PL2283134T3 - Sposób skutecznego pominięcia eksonu (44) w dystrofii mięśniowej Duchenne'a i związane z nim środki - Google Patents

Sposób skutecznego pominięcia eksonu (44) w dystrofii mięśniowej Duchenne'a i związane z nim środki

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Publication number
PL2283134T3
PL2283134T3 PL09746807T PL09746807T PL2283134T3 PL 2283134 T3 PL2283134 T3 PL 2283134T3 PL 09746807 T PL09746807 T PL 09746807T PL 09746807 T PL09746807 T PL 09746807T PL 2283134 T3 PL2283134 T3 PL 2283134T3
Authority
PL
Poland
Prior art keywords
skipping
muscular dystrophy
duchenne muscular
associated means
efficient exon
Prior art date
Application number
PL09746807T
Other languages
English (en)
Inventor
Gerardus Johannes Platenburg
Kimpe Josephus Johannes De
Deutekom Judith Christina Theodora Van
Ommen Garrit-Jan Boudewijn Van
Annemieke Aartsma-Rus
Original Assignee
Biomarin Tech Bv
Academisch Ziekenhuis Leiden
Priority date (The priority date is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the date listed.)
Filing date
Publication date
Application filed by Biomarin Tech Bv, Academisch Ziekenhuis Leiden filed Critical Biomarin Tech Bv
Publication of PL2283134T3 publication Critical patent/PL2283134T3/pl

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    • C12N15/00—Mutation or genetic engineering; DNA or RNA concerning genetic engineering, vectors, e.g. plasmids, or their isolation, preparation or purification; Use of hosts therefor
    • C12N15/09—Recombinant DNA-technology
    • C12N15/11—DNA or RNA fragments; Modified forms thereof; Non-coding nucleic acids having a biological activity
    • C12N15/113—Non-coding nucleic acids modulating the expression of genes, e.g. antisense oligonucleotides; Antisense DNA or RNA; Triplex- forming oligonucleotides; Catalytic nucleic acids, e.g. ribozymes; Nucleic acids used in co-suppression or gene silencing
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    • A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61P—SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
    • A61P21/00—Drugs for disorders of the muscular or neuromuscular system
    • A—HUMAN NECESSITIES
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    • A61P—SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
    • A61P21/00—Drugs for disorders of the muscular or neuromuscular system
    • A61P21/04—Drugs for disorders of the muscular or neuromuscular system for myasthenia gravis
    • A—HUMAN NECESSITIES
    • A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
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    • C12N2320/00—Applications; Uses
    • C12N2320/30—Special therapeutic applications
    • C12N2320/33—Alteration of splicing

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  • Medicines That Contain Protein Lipid Enzymes And Other Medicines (AREA)
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PL09746807T 2008-05-14 2009-05-14 Sposób skutecznego pominięcia eksonu (44) w dystrofii mięśniowej Duchenne'a i związane z nim środki PL2283134T3 (pl)

Applications Claiming Priority (4)

Application Number Priority Date Filing Date Title
EP08156193A EP2119783A1 (en) 2008-05-14 2008-05-14 Method for efficient exon (44) skipping in Duchenne Muscular Dystrophy and associated means
US12801008P 2008-05-15 2008-05-15
PCT/NL2009/050258 WO2009139630A2 (en) 2008-05-14 2009-05-14 Method for efficient exon (44) skipping in duchenne muscular dystrophy and associated means
EP09746807.8A EP2283134B1 (en) 2008-05-14 2009-05-14 Method for efficient exon (44) skipping in duchenne muscular dystrophy and associated means

Publications (1)

Publication Number Publication Date
PL2283134T3 true PL2283134T3 (pl) 2016-03-31

Family

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PL09746807T PL2283134T3 (pl) 2008-05-14 2009-05-14 Sposób skutecznego pominięcia eksonu (44) w dystrofii mięśniowej Duchenne'a i związane z nim środki
PL14179979T PL2813570T3 (pl) 2008-05-14 2009-05-14 Sposób skutecznego pominięcia eksonu (44) w dystrofii mięśniowej Duchenne'a i związane z nim środki

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PL14179979T PL2813570T3 (pl) 2008-05-14 2009-05-14 Sposób skutecznego pominięcia eksonu (44) w dystrofii mięśniowej Duchenne'a i związane z nim środki

Country Status (18)

Country Link
US (4) US9139828B2 (pl)
EP (5) EP2119783A1 (pl)
JP (2) JP5696039B2 (pl)
CN (1) CN102171342B (pl)
AU (5) AU2009247037B2 (pl)
CA (2) CA2723968C (pl)
CY (1) CY1117098T1 (pl)
DK (2) DK2813570T3 (pl)
ES (3) ES2551154T3 (pl)
HK (3) HK1154620A1 (pl)
HR (2) HRP20151053T1 (pl)
HU (2) HUE026385T2 (pl)
IL (5) IL300399A (pl)
LT (1) LT2813570T (pl)
NZ (2) NZ600183A (pl)
PL (2) PL2283134T3 (pl)
PT (2) PT2283134E (pl)
WO (1) WO2009139630A2 (pl)

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