JP7577291B6 - Ａａｖカプシド設計 - Google Patents

Ａａｖカプシド設計 Download PDF

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JP7577291B6
JP7577291B6 JP2019520377A JP2019520377A JP7577291B6 JP 7577291 B6 JP7577291 B6 JP 7577291B6 JP 2019520377 A JP2019520377 A JP 2019520377A JP 2019520377 A JP2019520377 A JP 2019520377A JP 7577291 B6 JP7577291 B6 JP 7577291B6
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hsa
mir
aav
raav
transgene
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JP7577291B2 (ja
JP2019530463A5 (cg-RX-API-DMAC7.html
JP2019530463A (ja
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ガオ，グワンピン
シュウ，グワンチャオ
タイ，フィリップ
ウェイ，ユカン
ルオ，リー
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ユニバーシティ オブ マサチューセッツ
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  • Health & Medical Sciences (AREA)
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  • Organic Chemistry (AREA)
  • General Health & Medical Sciences (AREA)
  • Bioinformatics & Cheminformatics (AREA)
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  • Animal Behavior & Ethology (AREA)
  • Public Health (AREA)
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  • Biomedical Technology (AREA)
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  • General Engineering & Computer Science (AREA)
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  • Microbiology (AREA)
  • Plant Pathology (AREA)
  • Physics & Mathematics (AREA)
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  • Proteomics, Peptides & Aminoacids (AREA)
  • Diabetes (AREA)
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JP2019520377A 2016-10-13 2017-10-13 Ａａｖカプシド設計 Active JP7577291B6 (ja)

Priority Applications (1)

Application Number Priority Date Filing Date Title
JP2023015896A JP7742533B2 (ja) 2016-10-13 2023-02-06 Ａａｖカプシド設計

Applications Claiming Priority (7)

Application Number Priority Date Filing Date Title
US201662408022P 2016-10-13 2016-10-13
US62/408,022 2016-10-13
US201662417756P 2016-11-04 2016-11-04
US62/417,756 2016-11-04
US201762486642P 2017-04-18 2017-04-18
US62/486,642 2017-04-18
PCT/US2017/056614 WO2018071831A1 (en) 2016-10-13 2017-10-13 Aav capsid designs

Related Child Applications (1)

Application Number Title Priority Date Filing Date
JP2023015896A Division JP7742533B2 (ja) 2016-10-13 2023-02-06 Ａａｖカプシド設計

Publications (4)

Publication Number Publication Date
JP2019530463A JP2019530463A (ja) 2019-10-24
JP2019530463A5 JP2019530463A5 (cg-RX-API-DMAC7.html) 2020-11-26
JP7577291B2 JP7577291B2 (ja) 2024-11-05
JP7577291B6 true JP7577291B6 (ja) 2024-11-26

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JP2023015896A Active JP7742533B2 (ja) 2016-10-13 2023-02-06 Ａａｖカプシド設計

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US (2) US11578340B2 (cg-RX-API-DMAC7.html)
EP (1) EP3526333A4 (cg-RX-API-DMAC7.html)
JP (2) JP7577291B6 (cg-RX-API-DMAC7.html)
KR (2) KR20190075964A (cg-RX-API-DMAC7.html)
CN (1) CN110506119A (cg-RX-API-DMAC7.html)
AU (2) AU2017341849B2 (cg-RX-API-DMAC7.html)
CA (1) CA3040483A1 (cg-RX-API-DMAC7.html)
WO (1) WO2018071831A1 (cg-RX-API-DMAC7.html)

Families Citing this family (44)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US8734809B2 (en) 2009-05-28 2014-05-27 University Of Massachusetts AAV's and uses thereof
RU2738421C2 (ru) 2014-10-21 2020-12-14 Юниверсити Оф Массачусетс Варианты рекомбинантных aav и их применения
GB201508026D0 (en) 2015-05-11 2015-06-24 Ucl Business Plc Capsid
US20200316221A1 (en) * 2016-10-13 2020-10-08 University Of Massachusetts Aav capsid designs
WO2018071831A1 (en) 2016-10-13 2018-04-19 University Of Massachusetts Aav capsid designs
US20230048025A1 (en) * 2016-12-22 2023-02-16 Oregon Health & Science University Adeno associated viral vectors
CN110462037A (zh) * 2017-01-30 2019-11-15 学校法人日本医科大学 腺相关病毒(aav)衣壳蛋白的突变体
MX2019012113A (es) 2017-04-14 2020-09-10 Univ Nat Taiwan Terapia génica para la deficiencia de la aadc.
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