CN112501208A - 用于溶酶体障碍的基因疗法 - Google Patents

用于溶酶体障碍的基因疗法 Download PDF

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CN112501208A
CN112501208A CN202011187145.9A CN202011187145A CN112501208A CN 112501208 A CN112501208 A CN 112501208A CN 202011187145 A CN202011187145 A CN 202011187145A CN 112501208 A CN112501208 A CN 112501208A
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nucleic acid
vector
sequence
itr
raav
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阿萨·阿贝利奥维奇
劳拉·赫克曼
赫维·莱茵
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Privelle Therapeutics
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Privelle Therapeutics
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CN202011187145.9A 2017-10-03 2018-10-03 用于溶酶体障碍的基因疗法 Pending CN112501208A (zh)

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US201762567303P 2017-10-03 2017-10-03
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CN201880075728.7A CN111465691A (zh) 2017-10-03 2018-10-03 用于溶酶体障碍的基因疗法

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US (3) US11807849B2 (https=)
EP (1) EP3692151A4 (https=)
JP (4) JP2020537542A (https=)
KR (2) KR20200078513A (https=)
CN (2) CN112501208A (https=)
AU (3) AU2018346102B2 (https=)
BR (1) BR112020006671A2 (https=)
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