee Related JP6767483B2 (ja)

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Application Number Priority Date Filing Date Title
US201562251288P 2015-11-05 2015-11-05
US62/251,288 2015-11-05
US201662411980P 2016-10-24 2016-10-24
US62/411,980 2016-10-24
PCT/IB2016/056572 WO2017077451A1 (en) 2015-11-05 2016-11-01 Modified friedreich ataxia genes and vectors for gene therapy

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JP2020156320A Division JP2021019591A (ja) 2015-11-05 2020-09-17 遺伝子療法のための、改変されたフリードライヒ運動失調症遺伝子およびベクター

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JP2020156320A Pending JP2021019591A (ja) 2015-11-05 2020-09-17 遺伝子療法のための、改変されたフリードライヒ運動失調症遺伝子およびベクター

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US (2) US10548947B2 (enExample)
EP (1) EP3370778A1 (enExample)
JP (2) JP6767483B2 (enExample)
KR (2) KR102200642B1 (enExample)
CN (1) CN108348621A (enExample)
AU (2) AU2016347887B2 (enExample)
BR (1) BR112018007453A2 (enExample)
CA (1) CA2947584A1 (enExample)
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HK (1) HK1250924A1 (enExample)
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JP2021019591A (ja) * 2015-11-05 2021-02-18 バンブー セラペウティクス インク 遺伝子療法のための、改変されたフリードライヒ運動失調症遺伝子およびベクター

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