KR102178322B1 - 변형된 인자 ix, 및 세포, 기관 및 조직으로 유전자를 전달하기 위한 조성물, 방법 및 용도 - Google Patents

변형된 인자 ix, 및 세포, 기관 및 조직으로 유전자를 전달하기 위한 조성물, 방법 및 용도 Download PDF

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KR102178322B1
KR102178322B1 KR1020187002040A KR20187002040A KR102178322B1 KR 102178322 B1 KR102178322 B1 KR 102178322B1 KR 1020187002040 A KR1020187002040 A KR 1020187002040A KR 20187002040 A KR20187002040 A KR 20187002040A KR 102178322 B1 KR102178322 B1 KR 102178322B1
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캐서린 에이. 하이
사비어 안구엘라
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더 칠드런스 호스피탈 오브 필라델피아
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KR1020187002040A 2015-06-23 2016-06-23 변형된 인자 ix, 및 세포, 기관 및 조직으로 유전자를 전달하기 위한 조성물, 방법 및 용도 Active KR102178322B1 (ko)

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US201562183599P 2015-06-23 2015-06-23
US62/183,599 2015-06-23
US201662315453P 2016-03-30 2016-03-30
US62/315,453 2016-03-30
US201662338315P 2016-05-18 2016-05-18
US62/338,315 2016-05-18
US201662348781P 2016-06-10 2016-06-10
US62/348,781 2016-06-10
US201662349572P 2016-06-13 2016-06-13
US62/349,572 2016-06-13
PCT/US2016/039075 WO2016210170A1 (en) 2015-06-23 2016-06-23 Modified factor ix, and compositions, methods and uses for gene transfer to cells, organs and tissues

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KR1020187002040A Active KR102178322B1 (ko) 2015-06-23 2016-06-23 변형된 인자 ix, 및 세포, 기관 및 조직으로 유전자를 전달하기 위한 조성물, 방법 및 용도

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