KR20170054445A - 뉴클레아제-매개된 게놈 엔지니어링 및 조혈 줄기세포에서의 교정을 위한 방법 및 조성물 - Google Patents

뉴클레아제-매개된 게놈 엔지니어링 및 조혈 줄기세포에서의 교정을 위한 방법 및 조성물 Download PDF

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KR20170054445A
KR20170054445A KR1020177009275A KR20177009275A KR20170054445A KR 20170054445 A KR20170054445 A KR 20170054445A KR 1020177009275 A KR1020177009275 A KR 1020177009275A KR 20177009275 A KR20177009275 A KR 20177009275A KR 20170054445 A KR20170054445 A KR 20170054445A
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gene
dna
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그레고리 제이. 코스트
제프리 씨. 밀러
레이 장
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상가모 테라퓨틱스, 인코포레이티드
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KR1020177009275A 2014-09-16 2015-09-16 뉴클레아제-매개된 게놈 엔지니어링 및 조혈 줄기세포에서의 교정을 위한 방법 및 조성물 Ceased KR20170054445A (ko)

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US201462051159P 2014-09-16 2014-09-16
US62/051,159 2014-09-16
PCT/US2015/050411 WO2016044416A1 (en) 2014-09-16 2015-09-16 Methods and compositions for nuclease-mediated genome engineering and correction in hematopoietic stem cells

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