UA125373C2 - Вектор аденоасоційованого вірусу для лікування мукополісахаридозів - Google Patents
Вектор аденоасоційованого вірусу для лікування мукополісахаридозів Download PDFInfo
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- UA125373C2 UA125373C2 UAA201711584A UAA201711584A UA125373C2 UA 125373 C2 UA125373 C2 UA 125373C2 UA A201711584 A UAA201711584 A UA A201711584A UA A201711584 A UAA201711584 A UA A201711584A UA 125373 C2 UA125373 C2 UA 125373C2
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| PCT/EP2016/062655 WO2016193431A1 (en) | 2015-06-05 | 2016-06-03 | Adenoassociated virus vectors for the treatment of mucopolysaccharidoses |
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| US9309534B2 (en) | 2010-07-12 | 2016-04-12 | Universidad Autonoma De Barcelona | Gene therapy composition for use in diabetes treatment |
| EP2692868A1 (en) | 2012-08-02 | 2014-02-05 | Universitat Autònoma De Barcelona | Adeno-associated viral (AAV) vectors useful for transducing adipose tissue |
| US10973931B2 (en) | 2014-09-16 | 2021-04-13 | Universitat Autònoma De Barcelona | Adeno-associated viral vectors for the gene therapy of metabolic diseases |
| US11085055B2 (en) | 2014-12-05 | 2021-08-10 | Universitat Autonoma De Barcelona | Viral vectors for the treatment of diabetes |
| EP3242945B1 (en) | 2015-01-07 | 2021-09-01 | Universitat Autònoma de Barcelona | Single-vector gene construct comprising insulin and glucokinase genes |
| US11253612B2 (en) | 2016-04-15 | 2022-02-22 | The Trustees Of The University Of Pennsylvania | Gene therapy for treating mucopolysaccharidosis type II |
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| KR100762945B1 (ko) * | 2004-09-08 | 2007-10-04 | 진동규 | 동물 세포주를 이용한 이듀로네이트-설파타제의 발현 방법및 그 발현을 위한 세포주 |
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| WO2011108451A1 (ja) | 2010-03-01 | 2011-09-09 | 日本ケミカルリサーチ株式会社 | 遺伝子ノックアウト細胞を用いた組換え体リソソーム酵素の製造方法 |
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| KR101535791B1 (ko) * | 2010-11-12 | 2015-07-10 | 주식회사 녹십자 | 개량형 이듀로네이트-2-설파타제 및 이의 용도 |
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