AU2018346102B2 - Gene therapies for lysosomal disorders - Google Patents

Gene therapies for lysosomal disorders Download PDF

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Publication number
AU2018346102B2
AU2018346102B2 AU2018346102A AU2018346102A AU2018346102B2 AU 2018346102 B2 AU2018346102 B2 AU 2018346102B2 AU 2018346102 A AU2018346102 A AU 2018346102A AU 2018346102 A AU2018346102 A AU 2018346102A AU 2018346102 B2 AU2018346102 B2 AU 2018346102B2
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Australia
Prior art keywords
nucleic acid
seq
sequence
raav
expression construct
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AU2018346102A
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AU2018346102A1 (en
AU2018346102A2 (en
Inventor
Asa Abeliovich
Laura Heckman
Herve Rhinn
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Prevail Therapeutics Inc
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Prevail Therapeutics Inc
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Publication of AU2018346102A1 publication Critical patent/AU2018346102A1/en
Priority to AU2020260476A priority Critical patent/AU2020260476B2/en
Publication of AU2018346102A2 publication Critical patent/AU2018346102A2/en
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Priority to AU2023214366A priority patent/AU2023214366B2/en
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AU2018346102A 2017-10-03 2018-10-03 Gene therapies for lysosomal disorders Active AU2018346102B2 (en)

Priority Applications (2)

Application Number Priority Date Filing Date Title
AU2020260476A AU2020260476B2 (en) 2017-10-03 2020-10-29 Gene therapies for lysosomal disorders
AU2023214366A AU2023214366B2 (en) 2017-10-03 2023-08-11 Gene therapies for lysosomal disorders

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Application Number Priority Date Filing Date Title
US201762567305P 2017-10-03 2017-10-03
US201762567303P 2017-10-03 2017-10-03
US62/567,303 2017-10-03
US62/567,305 2017-10-03
PCT/US2018/054223 WO2019070891A1 (en) 2017-10-03 2018-10-03 GENE THERAPIES FOR LYSOSOMAL DISORDERS

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AU2023214366A Division AU2023214366B2 (en) 2017-10-03 2023-08-11 Gene therapies for lysosomal disorders

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AU2018346102A1 AU2018346102A1 (en) 2020-04-30
AU2018346102A2 AU2018346102A2 (en) 2020-11-12
AU2018346102B2 true AU2018346102B2 (en) 2023-05-11

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