KR20220004648A - Ttr 가이드 rna, 및 rna-가이드 dna 결합제를 암호화하는 폴리뉴클레오티드를 포함하는 조성물 및 방법 - Google Patents

Ttr 가이드 rna, 및 rna-가이드 dna 결합제를 암호화하는 폴리뉴클레오티드를 포함하는 조성물 및 방법 Download PDF

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KR20220004648A
KR20220004648A KR1020217035004A KR20217035004A KR20220004648A KR 20220004648 A KR20220004648 A KR 20220004648A KR 1020217035004 A KR1020217035004 A KR 1020217035004A KR 20217035004 A KR20217035004 A KR 20217035004A KR 20220004648 A KR20220004648 A KR 20220004648A
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lipid
composition
seq
rna
ttr
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용 창
세스 씨. 알렉산더
크리스티 엠. 우드
아티 마헨드라 프라카쉬 칸졸리아
쇼부 오다테
제시카 린 시쳐
레이날드 마이클 레스카뷰
월터 스트랩스
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인텔리아 테라퓨틱스, 인크.
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KR1020217035004A 2019-03-28 2020-03-27 Ttr 가이드 rna, 및 rna-가이드 dna 결합제를 암호화하는 폴리뉴클레오티드를 포함하는 조성물 및 방법 Pending KR20220004648A (ko)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201962825637P 2019-03-28 2019-03-28
US62/825,637 2019-03-28
PCT/US2020/025513 WO2020198697A1 (en) 2019-03-28 2020-03-27 Compositions and methods comprising a ttr guide rna and a polynucleotide encoding an rna-guided dna binding agent

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KR20220004648A true KR20220004648A (ko) 2022-01-11

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KR1020217035004A Pending KR20220004648A (ko) 2019-03-28 2020-03-27 Ttr 가이드 rna, 및 rna-가이드 dna 결합제를 암호화하는 폴리뉴클레오티드를 포함하는 조성물 및 방법

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US (3) US20230044994A1 (enExample)
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CN (1) CN113874076A (enExample)
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