CN113874076A - 包括ttr向导rna和对rna引导的dna结合剂进行编码的多核苷酸的组合物和方法 - Google Patents

包括ttr向导rna和对rna引导的dna结合剂进行编码的多核苷酸的组合物和方法 Download PDF

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CN113874076A
CN113874076A CN202080038208.6A CN202080038208A CN113874076A CN 113874076 A CN113874076 A CN 113874076A CN 202080038208 A CN202080038208 A CN 202080038208A CN 113874076 A CN113874076 A CN 113874076A
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composition
lipid
seq
rna
orf
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Y·常
S·C·亚历山大
K·M·伍德
A·M·P·坎乔利亚
S·奥达特
J·L·塞泽
R·M·莱斯卡博
W·斯特雷普斯
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Intellia Therapeutics Inc
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CN202080038208.6A 2019-03-28 2020-03-27 包括ttr向导rna和对rna引导的dna结合剂进行编码的多核苷酸的组合物和方法 Pending CN113874076A (zh)

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US201962825637P 2019-03-28 2019-03-28
US62/825,637 2019-03-28
PCT/US2020/025513 WO2020198697A1 (en) 2019-03-28 2020-03-27 Compositions and methods comprising a ttr guide rna and a polynucleotide encoding an rna-guided dna binding agent

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