AU2007235524B2 - Methods for the production of functional protein from DNA having a nonsense mutation and the treatment of disorders associated therewith - Google Patents
Methods for the production of functional protein from DNA having a nonsense mutation and the treatment of disorders associated therewith Download PDFInfo
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- AU2007235524B2 AU2007235524B2 AU2007235524A AU2007235524A AU2007235524B2 AU 2007235524 B2 AU2007235524 B2 AU 2007235524B2 AU 2007235524 A AU2007235524 A AU 2007235524A AU 2007235524 A AU2007235524 A AU 2007235524A AU 2007235524 B2 AU2007235524 B2 AU 2007235524B2
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| US60/813,085 | 2006-06-12 | ||
| PCT/US2007/008268 WO2007117438A2 (en) | 2006-03-30 | 2007-03-29 | Methods for the production of functional protein from dna having a nonsense mutation and the treatment of disorders associated therewith |
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| AU2007235524A1 AU2007235524A1 (en) | 2007-10-18 |
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| USRE48468E1 (en) | 2007-10-26 | 2021-03-16 | Biomarin Technologies B.V. | Means and methods for counteracting muscle disorders |
| US20120046342A1 (en) | 2009-04-24 | 2012-02-23 | Prosensa Technologies B.V. | Oligonucleotide comprising an inosine for treating dmd |
| EP2251437B1 (en) | 2009-05-13 | 2013-12-04 | Hannelore Breitenbach-Koller | Method for identifying compounds that control the translational activity of ribosomal proteins in differential mRNA expression |
| US8247436B2 (en) | 2010-03-19 | 2012-08-21 | Novartis Ag | Pyridine and pyrazine derivative for the treatment of CF |
| CN118581086A (zh) | 2012-01-27 | 2024-09-03 | 比奥马林技术公司 | 用于治疗杜兴型肌营养不良症和贝克型肌营养不良症的具有改善特性的rna调节性寡核苷酸 |
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Also Published As
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| RU2462246C2 (ru) | 2012-09-27 |
| CN101505739A (zh) | 2009-08-12 |
| IL222557A (en) | 2016-09-29 |
| IL194454A (en) | 2013-01-31 |
| EP2387995A1 (en) | 2011-11-23 |
| EP2007365A2 (en) | 2008-12-31 |
| JP2009532368A (ja) | 2009-09-10 |
| NZ596965A (en) | 2013-06-28 |
| SG170819A1 (en) | 2011-05-30 |
| NO20084488L (no) | 2008-12-19 |
| CA2647903A1 (en) | 2007-10-18 |
| CA2647903C (en) | 2016-12-13 |
| AU2007235524A1 (en) | 2007-10-18 |
| WO2007117438A3 (en) | 2008-10-23 |
| US20110046136A1 (en) | 2011-02-24 |
| IN2014CN04406A (enExample) | 2015-09-04 |
| BRPI0710213A2 (pt) | 2011-04-12 |
| US9289398B2 (en) | 2016-03-22 |
| US20160199357A1 (en) | 2016-07-14 |
| JP5367563B2 (ja) | 2013-12-11 |
| JP5798154B2 (ja) | 2015-10-21 |
| RU2008142957A (ru) | 2010-05-10 |
| NZ571899A (en) | 2012-07-27 |
| IL194454A0 (en) | 2009-08-03 |
| JP2013234189A (ja) | 2013-11-21 |
| WO2007117438A2 (en) | 2007-10-18 |
| IL222557A0 (en) | 2012-12-31 |
| MX2008012515A (es) | 2008-11-19 |
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