CN101505739A - 由具有无义突变的dna生产功能蛋白的方法以及相关疾病的治疗 - Google Patents
由具有无义突变的dna生产功能蛋白的方法以及相关疾病的治疗 Download PDFInfo
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- A61P—SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
- A61P5/00—Drugs for disorders of the endocrine system
- A61P5/10—Drugs for disorders of the endocrine system of the posterior pituitary hormones, e.g. oxytocin, ADH
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- A—HUMAN NECESSITIES
- A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
- A61P—SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
- A61P5/00—Drugs for disorders of the endocrine system
- A61P5/14—Drugs for disorders of the endocrine system of the thyroid hormones, e.g. T3, T4
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- A—HUMAN NECESSITIES
- A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
- A61P—SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
- A61P7/00—Drugs for disorders of the blood or the extracellular fluid
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- A—HUMAN NECESSITIES
- A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
- A61P—SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
- A61P7/00—Drugs for disorders of the blood or the extracellular fluid
- A61P7/04—Antihaemorrhagics; Procoagulants; Haemostatic agents; Antifibrinolytic agents
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- A—HUMAN NECESSITIES
- A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
- A61P—SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
- A61P9/00—Drugs for disorders of the cardiovascular system
- A61P9/10—Drugs for disorders of the cardiovascular system for treating ischaemic or atherosclerotic diseases, e.g. antianginal drugs, coronary vasodilators, drugs for myocardial infarction, retinopathy, cerebrovascula insufficiency, renal arteriosclerosis
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- Health & Medical Sciences (AREA)
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- Nuclear Medicine, Radiotherapy & Molecular Imaging (AREA)
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| US81308506P | 2006-06-12 | 2006-06-12 | |
| US60/813,085 | 2006-06-12 | ||
| PCT/US2007/008268 WO2007117438A2 (en) | 2006-03-30 | 2007-03-29 | Methods for the production of functional protein from dna having a nonsense mutation and the treatment of disorders associated therewith |
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Cited By (2)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| CN103074346A (zh) * | 2013-01-22 | 2013-05-01 | 山西大学 | 一种用于促通读药物筛选的有限细胞株的建立方法 |
| CN107916252A (zh) * | 2017-11-17 | 2018-04-17 | 首都儿科研究所 | 一株用于验证脊肌萎缩症的永生淋巴细胞株 |
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| ES2593836T3 (es) | 2009-04-24 | 2016-12-13 | Biomarin Technologies B.V. | Oligonucleótido que comprende una inosina para tratar la DMD |
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2008
- 2008-09-28 IL IL194454A patent/IL194454A/en not_active IP Right Cessation
- 2008-10-24 NO NO20084488A patent/NO20084488L/no not_active Application Discontinuation
-
2012
- 2012-10-18 IL IL222557A patent/IL222557A/en active IP Right Grant
-
2013
- 2013-06-25 JP JP2013133071A patent/JP5798154B2/ja not_active Expired - Fee Related
-
2016
- 2016-02-16 US US15/044,225 patent/US20160199357A1/en not_active Abandoned
Cited By (3)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| CN103074346A (zh) * | 2013-01-22 | 2013-05-01 | 山西大学 | 一种用于促通读药物筛选的有限细胞株的建立方法 |
| CN107916252A (zh) * | 2017-11-17 | 2018-04-17 | 首都儿科研究所 | 一株用于验证脊肌萎缩症的永生淋巴细胞株 |
| CN107916252B (zh) * | 2017-11-17 | 2021-01-22 | 首都儿科研究所 | 一株用于验证脊肌萎缩症的永生淋巴细胞株 |
Also Published As
| Publication number | Publication date |
|---|---|
| EP2007365A2 (en) | 2008-12-31 |
| IL194454A (en) | 2013-01-31 |
| CA2647903C (en) | 2016-12-13 |
| EP2387995A1 (en) | 2011-11-23 |
| SG170819A1 (en) | 2011-05-30 |
| NZ571899A (en) | 2012-07-27 |
| RU2008142957A (ru) | 2010-05-10 |
| RU2462246C2 (ru) | 2012-09-27 |
| IL222557A (en) | 2016-09-29 |
| CA2647903A1 (en) | 2007-10-18 |
| IN2014CN04406A (enExample) | 2015-09-04 |
| US9289398B2 (en) | 2016-03-22 |
| JP2009532368A (ja) | 2009-09-10 |
| IL222557A0 (en) | 2012-12-31 |
| AU2007235524B2 (en) | 2013-09-12 |
| JP5798154B2 (ja) | 2015-10-21 |
| NO20084488L (no) | 2008-12-19 |
| NZ596965A (en) | 2013-06-28 |
| MX2008012515A (es) | 2008-11-19 |
| JP2013234189A (ja) | 2013-11-21 |
| WO2007117438A3 (en) | 2008-10-23 |
| US20110046136A1 (en) | 2011-02-24 |
| BRPI0710213A2 (pt) | 2011-04-12 |
| IL194454A0 (en) | 2009-08-03 |
| JP5367563B2 (ja) | 2013-12-11 |
| AU2007235524A1 (en) | 2007-10-18 |
| WO2007117438A2 (en) | 2007-10-18 |
| US20160199357A1 (en) | 2016-07-14 |
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