TWI835719B - 經修飾之嚮導rna - Google Patents
經修飾之嚮導rna Download PDFInfo
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- TWI835719B TWI835719B TW106143268A TW106143268A TWI835719B TW I835719 B TWI835719 B TW I835719B TW 106143268 A TW106143268 A TW 106143268A TW 106143268 A TW106143268 A TW 106143268A TW I835719 B TWI835719 B TW I835719B
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| WO2017136794A1 (en) | 2016-02-03 | 2017-08-10 | Massachusetts Institute Of Technology | Structure-guided chemical modification of guide rna and its applications |
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| JP7231935B2 (ja) | 2016-08-03 | 2023-03-08 | プレジデント アンド フェローズ オブ ハーバード カレッジ | アデノシン核酸塩基編集因子およびそれらの使用 |
| EP3497214B1 (en) | 2016-08-09 | 2023-06-28 | President and Fellows of Harvard College | Programmable cas9-recombinase fusion proteins and uses thereof |
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| RU2019135845A (ru) | 2017-04-11 | 2021-05-11 | Ридженерон Фармасьютикалз, Инк. | Анализы для скрининга активности модуляторов членов семейства (17-бета)гидроксистероиддегидрогеназ (hsd17b) |
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| CN111417728A (zh) | 2017-09-29 | 2020-07-14 | 因特利亚治疗公司 | 用于ttr基因编辑及治疗attr淀粉样变性的组合物及方法 |
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